- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Genetic Disease, X-Linked
Total 15138 results
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Central Hospital, Nancy, FranceCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...Terminated
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Sheba Medical CenterUnknown
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Maastricht University Medical CenterCompleted
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Faculdades Metropolitanas UnidasUniversity of Sao PauloCompleted
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityCompletedRett Syndrome
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Eunice Kennedy Shriver National Institute of Child...UnknownRett SyndromeUnited States
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West China HospitalRecruiting
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Massachusetts General HospitalNational Institutes of Health (NIH)UnknownHealthy | Fragile X SyndromeUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingGranuloma | Granulomatous Disease, Chronic | Leukocyte Disease | Genetic Disease, X-Linked | Genetic Disease, InbornUnited States
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruiting
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
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Children's Hospital of Fudan UniversityRecruiting
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Tetra Discovery PartnersEnrolling by invitationFragile X SyndromeUnited States
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Healx LimitedWithdrawnFragile X SyndromeUnited States, Australia
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Children's Hospital Medical Center, CincinnatiCompleted
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Université de SherbrookeFRAXA Research FoundationCompleted
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NovartisCompletedFragile X SyndromeFrance, Italy, Switzerland
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Neuren Pharmaceuticals LimitedCompleted
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Randi J. Hagerman, MDCompleted
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Indiana UniversityIndiana Clinical and Translational Sciences InstituteCompleted
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Indiana University School of MedicineCompletedFragile X SyndromeUnited States
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Hoffmann-La RocheCompleted
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Novartis PharmaceuticalsTerminatedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, Denmark, Italy, Netherlands, Spain, Sweden, United Kingdom, France
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Stanford UniversityNational Institute of Mental Health (NIMH); Autism SpeaksCompleted
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FRAXA Research FoundationFragile X Research Foundation of CanadaCompleted
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.SuspendedFragile X SyndromeUnited States
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NeuropharmCompleted
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University Hospital, Basel, SwitzerlandNovartisCompletedRett's SyndromeSwitzerland
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Children's Hospital of Fudan UniversityRecruiting
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, United Kingdom
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRecruiting
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... and other collaboratorsRecruiting
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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Edison Pharmaceuticals IncWithdrawn
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Anavex Life Sciences Corp.Completed
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompleted
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Neuren Pharmaceuticals Limitedrettsyndrome.orgCompleted
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUnknownRett SyndromeDenmark, Israel
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Rigshospitalet, DenmarkCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)CompletedRett SyndromeUnited States
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Edison Pharmaceuticals IncCompleted
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Boston Children's HospitalInternational Rett Syndrome FoundationCompleted
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The Cleveland ClinicTerminated
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationCompleted