- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Genetic Diseases in Colombia
Total 14270 results
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Fundación Grupo de Investigación en Cuidados Intensivos...Recordati Rare DiseasesActive, not recruiting
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Natera, Inc.Ferring PharmaceuticalsTerminatedIn Vitro Fertilization (IVF) | Preimplantation Genetic Diagnosis (PGD) | Preimplantation Gentic Screening (PGS)United States
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University of Missouri-ColumbiaTerminatedAtopic DermatitisUnited States
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University of British ColumbiaVancouver General HospitalWithdrawn
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University of British ColumbiaCompleted
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University of British ColumbiaUnknown
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Escuela NeijingCompletedAge-related Macular Degeneration | Stargardt Disease | Macular DystrophyColombia
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Rutgers, The State University of New JerseyNational Cancer Institute (NCI); Georgetown UniversityRecruitingHereditary Cancer | Genetic TestingUnited States
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University of Missouri-ColumbiaRecruitingGenetic Predisposition to Disease | Healthy VolunteersUnited States
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University of British ColumbiaBiogenCompletedHemophilia A, Congenital | Hemophilia B, CongenitalCanada
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Children's National Research InstituteFoundation to Eradicate DuchenneActive, not recruitingDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...Completed
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRecruiting
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Sangamo TherapeuticsTerminated
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The Duchenne RegistryParent Project Muscular DystrophyRecruiting
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Timothy EkhlassiEnrolling by invitationPain | Dermatochalasis | Dermatochalasis of Eyelid | Dermatochalasis of Both Upper Eyelids | Dermatochalasis of Both Eyes | Dermatochalasis of Right Upper Eyelid | Dermatochalasis of Left Upper EyelidCanada
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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University of British ColumbiaCanadian Institutes of Health Research (CIHR); Saudi Arabian Cultural Bureau...Unknown
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Silk Road Therapies, Inc.Not yet recruitingBehcet Syndrome | Behcet DiseaseUnited States
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Welichem Biotech Inc.CompletedDermatitis, AtopicCanada
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Northwestern UniversityGeorgetown UniversityEnrolling by invitationChronic Kidney Diseases | Genetic PredispositionUnited States
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... and other collaboratorsCompletedBrain Diseases, Metabolic, Inborn | Ornithine Transcarbamylase Deficiency | Urea Cycle DisorderUnited States
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Prolong PharmaceuticalsCompletedSickle Cell DiseaseColombia, Panama
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Children's National Research InstituteEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationChild Development | Congenital Zika Syndrome | Zika Virus | Congenital InfectionUnited States, Colombia
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Santhera PharmaceuticalsSanthera PharmaceuticalsActive, not recruitingDuchenne Muscular DystrophyCanada
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Acceleron Pharma Inc. (a wholly owned subsidiary...Terminated
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Assistance Publique - Hôpitaux de ParisAssociation pour l'Etude des Fonctions Digestives (AEFD)UnknownPorphyria Cutanea TardaFrance
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Novo Nordisk A/SRecruitingIdiopathic Short StatureUnited States
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Adam S. Kibel, MDNational Cancer Institute (NCI)RecruitingProstate Cancer | Polygenic Risk ScoreUnited States
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)CompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States
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University of British ColumbiaRecruiting
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University of British ColumbiaCompleted
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National Human Genome Research Institute (NHGRI)RecruitingGenetic DiseaseUnited States
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Apyx MedicalCompletedLax SkinUnited States
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McMaster UniversityRecruiting
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University of British ColumbiaActive, not recruiting
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University of South CarolinaPfizerCompleted
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National Human Genome Research Institute (NHGRI)Merck Sharp & Dohme LLC; Duke University; University of Massachusetts, WorcesterRecruitingFever | Genetic Diseases | Familial Mediterranean Fever (FMF) | Autoinflammation | Periodic Fever | ROSAH | ALPK1United States
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Salem Anaesthesia Pain ClinicCompletedSickle Cell Disease | Sickle Cell AbnormalityCanada
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University of British ColumbiaRecruiting
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University of British ColumbiaCompleted
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University of British ColumbiaCompletedHealthy | Cystic Fibrosis | Lung; DiseaseCanada
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Assistance Publique - Hôpitaux de ParisCompleted
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BioMarin PharmaceuticalRecruitingIdiopathic Short StatureUnited States
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University of British ColumbiaTerminated
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University of British ColumbiaUnknownBronchiectasis | Cystic FibrosisCanada
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University of British ColumbiaVancouver Coastal Health Research Institute; Genome British ColumbiaRecruitingAcute Coronary Syndrome | Familial Hypercholesterolemia | STEMI | NSTEMI - Non-ST Segment Elevation MI | Familial Hypercholesterolemia - Heterozygous | Familial Hypercholesterolemia Due to Genetic Defect of Apolipoprotein B | Familial Hypercholesterolemia Due to Heterozygous LDL Receptor Mutation and other conditionsCanada
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Children's National Research InstituteCompleted