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- US Clinical Trials Registry
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Clinical Trials on Genetic Screening in Netherlands
Total 796 results
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Jaeb Center for Health ResearchUsher 1F Collaborative; Marjorie C. Adams FoundationActive, not recruitingRetinal Degeneration | Retinitis Pigmentosa | Eye Diseases, HereditarySwitzerland, United States, Germany, Netherlands, Canada, France, Israel
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Ionis Pharmaceuticals, Inc.Active, not recruitingHereditary AngioedemaNetherlands, United States
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ReveraGen BioPharma, Inc.University of Pittsburgh; Newcastle University; European Union; Cooperative International...CompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, United Kingdom, Spain, Netherlands, Sweden, Czechia, Australia, Greece, Israel
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Novartis PharmaceuticalsTerminatedAtopic DermatitisUnited Kingdom, Germany, Russian Federation, Taiwan, Belgium, Netherlands, Japan, Finland, Slovakia, United States, Iceland, Canada, Poland
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ShireTerminatedSanfilippo Syndrome | Mucopolysaccharidosis (MPS)United States, United Kingdom, Spain, Germany, France, Italy, Netherlands
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC DeficiencyNetherlands, United States, Germany, Canada, Puerto Rico, United Kingdom
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Menarini International Operations Luxembourg SACompletedGoutPoland, Serbia, Germany, Italy, Netherlands, Romania
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Rhythm Pharmaceuticals, Inc.Active, not recruitingGenetic ObesityUnited States, Spain, Netherlands, Germany, United Kingdom, Canada, Israel, Greece
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CSL BehringCompletedSickle Cell DiseaseUnited States, United Kingdom, Netherlands
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SanofiActive, not recruitingDermatitis AtopicAustralia, United States, Argentina, Brazil, Canada, Colombia, France, Mexico, Netherlands
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Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Finland, Switzerland, Netherlands, Portugal
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Ferring PharmaceuticalsCompletedTurner's SyndromeCzech Republic, France, Netherlands
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Editas Medicine, Inc.CompletedEye Diseases | Retinal Degeneration | Eye Diseases, Hereditary | Vision Disorders | Blindness | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Netherlands, France, Germany
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisNetherlands, Italy, United Kingdom
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HomozygousGreece, Lebanon, Turkey, France, Canada, Malaysia, Netherlands, United States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophyKorea, Republic of, Chile, Taiwan, China, United States, United Kingdom, Netherlands, Spain, Australia, Norway, Russian Federation, Greece, Italy, Turkey, Mexico, Canada, Hong Kong, New Zealand, Ukraine
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ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
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BioMarin PharmaceuticalNo longer availableDuchenne Muscular DystrophyUnited States, Germany, United Kingdom, Japan, Netherlands, France, Spain, Korea, Republic of, Italy, Belgium, Taiwan, Argentina, Australia, Bulgaria, Czechia, Israel, Norway, Poland, Russian Federation, Turkey
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BayerUltragenix pharmaceuticalActive, not recruitingHemophilia ANetherlands, United States, Germany, United Kingdom, France, Bulgaria
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, Poland, Netherlands, Canada, Argentina, United Kingdom, Norway, Brazil, Czech Republic
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, United Kingdom, Belgium, France, Germany
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Bioverativ, a Sanofi companySwedish Orphan BiovitrumCompletedHemophilia BUnited States, Italy, Ireland, New Zealand, United Kingdom, Australia, Netherlands, Denmark, Poland, Sweden, France
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ItalfarmacoCromsourceEnrolling by invitationDuchenne Muscular DystrophySpain, United States, Canada, Belgium, France, Israel, Italy, Netherlands, Serbia, Germany, United Kingdom
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Kamada, Ltd.CompletedEmphysemaUnited Kingdom, Canada, Denmark, Germany, Ireland, Netherlands, Sweden
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Ultragenyx Pharmaceutical IncActive, not recruitingGlycogen Storage Disease Type IA | Von Gierke's Disease (GSD Type Ia)Netherlands, United States, Canada, Spain
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Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, Netherlands
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Novartis PharmaceuticalsTerminatedCystic Fibrosis | Allergic Bronchopulmonary AspergillosisUnited Kingdom, Germany, Belgium, Italy, Netherlands
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BayerMerck Sharp & Dohme LLCTerminatedEarly Signs of Efficacy Study With Riociguat in Adult Homozygous Delta F508 Cystic Fibrosis PatientsCystic FibrosisGermany, United States, France, Canada, Belgium, Netherlands, United Kingdom
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UCB Pharma SACompletedUnverricht-Lundborg DiseaseFrance, Italy, Sweden, Finland, Netherlands, Tunisia, Réunion
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PfizerCompletedPhase 1 Sickle CellUnited States, United Kingdom, Belgium, Netherlands, Italy
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CSL BehringActive, not recruitingHemophilia BUnited States, Belgium, Netherlands, Denmark, Germany, Ireland, Sweden, United Kingdom
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LEO PharmaCompletedAtopic DermatitisUnited States, Germany, Belgium, Canada, Spain, United Kingdom, Poland, Netherlands
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PfizerAvailableAtopic DermatitisTaiwan, United States, Australia, Austria, Belgium, Canada, Greece, Mexico, Netherlands, Russian Federation, Spain, Switzerland
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PedNet Haemophilia Research FoundationLund University HospitalRecruitingFactor IX Deficiency | Factor VIII DeficiencyNorway, Austria, Belgium, Canada, Czechia, Denmark, Finland, France, Germany, Greece, Ireland, Israel, Italy, Netherlands, Portugal, Spain, Sweden, Switzerland, United Kingdom
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Hoffmann-La RocheActive, not recruitingAngelman SyndromeUnited States, Spain, Netherlands, Italy
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Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
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QLT Inc.CompletedLeber Congenital Amaurosis (LCA) | Retinitis Pigmentosa (RP)United States, Canada, Denmark, Germany, Netherlands, Switzerland, United Kingdom
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SangartWithdrawnSickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Anemia | Hemoglobin SC Disease | Sickle Cell Disorders | Sickle Cell Hemoglobin C DiseaseFrance, United Kingdom, Netherlands, Turkey, Bahrain, Belgium, Brazil, Lebanon, Qatar
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Boehringer IngelheimRecruitingBronchiectasis | Cystic FibrosisUnited States, Spain, Belgium, Netherlands, Germany, France, Italy
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsSaudi Arabia, Algeria, Turkey, Germany, Poland, Netherlands, Italy, Belgium, South Africa, United Kingdom, Sweden, Austria, Portugal, France, Czech Republic, Venezuela
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Australia, Austria, Netherlands, Taiwan, Ukraine
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Wyeth is now a wholly owned subsidiary of PfizerWithdrawnHemophilia AItaly, United States, Netherlands, United Kingdom, Germany, New Zealand, Belgium, France
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REGENXBIO Inc.National Heart, Lung, and Blood Institute (NHLBI)TerminatedHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Italy, Netherlands
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Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
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Galapagos NVCompletedCystic FibrosisBelgium, Bulgaria, Germany, Greece, Netherlands, Serbia, Sweden, United Kingdom
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Hemab ApSRecruitingGlanzmann ThrombastheniaUnited States, Belgium, France, Italy, Netherlands, United Kingdom
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Hoffmann-La RocheCompletedAtopic DermatitisUnited States, Korea, Republic of, Canada, United Kingdom, Germany, Australia, Poland, Finland, France, Spain, Switzerland, Czechia, Netherlands, Taiwan
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AstraZenecaCompletedFamilial HypercholesterolemiaUnited States, Spain, Netherlands, Norway, Canada
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University Medical Center GroningenNot yet recruitingADPKDNetherlands, United Kingdom, Belgium, Germany, France, Spain
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden