- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetic Disease
Total 381248 results
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Novo Nordisk A/SCompletedNoonan Syndrome | Genetic DisorderSweden
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Tulane UniversityAllerganCompleted
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University of Colorado, DenverCompletedFocal Dermal Hypoplasia
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingLeukoencephalopathies | Genetic Disease | White Matter Disease | Ataxia, Cerebellar | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate ElevationUnited States
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Aga Khan University Hospital, PakistanCompletedBreast Cancer | Genetic Predisposition | BRCA Mutation | Occult CancerPakistan
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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University of UtahEnrolling by invitationTotal Joint Arthroplasty | Periprosthetic Joint InfectionsUnited States
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National Institute of Environmental Health Sciences...Massachusetts General HospitalRecruitingInfertility | Hypogonadism | Amenorrhea | Genetic DisorderUnited States
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Edimer PharmaceuticalsCompletedHypohidrotic Ectodermal DysplasiaUnited States
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Edimer PharmaceuticalsCompletedHypohidrotic Ectodermal DysplasiaUnited States
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Hospital Universitari Vall d'Hebron Research InstituteCompleted
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University of MiamiCompletedDermatochalasis | Eyelid DermatochalasisUnited States
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Ankara UniversityActive, not recruitingSudden Infant DeathTurkey
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Goldman, Butterwick, Fitzpatrick and GroffGalderma R&DNot yet recruitingSkin LaxityUnited States
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University of Texas Southwestern Medical CenterCompleted
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BTL Industries Ltd.Completed
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Apyx MedicalCompletedLax SkinUnited States
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Cynosure, Inc.CompletedSkin LaxityUnited States
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Northwestern UniversityWithdrawn
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R2 DermatologyCompleted
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Venus ConceptCompleted
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Ulthera, IncCompleted
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Ulthera, IncCompleted
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Ulthera, IncTerminatedSkin LaxityUnited States
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Rambam Health Care CampusIsrael Cancer AssociationWithdrawnBusulfan Pharmacokinetic Analysis | GST Genetic PolymorphismIsrael
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Edimer PharmaceuticalsCompletedEctodermal DysplasiaUnited States
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Assistance Publique - Hôpitaux de ParisCompletedAnkylosing SpondylitisFrance
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Fondation Ophtalmologique Adolphe de RothschildInstitut National de la Santé Et de la Recherche Médicale, FranceTerminated
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Novo Nordisk A/SCompletedPrader-Willi Syndrome | Genetic DisorderGermany, Denmark, Switzerland
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Galderma Brasil Ltda.Recruiting
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Goldman, Butterwick, Fitzpatrick and GroffSofwave Medical LTDRecruitingSkin LaxityUnited States
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InMode MD Ltd.CompletedSkin LaxityUnited States
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Apyx MedicalCompleted
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Botanee Group Co., Ltd.Completed
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Apyx MedicalActive, not recruiting
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BTL Industries Ltd.Completed
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University of Texas Southwestern Medical CenterCompleted
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Recros Medica, Inc.UnknownSkin LaxityUnited States
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Ulthera, IncCompleted
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Ulthera, IncCompleted
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Ulthera, IncCompleted
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Ulthera, IncCompleted
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Ulthera, IncCompletedSkin LaxityUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingPrimary Immune DeficiencyUnited States, Turkey
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Wright State UniversityOnset DermatologicsTerminatedKeratosis PilarisUnited States
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AOBiome LLCCompletedKeratosis PilarisUnited States
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Copenhagen University Hospital at HerlevUnknownDepression | Pathologic Processes | Heart Diseases | Cardiovascular Diseases | Congenital Abnormalities | Death | Death, Sudden | Arrhythmias, Cardiac | ADHD | Heart Arrest | Heart Defects, Congenital | Cardiovascular Abnormalities | Genetic Disease | Death, Sudden, Cardiac | Psychiatric Disorder | Genetic Syndrome | Long... and other conditionsDenmark