- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetics/Birth Defects in Canada
Total 2421 results
-
National Cancer Institute (NCI)TerminatedRecurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities | Adult Acute Myeloid Leukemia With Inv(16)(p13;q22) | Adult Acute Myeloid Leukemia With t(16;16)(p13;q22) | Adult Acute Myeloid Leukemia With t(8;21)(q22;q22) | Secondary Acute Myeloid Leukemia and other conditionsCanada
-
Mount Sinai Hospital, CanadaPrincess Margaret Hospital, CanadaActive, not recruitingAdult Soft Tissue SarcomaCanada, United States, Belgium
-
Ultragenyx Pharmaceutical IncCompletedOrnithine Transcarbamylase (OTC) DeficiencyUnited Kingdom, United States, Canada, Spain
-
Ottawa Hospital Research InstituteCanadian Institutes of Health Research (CIHR)RecruitingCovid19 | Acute Respiratory Distress SyndromeCanada
-
PfizerCompletedTransthyretin Amyloidosis | Transthyretin Gene MutationsUnited States, France, Spain, Taiwan, Israel, Korea, Republic of, Denmark, Canada, Netherlands, Japan, Sweden, Brazil, Mexico, Argentina, Portugal, Belgium, Bulgaria, Cyprus, Germany, Italy, Malaysia, Romania, Saudi Arabia, Turkey, United...
-
Children's Oncology GroupNational Cancer Institute (NCI)CompletedNeurotoxicity | Long-term Effects Secondary to Cancer Therapy in ChildrenUnited States, Canada
-
Vertex Pharmaceuticals IncorporatedCompletedCystic Fibrosis, Homozygous for the F508del CFTR MutationUnited States, France, Spain, Belgium, Canada, Austria, Australia, Germany, United Kingdom, Denmark
-
Vertex Pharmaceuticals IncorporatedCompletedCystic Fibrosis, Homozygous for the F508del CFTR MutationUnited States, Germany, Canada, Netherlands, Czech Republic, Italy, Ireland, Sweden, United Kingdom, Australia, France
-
AO Foundation, AO SpineCompletedSpinal DeformityUnited States, Turkey, Hong Kong, United Kingdom, China, Australia, Netherlands, Canada, Japan, Brazil, India, Israel, Pakistan, Spain
-
ShireTerminatedMetabolic Diseases | Brain Diseases | Central Nervous System Diseases | Nervous System Diseases | Demyelinating Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Lysosomal Storage Diseases | Lipid Metabolism Disorders | Sphingolipidoses | Hereditary Central Nervous System Demyelinating Diseases and other conditionsUnited States, Denmark, France, Argentina, Belgium, Brazil, Canada, Germany, Japan, Turkey
-
Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
-
ShireTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, France, Netherlands, Spain, Hungary, Italy, Canada, Poland, Japan, Germany
-
PfizerCompletedHuntington's DiseaseUnited States, Germany, United Kingdom, Canada, Poland
-
Novartis PharmaceuticalsCompletedType2 Diabetes | Familial Hypercholesterolemia | Atherosclerotic Cardiovascular Disease | Symptomatic AtherosclerosisGermany, United Kingdom, Netherlands, United States, Canada
-
Medivation, Inc.PfizerCompletedHuntington DiseaseGermany, Canada, United States, Denmark, United Kingdom, Australia, Sweden
-
Gilead SciencesCompletedCystic Fibrosis | Burkholderia InfectionsUnited States, Canada
-
Huntington Study GroupNational Institute of Neurological Disorders and Stroke (NINDS); National Human...UnknownHuntington DiseaseUnited States, Canada
-
Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaKorea, Republic of, Canada, United States, Australia, Japan, United Kingdom, Sweden
-
Enzyvant Therapeutics GmBHCompletedFarber Disease | Farber's Disease | Farber Lipogranulomatosis | Acid Ceramidase Deficiency | Ceramidase Deficiency | N-Laurylsphingosine Deacylase Deficiency | ASAH1 MutationUnited States, Egypt, Canada, Italy, Turkey, Argentina, Germany, India, Sweden
-
Otsuka Pharmaceutical Development & Commercialization...CompletedTic Disorder | Tourette's DisorderUnited States, Canada, Hungary, Italy
-
Gaziler Physical Medicine and Rehabilitation Education...CompletedCarpal Tunnel SyndromeTurkey
-
Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, France, Netherlands, Spain, United Kingdom, Belgium, Bulgaria, Canada, Denmark, Germany, Israel, Italy, Poland, Turkey
-
Insmed IncorporatedCompletedPseudomonas Aeruginosa InfectionFrance, Poland, United Kingdom, Germany, Spain, Belgium, Bulgaria, Denmark, Greece, Canada, Netherlands, Hungary, Italy, Ireland, Sweden, Slovakia, Austria, Serbia
-
SanofiActive, not recruitingGaucher's Disease Type III | Gaucher's Disease Type ICanada, Argentina, France, Italy, Japan, Russian Federation, Spain, Sweden, Turkey, United Kingdom
-
University of OklahomaColumbia University; Pontificia Universidad Catolica de Chile; University of... and other collaboratorsRecruitingPremature BirthUnited States, Canada, Chile
-
Vision Research FoundationWithdrawnRetinopathy of PrematurityUnited States, Canada
-
Boston Children's HospitalAgios Pharmaceuticals, Inc.CompletedPyruvate Kinase Deficiency | Congenital Non-Spherocytic Hemolytic AnemiaUnited States, Germany, Canada, Czechia, Italy, Netherlands
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AFrance, United States, Switzerland, Malaysia, Brazil, Canada, Japan, United Kingdom, Israel, Portugal, Ukraine, Greece, Lithuania, Puerto Rico, Turkey, Italy
-
Janssen Research & Development, LLCActive, not recruitingHemolytic Disease of the Fetus and NewbornUnited States, Canada, Netherlands, Belgium, Germany, Spain, Sweden, United Kingdom, Australia
-
Teva Branded Pharmaceutical Products R&D, Inc.Nuvelution TS Pharma, Inc.TerminatedTourette SyndromeUnited States, Argentina, Australia, Canada, Colombia, Denmark, Hungary, Italy, Korea, Republic of, Mexico, Poland, Russian Federation, Serbia, Spain, Ukraine
-
Teva Branded Pharmaceutical Products R&D, Inc.Completed
-
Massachusetts General HospitalNational Institute of Neurological Disorders and Stroke (NINDS); University...TerminatedHuntington's DiseaseUnited States, Australia, Canada
-
Ionis Pharmaceuticals, Inc.RecruitingHereditary AngioedemaUnited States, Puerto Rico, Belgium, Bulgaria, Canada, France, Germany, Israel, Italy, Netherlands, Poland, Spain, Turkey, United Kingdom
-
Sage TherapeuticsRecruitingHuntington's DiseaseUnited States, Australia, Canada, United Kingdom
-
PrileniaTerminatedHuntington's DiseaseUnited States, Australia, Austria, Canada, France, Germany, Italy, Netherlands, Poland, Russian Federation, United Kingdom
-
ShireCompletedHunter Syndrome | Mucopolysaccharidosis II (MPS II)United States, France, United Kingdom, Germany, Sweden, Spain, Brazil, Canada, Italy, Romania
-
Neurocrine BiosciencesHuntington Study GroupActive, not recruitingChorea, HuntingtonUnited States, Canada
-
LMU KlinikumSeventh Framework Programme; NBIA AllianceRecruitingNeurodegeneration With Brain Iron Accumulation (NBIA) | Pantothenate Kinase-associated Neurodegeneration (PKAN) | Aceruloplasminemia | Beta-Propeller Protein-Associated Neurodegeneration (BPAN) | Mitochondrial Membrane Protein Associated Neurodegeneration (MPAN) | Fatty Acid Hydroxylase-associated... and other conditionsCanada, Czechia, Germany, Italy, Netherlands, Poland, Serbia, Spain
-
Unity Health TorontoRecruitingAcute Respiratory Distress Syndrome (ARDS)Canada, Spain, Italy, Brazil
-
ShireTakeda Development Center Americas, Inc.CompletedHereditary Angioedema (HAE)Canada, United States, Puerto Rico
-
Teva Branded Pharmaceutical Products R&D, Inc.CompletedHuntington's DiseaseUnited States, Canada, Czechia, Germany, Italy, Netherlands, Portugal, Russian Federation, Spain, United Kingdom
-
Emalex Biosciences Inc.CompletedTourette SyndromeUnited States, Poland, France, Canada, Germany
-
PfizerCompletedPolycystic Kidney, Autosomal DominantUnited States, Canada, Australia, Sweden, Spain, Poland, Korea, Republic of, Switzerland, United Kingdom, Moldova, Republic of, Italy, Czech Republic, Hungary, Lithuania, Romania, Slovakia, Turkey
-
Novartis PharmaceuticalsCompletedCancerFrance, Australia, United States, Canada, United Kingdom
-
Grifols Therapeutics LLCActive, not recruitingPulmonary Emphysema in Alpha-1 PI DeficiencyUnited States, Australia, Denmark, New Zealand, Estonia, Poland, Russian Federation, Sweden, Brazil, Canada, France, Finland
-
TakedaWithdrawnMetachromatic Leukodystrophy (MLD)Spain
-
TakedaTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, Spain, Netherlands, Hungary, Italy, Canada, Germany, France, Japan, Poland
-
National Cancer Institute (NCI)Multicenter Hemophilia Cohort StudyCompletedHepatocellular Carcinoma | Non-Hodgkin Lymphoma | Liver DecompensationUnited States, Germany, Italy, Brazil, Canada, France, Greece, Sweden
-
PrileniaActive, not recruitingHuntington DiseaseUnited States, Austria, Canada, Czechia, France, Germany, Italy, Netherlands, Poland, Spain, United Kingdom
-
Radiation Therapy Oncology GroupNational Cancer Institute (NCI); NRG OncologyCompletedNeurotoxicity | Cognitive/Functional Effects | Psychosocial Effects of Cancer and Its Treatment | Adult Diffuse Astrocytoma | Adult Mixed Glioma | Adult Oligodendroglioma | SeizureUnited States, Canada