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Clinical Trials on Genetic Mutation in New Zealand
Total 2558 results
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Intellia TherapeuticsRecruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisUnited Kingdom, New Zealand, Sweden
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Stony Brook UniversityOtto Bock Healthcare Products GmbHCompletedAmputationUnited States
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Novartis PharmaceuticalsCompletedNALP3 MutationUnited Kingdom, France, Germany, India, Spain
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CSL LimitedCompletedPrimary Immune DeficiencyAustralia, New Zealand
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Memorial Sloan Kettering Cancer CenterActive, not recruitingScreening Breast MRI in Patients Who Are BRCA Mutation CarriersUnited States
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RWJ Barnabas Health at Jersey City Medical CenterUnknownLynch Syndrome | Endometrial Cancer | Somatic Mutation | Cancer Gene MutationUnited States
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Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisGermany, New Zealand, Australia
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Southwest Oncology GroupNational Cancer Institute (NCI)CompletedBreast Cancer | brca1 Mutation Carrier | brca2 Mutation CarrierUnited States
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Rutgers, The State University of New JerseyNational Cancer Institute (NCI)RecruitingBRCA1 Gene Mutation | BRCA2 Gene Mutation | Recurrent Ovarian Carcinoma | Recurrent Malignant Solid Neoplasm | Metastatic Malignant Solid Neoplasm | Stage IV Breast Cancer AJCC v6 and v7 | Stage III Breast Cancer AJCC v7 | Stage IIIA Breast Cancer AJCC v7 | Stage IIIB Breast Cancer AJCC v7 | Stage IIIC... and other conditionsUnited States
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PharmaxisCompletedCystic FibrosisAustralia, New Zealand
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Memorial Sloan Kettering Cancer CenterRecruitingStudy of Cemiplimab Combined With Dabrafenib and Trametinib in People With Anaplastic Thyroid CancerThyroid Cancer | Anaplastic Thyroid Cancer | BRAF Gene Mutation | BRAF Mutation-Related TumorsUnited States
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Rana McKay, MDUniversity of California, San Diego; AstraZenecaRecruitingProstate Cancer | BRCA1 Mutation | BRCA2 Mutation | Prostatic Adenocarcinoma | High-Risk CancerUnited States
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AlexionCompletedWilson DiseaseUnited States, New Zealand, United Kingdom
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University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI); Columbia University; The Cleveland... and other collaboratorsRecruitingAmyloidosis, Familial | Amyloidosis, Hereditary | Amyloidosis Cardiac | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin Gene MutationUnited States
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Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
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The University of QueenslandTelethon Kids InstituteCompletedBronchiectasis | Cystic FibrosisAustralia, New Zealand
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PfizerCompletedSolid Tumors Harboring a BRAF V600 MutationUnited States, France, Italy, Singapore, Australia, Spain, Switzerland, Canada, Belgium
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Columbia UniversityLudwig-Maximilians - University of Munich; Moorfields Eye Hospital NHS Foundation... and other collaboratorsRecruitingRetinitis Pigmentosa Associated With CNGB1 MutationsUnited States, France, Germany, United Kingdom
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Blueprint Medicines CorporationActive, not recruitingNeoplasms | Neoplasms by Histologic Type | Lung Diseases | Neoplasms by Site | Adenocarcinoma | Carcinoma | Carcinoma, Non-Small-Cell Lung | Respiratory Tract Neoplasms | Carcinoma, Bronchogenic | Bronchial Neoplasms | Metastatic Lung Cancer | Antineoplastic Agents | Brain Metastases | Lung Neoplasm Malignant | EGFR... and other conditionsUnited States, Canada, Korea, Republic of, Japan, Taiwan
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Baxalta now part of ShireCompletedAlpha 1-Antitrypsin DeficiencyNew Zealand, Australia
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BiogenIonis Pharmaceuticals, Inc.Active, not recruitingALS Caused by Superoxide Dismutase 1 (SOD1) MutationUnited States, Canada, Italy, Belgium, New Zealand, Japan, France, Germany, United Kingdom
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Otto Bock Healthcare Products GmbHHanger Clinic: Prosthetics & OrthoticsActive, not recruitingLower Limb Amputation Above Knee (Injury) | Lower Limb Amputation Knee | Congenital Amputation of Lower LimbUnited States
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New York State Psychiatric InstituteNational Institute of Mental Health (NIMH)CompletedBorderline Personality DisorderUnited States
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Murdoch Childrens Research InstituteRoyal Children's HospitalCompletedPrimary Immunodeficiency | Invasive Pneumococcal Disease, Protection Against | Invasive Pneumococcal Disease, Recurrent Isolated, 1 | Invasive Pneumococcal Disease, Recurrent Isolated, 2Australia, New Zealand
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ReCode TherapeuticsRecruitingPrimary Ciliary DyskinesiaUnited Kingdom, United States, Australia, New Zealand
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Arrowhead PharmaceuticalsTerminatedCystic Fibrosis, PulmonaryAustralia, New Zealand
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PfizerMedivation, Inc.; Myriad Genetic Laboratories, Inc.TerminatedBreast Neoplasms | BRCA 1 Gene Mutation | BRCA 2 Gene MutationUnited States, Spain, United Kingdom, Germany, France
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AstraZenecaCompletedEGFR Mutation Status in aNSCLC PatientsKorea, Republic of, Russian Federation, Malaysia, China, Australia, Taiwan, Thailand, Indonesia, Singapore
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Sebastian BauerHannover Medical School; University Hospital Tuebingen; Universitätsmedizin Mannheim and other collaboratorsUnknownGIST, Malignant | KIT Gene Mutation | KIT Exon 13 MutationGermany
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)CompletedAlpha 1-Antitrypsin DeficiencyAustralia, New Zealand
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Recursion Pharmaceuticals Inc.RecruitingSolid Tumor | APC Gene Mutation | AXIN1 Gene MutationUnited States
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PfizerTerminatedDilated Cardiomyopathy | Lamin A/C Gene MutationUnited States, Spain, Canada, Belgium, Italy, Argentina, Mexico, Netherlands, Norway, United Kingdom
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VA Office of Research and DevelopmentRecruitingChronic Pain | Lower Limb Amputation | Phantom Pain | Upper Limb Amputation | Phantom Limb Pain After AmputationUnited States
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AstraZenecaNo longer available
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PfizerTerminatedHemophilia AUnited States, New Zealand
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D3 Bio (Wuxi) Co., LtdRecruitingAdvanced Solid Tumors With MAPK Pathway MutationsAustralia, China, United States
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CSL LimitedCompleted
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Lassen Therapeutics 1 PTY LTDRecruitingThyroid Eye Disease | Pulmonary FibrosisAustralia, New Zealand, Hong Kong
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HutchmedRecruitingIsocitrate Dehydrogenase Gene MutationSpain, United States
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VA Office of Research and DevelopmentRutgers University; University of Rhode IslandRecruitingAmputation, Lower LimbUnited States
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Boston Children's HospitalBoston Medical Center; National Human Genome Research Institute (NHGRI); The... and other collaboratorsRecruitingGenetic Predisposition to Disease | Genetics Disease | Genetics/Birth DefectsUnited States
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NYU Langone HealthWithdrawnAmputation, Traumatic | Finger InjuriesUnited States
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AstraZenecaMerck Sharp & Dohme LLC; Myriad Genetic Laboratories, Inc.Active, not recruitingBreast Cancer Metastatic | BRCA 1 Gene Mutation | BRCA 2 Gene MutationItaly, Spain, United States, Czechia, Romania, France, Korea, Republic of, United Kingdom, Hungary, Japan, Peru, Poland, Russian Federation, Turkey, China, Taiwan, Bulgaria, Switzerland, Mexico
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PfizerMedivation, Inc.CompletedBreast Neoplasms | BRCA 1 Gene Mutation | BRCA 2 Gene MutationKorea, Republic of, United States, Australia, Spain, Belgium, France, Ireland, Taiwan, Poland, Germany, Israel, Brazil, United Kingdom, Italy, Russian Federation, Ukraine
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Incyte CorporationTerminatedAdvanced or Metastatic Solid Tumors | FGFR Mutations | FGFR TranslocationsUnited States
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Calithera Biosciences, IncTerminatedNon-Small Cell Lung Cancer | Non-squamous Non-small-cell Lung Cancer | Non-Squamous Non-Small Cell Neoplasm of Lung | KEAP1 Gene Mutation | NRF2 Gene Mutation | NFE2L2 Gene MutationUnited States
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingMELAS or m.3243 A>G Mitochondrial DNA Mutation CarrierUnited States
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OnKure, Inc.Active, not recruitingMelanoma | NRAS Gene Mutation | RAS MutationUnited States
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Intellia TherapeuticsActive, not recruitingHereditary AngioedemaFrance, New Zealand, Germany, United Kingdom, Netherlands, Australia