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Clinical Trials on Genetic Predisposition to Disease in Colombia
Total 981 results
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University of Missouri-ColumbiaBioMarin PharmaceuticalEnrolling by invitationPhenylketonuriasUnited States
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Children's National Research InstituteGeorgetown UniversityWithdrawn
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Amneal Pharmaceuticals, LLCCompletedAtrophic Vaginitis Due to MenopauseUnited States
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McGill University Health Centre/Research Institute...Canadian Cystic Fibrosis Foundation; PHAC/CIHR Influenza Research Network; Ministere...Unknown
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Asklepion Pharmaceuticals, LLCRecruitingAcute Vaso Occlusive Crisis (VOC)United States
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Novartis PharmaceuticalsCompletedModerate to Severe Plaque-type PsoriasisGermany, United States, Belgium, Colombia, Spain, Estonia, Hungary, Japan, Lithuania, Taiwan, Australia, Korea, Republic of, Canada, Singapore, Italy, Israel, Sweden, Guatemala, United Kingdom, Argentina, France, Poland, Latvia, Iceland, Finla... and more
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Gamida Cell ltdTerminatedSickle Cell Disease | ThalassemiaFrance, United States
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Clinuvel Pharmaceuticals LimitedCompletedErythropoietic ProtoporphyriaNetherlands, Finland, France, Germany, Ireland, United Kingdom
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Cooperative International Neuromuscular Research...Carolinas Medical Center lead study siteCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2B (Miyoshi Myopathy, Dysferlin Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2I (FKRP-deficiency)United States
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Spark TherapeuticsCompletedHematologic Diseases | Hemophilia A | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Blood Coagulation Disorder | Factor VIII DeficiencyUnited States, Australia, Thailand, Canada
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Georgetown UniversityUnknown
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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Children's National Research InstituteBoston Children's HospitalRecruitingUrea Cycle DisordersUnited States
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University of Missouri-ColumbiaCompleted
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Cooperative International Neuromuscular Research...UnknownDuchenne Muscular DystrophyUnited States, Canada
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Cartiheal (2009) LtdActive, not recruitingCartilage or Osteochondral Defects in the Knee | Up to Moderate OsteoarthritisUnited States, Israel, Belgium, Italy, Serbia, Hungary, Poland, Romania
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Vanda PharmaceuticalsRecruitingSleep Disturbances in Smith-Magenis SyndromeUnited States
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OctapharmaCompletedSevere Hemophilia AUnited States, Bulgaria
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Scioderm, Inc.Amicus TherapeuticsTerminatedEpidermolysis BullosaPoland, Spain, Serbia, Netherlands, United States, Austria, Australia, Israel, Germany, France, United Kingdom, Lithuania
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University of British ColumbiaChildren's & Women's Health Centre of British Columbia; Vancouver Foundation; Circle of CareTerminatedExostoses, Multiple HereditaryCanada
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University of British ColumbiaSuspendedExostoses, Multiple HereditaryCanada
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Children's National Research InstituteRecruitingSickle Cell Disease | Cognitive Deficit in Attention | Attention DeficitUnited States
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University of British ColumbiaQueen's University; Montreal Heart Institute; Quebec Heart InstituteCompletedBrugada Syndrome | Long QT Syndrome | Arrhythmogenic Right Ventricular Cardiomyopathy | Catecholaminergic Polymorphic Ventricular Tachycardia | Inherited Cardiac ArrhythmiasCanada
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Immunovant Sciences GmbHCompletedGraves' OphthalmopathyCanada
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial Disorders | Mitochondrial Genetic Disorders | Disorder of Mitochondrial Respiratory Chain Complexes | Deletion and Duplication of Mitochondrial DNAUnited States, Canada
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University of British ColumbiaCompletedSickle Cell Disease | Beta-Thalassemia | Sickle Cell Trait | Sickle Cell-Beta Thalassemia | Sickle Cell-SS DiseaseCanada, Nepal
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Emory UniversityPatient-Centered Outcomes Research InstituteCompletedSickle Cell DiseaseUnited States
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University of British ColumbiaUnity Health Toronto; University of Calgary; Queen's University; Ottawa Heart Institute... and other collaboratorsCompletedCardiac Arrest | Early Repolarization Syndrome | Brugada Syndrome | Long QT Syndrome | Arrhythmogenic Right Ventricular Cardiomyopathy | Catecholaminergi Polymorphic Ventricular Tachycardia | Idiopathic VentricularFibrillationCanada
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Vancouver General HospitalNovo Nordisk A/STerminated
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Children's National Research InstitutePatient-Centered Outcomes Research Institute; Eunice Kennedy Shriver National... and other collaboratorsCompleted
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Canadian Fabry Research ConsortiumNova Scotia Health AuthorityRecruiting
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Children's National Research InstituteActelionCompletedSandhoff Disease | GM2 Gangliosidoses | Tay-SachsUnited States
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Children's National Research InstituteRecruitingViral Infection | Hematopoietic Stem Cell Transplantation (HSCT) | Primary Immunodeficiency Disorders (PID)United States
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University of ReginaProvincial Health Services Authority; Saskatchewan Health Authority - Regina...Not yet recruitingMental Health | Cystic Fibrosis in Children | Siblings | Internet-based InterventionCanada
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Cooperative International Neuromuscular Research...United States Department of DefenseCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Japan, Canada
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National Human Genome Research Institute (NHGRI)RecruitingInborn Errors of Metabolism | Methylmalonic Acidemia | Organic AcidemiaUnited States
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CENTOGENE GmbH RostockWithdrawnDefective MineralizationGermany, Sri Lanka, India
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Baxalta now part of ShireCompletedHemophilia BColombia, Bulgaria, Chile, Poland, Romania, Argentina, Brazil, Czechia, Russian Federation, Ukraine
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Bausch Health Americas, Inc.TerminatedModerate to Severe Plaque PsoriasisUnited States, Austria, France, Poland, Australia, Czechia, Canada, Hungary, Portugal, Spain, Netherlands
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Capricor Inc.RecruitingNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States
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University of British ColumbiaMHE CoalitionCompletedExostoses, Multiple HereditaryCanada
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Scioderm, Inc.Amicus TherapeuticsCompletedEpidermolysis BullosaItaly, Spain, Serbia, United States, Australia, Netherlands, Austria, Germany, Israel, Lithuania, France, United Kingdom, Poland
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University of British ColumbiaMedical University of Graz; Hospital de Clinicas de Porto AlegreUnknownMorquio B Disease | GM1 Gangliosidosis Type IIICanada
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States, Canada, Argentina, Australia, Israel, Italy
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ShireCompletedAngioedemaUnited States
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National Institute of Neurological Disorders and...CompletedLysosomal Storage DiseaseUnited States, France, Israel, Netherlands
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDown Syndrome | Subclinical HypothyroidismUnited States