- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Genetic Disease, X-Linked
Total 15138 results
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University of MessinaCompleted
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Cedars-Sinai Medical CenterCompleted
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Cooperative International Neuromuscular Research...United States Department of DefenseTerminated
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Cedars-Sinai Medical CenterMuscular Dystrophy AssociationCompleted
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Rigshospitalet, DenmarkGlostrup University Hospital, CopenhagenCompletedBecker Muscular DystrophyDenmark
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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Santhera PharmaceuticalsCompletedDuchenne Muscular DystrophyBelgium
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Assistance Publique - Hôpitaux de ParisCompletedMuscular Dystrophy, DuchenneFrance
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National Center for Research Resources (NCRR)Children's National Research InstituteCompletedMuscular Dystrophy, DuchenneUnited States
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States, Canada, Argentina, Australia, Israel, Italy
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Hasan Kalyoncu UniversityNot yet recruitingHemophilia A | Hemophilia B | HemophiliaTurkey
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Assiut UniversityNot yet recruitingHemophilia A | Hemophilia B
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BUnited States, Italy, Spain, Taiwan, Australia, Belgium, United Kingdom, France, Germany, India, South Africa, Canada, Poland, Armenia, Turkey
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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Regeneron PharmaceuticalsRecruitingHemophilia BUnited States, Germany, United Kingdom, Canada
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BBulgaria, United States, United Kingdom, Russian Federation, Switzerland
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St. Jude Children's Research HospitalChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingHemophilia BUnited States, United Kingdom
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Swedish Orphan BiovitrumIQVIA Pvt. LtdTerminatedHemophilia A | Hemophilia BBulgaria, Croatia, Czechia, France, Hungary, Ireland, Italy, Romania, Slovenia, Spain, United Kingdom
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Freeline TherapeuticsTerminatedHemophilia BUnited States, United Kingdom
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University College, LondonTerminatedHemophilia BIreland, United Kingdom, Italy, United States
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CSL BehringCompletedHemophilia BGermany, Denmark, Netherlands
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, Canada, China, France, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, Italy, Japan, South Africa, Spain, Taiwan
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, China, Denmark, France, Israel, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, South Africa, Spain, Taiwan, Hungary, Italy
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Sangamo TherapeuticsTerminated
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Catalyst BiosciencesCompletedHemophilia BSouth Africa
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Baxalta now part of ShireCompletedHemophilia BKorea, Republic of
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Baxalta now part of ShireCompleted
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Medexus Pharma, Inc.CompletedHemophilia BUnited States, France, United Kingdom, India, Israel, Italy, Poland
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Baxalta now part of ShireCompletedHemophilia A | Hemophilia BUnited States
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ISU Abxis Co., Ltd.Catalyst BiosciencesCompletedHemophilia BKorea, Republic of
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BayerCompletedHemophilia A | Hemophilia BUkraine, United Kingdom, Bulgaria, Germany, Japan
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Royal Free Hospital NHS Foundation TrustUnknown
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Nationwide Children's HospitalCompleted
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CSL BehringCompletedHemophilia BGermany, Australia, Italy, Israel, Czech Republic, Spain, France, Canada, Austria, Russian Federation
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PfizerCompletedHemophilia BCanada, Singapore, Turkey, Croatia, Korea, Republic of, Mexico, Poland, Bulgaria, Malaysia
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CSL BehringCompletedHemophilia BSpain, Italy, France, Germany, Austria, Israel
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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NightstaRx Ltd, a Biogen CompanyCompletedX-Linked Retinitis PigmentosaUnited States, France, United Kingdom, Finland, Netherlands, Germany, Canada
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University Hospital, MontpellierAgence de La BiomédecineActive, not recruitingFragile X Syndrome | Huntington Disease | Myotonic Dystrophy 1France
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Assistance Publique - Hôpitaux de ParisCompletedHypohidrotic Ectodermal DysplasiaFrance
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SwanBio Therapeutics, Inc.RecruitingAMN | AMN Gene Mutation | X-ALDNetherlands, United States
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States
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Assiut UniversityNot yet recruiting
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National Institute of Allergy and Infectious Diseases...Completed
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Cyprium Therapeutics, Inc.Enrolling by invitation
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Eunice Kennedy Shriver National Institute of Child...Completed