- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Genetic Mutations in Austria
Total 1153 results
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada, United Kingdom, Australia, Spain, Germany, Italy, Austria, Belgium, Denmark
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BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Turkey, United Kingdom, Germany, Netherlands, Slovakia, Austria, Belgium, Czechia
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ArriVent BioPharma, Inc.Allist Pharmaceuticals, Inc.RecruitingAdvanced Non-Small Cell Lung Cancer | Metastatic Non-Small Cell Lung Cancer | EGFR Exon 20 MutationsUnited States, Australia, Spain, France, Italy, China, Japan, Korea, Republic of, Malaysia, Netherlands, Philippines, Singapore, Taiwan, Thailand, Brazil, Israel, United Kingdom, Mexico
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ShireCompletedFabry DiseaseUnited States, United Kingdom, Australia, Czechia, Finland, Paraguay, Poland, Slovenia
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AmgenActive, not recruitingAtopic DermatitisKorea, Republic of, United States, Turkey, Hong Kong, United Kingdom, Australia, Brazil, Canada, Argentina
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Regeneron PharmaceuticalsSanofiTerminatedAtopic DermatitisUnited States, Hungary, Korea, Republic of, Germany, Japan, Poland, Australia, Canada, Czechia, Spain, United Kingdom
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PfizerCompletedDermatitis, AtopicUnited States, Hungary, Canada, Germany, Australia, Czechia, Poland, United Kingdom
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TakedaEnrolling by invitationAlpha1-Antitrypsin DeficiencyUnited Kingdom, Germany, United States, Austria, Portugal
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Alexion PharmaceuticalsCompletedWilson DiseaseUnited States, Germany, Austria, Poland, United Kingdom
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Arcutis Biotherapeutics, Inc.CompletedAtopic Dermatitis EczemaUnited States, Canada
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Regeneron PharmaceuticalsSanofiCompletedDermatitis, AtopicUnited States, France, Poland, United Kingdom, Germany, Hong Kong, Canada, Korea, Republic of, Italy, Lithuania, Sweden
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SanofiRecruitingDermatitis AtopicNorway, Spain, Argentina, Israel, Greece, United States, Australia, Brazil, Canada, China, Colombia, Denmark, France, Italy, Japan, Korea, Republic of, Mexico, Netherlands, Portugal, Russian Federation
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Kowa Research Institute, Inc.CompletedFuchs' Endothelial Corneal DystrophyUnited States, Australia, Germany, Spain, Denmark
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Flatley Discovery Lab LLCCompletedCystic FibrosisUnited Kingdom, Australia, Germany, Czechia
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TakedaCompletedHereditary Angioedema (HAE)France, Germany, Austria, Greece
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PfizerCompletedHyperlipidemia | Hypercholesterolemia, FamilialAustralia, Canada, United States, France, South Africa, Sweden, Norway, Denmark, Iceland
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States, Canada, Australia, United Kingdom, Germany, Ireland, Israel, Sweden
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SanofiRecruitingDermatitis AtopicIsrael, Chile, Australia, United States, France, Canada, Germany, Korea, Republic of, Taiwan, China, Brazil, Poland
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Zynerba Pharmaceuticals, Inc.Completed22Q Deletion SyndromeUnited States, Australia
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisBelgium, Spain, Australia, Canada
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Bellus Health IncCompletedAtopic Dermatitis | Chronic PruritusUnited States, Canada
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TakedaTakeda Development Center Americas, Inc.RecruitingAlpha1-Antitrypsin DeficiencyUnited States, Belgium, Switzerland, Canada, Australia, Germany, United Kingdom, Austria, France, Spain, Portugal, Italy, Poland, Brazil
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AlexionCompletedWilson DiseaseUnited States, Germany, Austria, Poland, United Kingdom
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Cara Therapeutics, Inc.CompletedPruritus | Atopic DermatitisUnited States, Canada
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Eli Lilly and CompanyIncyte CorporationCompletedAtopic DermatitisBelgium, Netherlands, Japan, Spain, Switzerland, United Kingdom, Germany, France, Austria, Russian Federation, Poland, Italy, Brazil, Finland
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, Canada, China, France, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, Italy, Japan, South Africa, Spain, Taiwan
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AnaptysBio, Inc.RecruitingAtopic Dermatitis EczemaGeorgia, United States, Australia, Canada, Czechia, New Zealand, Poland
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AbbVieActive, not recruitingAtopic DermatitisUnited States, Australia, Belgium, Bulgaria, Canada, China, Denmark, France, Germany, Hungary, Italy, Korea, Republic of, Mexico, Netherlands, Poland, Portugal, Puerto Rico, Romania, Slovakia, South Africa, Spain, Sweden, Switzerland, Taiwa... and more
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden
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BioMarin PharmaceuticalCompletedMPS VIUnited States, Australia, France, Brazil, Germany, Portugal, United Kingdom
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Baxalta now part of ShireAmerican Thrombosis and Hemostasis Network; UDC Rare Bleeding and Clotting...CompletedProtein C DeficiencyUnited States, United Kingdom, Germany, Italy, Netherlands, Austria
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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Wuerzburg University HospitalCompletedCystic FibrosisUnited States, Austria, Canada, France, Germany, Netherlands, Switzerland, United Kingdom
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Eli Lilly and CompanyDermira, Inc.Active, not recruitingAtopic DermatitisUnited States, Spain, Canada, France, Korea, Republic of, Taiwan, Australia, Germany, Bulgaria, Estonia, Latvia, Lithuania, Mexico, Poland, Singapore, Ukraine
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Sydney Children's Hospitals NetworkJohns Hopkins University; Children's Hospital of Philadelphia; University of... and other collaboratorsUnknownCharcot-Marie-Tooth DiseaseUnited States, Australia, Italy
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BayerNot yet recruitingAdvanced Non-small Cell Lung Cancer | HER2 MutationUnited States, China, Korea, Republic of, Belgium, Hong Kong, Japan, Taiwan, Denmark, Germany, Israel, Poland, Italy, United Kingdom, Bulgaria, Czechia, Portugal, Switzerland, Greece, Turkey, Romania, Sweden, France, Singapore, Mexico, ... and more
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LEO PharmaTerminatedAtopic DermatitisUnited States, Netherlands, United Kingdom, France, Canada, Ireland, Austria, Germany, Poland
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Baxalta now part of ShireCompletedHemophilia AUnited States, Spain, Netherlands, Australia, Czechia, Korea, Republic of, Poland, Germany, Taiwan, Israel, Ukraine, United Kingdom, Malaysia, Japan, Austria, Switzerland, Sweden, Bulgaria, Lithuania, Romania
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Boehringer IngelheimCompletedCystic FibrosisUnited States, Australia, Austria, Belgium, Canada, Czech Republic, France, Germany, Hungary, Ireland, Israel, Italy, Poland, Portugal, Russian Federation, Slovakia, South Africa, Spain, Switzerland, United Kingdom
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OctapharmaRecruitingCongenital Antithrombin DeficiencySpain, Italy, United States, Serbia, France, Hungary, Austria, Germany, United Kingdom, Israel
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AmgenTerminatedOsteogenesis Imperfecta (OI)Canada, Czechia, Spain, United Kingdom, United States, Italy, Hungary, Australia, Belgium, France, Germany, Poland
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ShireCompletedHereditary Angioedema (HAE)United States, Canada, Australia, Austria, Colombia, Germany, Hungary, Israel, Italy, Spain
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Ultragenyx Pharmaceutical IncTerminatedGlucose Transporter Type 1 Deficiency SyndromeUnited States, Spain, Denmark, United Kingdom, Australia
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, China, Denmark, France, Israel, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, South Africa, Spain, Taiwan, Hungary, Italy
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Tyra Biosciences, IncRecruitingSolid Tumor | Bladder Cancer | Advanced Solid Tumor | Urothelial Carcinoma | Metastatic Urothelial Carcinoma | Solid Tumor, Adult | FGFR3 Gene Mutation | Urinary Tract Cancer | Locally Advanced Urothelial Carcinoma | Advanced Urothelial Carcinoma | Non-muscle-invasive Bladder Cancer | FGFR3 Gene Alteration | Urinary... and other conditionsAustralia, United States, France, Spain
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Galapagos NVCompletedCystic FibrosisUnited Kingdom, Australia, Ireland, Germany, Czech Republic
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Otsuka Pharmaceutical Europe LtdUnknownAutosomal Dominant Polycystic Kidney DiseaseSpain, United Kingdom, Germany, France, Belgium, Switzerland, Austria
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Vyne Therapeutics Inc.CompletedPruritus | Atopic DermatitisUnited States
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Friedreich's Ataxia Research AllianceRecruitingFriedreich AtaxiaUnited States, Canada, New Zealand, Australia, France, Austria, Belgium, Brazil, Czechia, Germany, Greece, Ireland, Italy, Spain, United Kingdom, India, Netherlands
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Skin Neoplasm | Nodular Basal Cell Carcinoma of SkinAustralia