- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetics/Birth Defects in Canada
Total 2421 results
-
Massachusetts General HospitalNational Center for Complementary and Integrative Health (NCCIH); University...TerminatedHuntington's DiseaseUnited States, Canada, New Zealand, Australia
-
HP Therapeutics FoundationHuntington Study GroupUnknownHuntington DiseaseUnited States, Canada, Australia
-
Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Canada, Japan, France, Denmark
-
Assaf-Harofeh Medical CenterRecruitingPremature Birth | Twin Pregnancy With Antenatal Problem | Twin Pregnancy, Antepartum Condition or Complication | Twin Dichorionic Diamniotic Placenta | Twin Monochorionic Monoamniotic Placenta | Twin; Pregnancy, Affecting Fetus or Newborn | Prenatal DisorderBelgium, Canada, Germany, Israel, Spain, United Kingdom
-
AMAG Pharmaceuticals, Inc.ResearchPoint GlobalCompletedPreterm BirthUnited States, Spain, Russian Federation, Canada, Bulgaria, Czechia, Hungary, Italy, Ukraine
-
BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IV AUnited States, Canada, France, Taiwan, Argentina, Colombia, Spain, Turkey, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, United Kingdom, Germany, Norway, Portugal, Italy, Qatar
-
Pharnext S.C.A.Premier Research Group plc; Eurofins Optimed; Synteract HCR (Syneos Health); Gr... and other collaboratorsActive, not recruitingCharcot-Marie-Tooth Disease, Type IAUnited States, Belgium, Canada, France, Netherlands, Spain, United Kingdom
-
SanofiRecruitingFabry DiseaseChina, Finland, Germany, Norway, United Kingdom, United States, Denmark, Austria, Greece, Romania, Argentina, Brazil, Canada, Japan, Mexico, Poland, Italy, France, Turkey, Australia, Switzerland
-
Rhythm Pharmaceuticals, Inc.CompletedBardet Biedl Syndrome (BBS) | Alström Syndrome (AS)United States, United Kingdom, France, Canada, Puerto Rico, Spain
-
Target PharmaSolutions, Inc.RecruitingPsoriasis | Atopic Dermatitis | Vitiligo | Hidradenitis Suppurativa | Alopecia Areata | Chronic Spontaneous UrticariaUnited States, Spain, Canada, Germany
-
Otsuka Pharmaceutical Development & Commercialization...CompletedTourette's DisorderUnited States, Germany, Taiwan, Korea, Republic of, Mexico, Hungary, Bulgaria, Ukraine, Romania, Canada
-
BioCryst PharmaceuticalsCompletedHereditary Angioedema | HAEUnited States, Austria, Canada, Czechia, France, Germany, Hungary, North Macedonia, Romania, Spain, United Kingdom
-
FFF EnterprisesOMRIX BiopharmaceuticalsCompletedImmunologic Deficiency SyndromesUnited States, Canada
-
CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Germany, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom
-
Sera Prognostics, Inc.High Risk Pregnancy Center, Las Vegas, NevadaActive, not recruitingPreterm Birth | Preterm LaborUnited States
-
Infinity Pharmaceuticals, Inc.CompletedGastrointestinal Stromal Tumors | Soft Tissue SarcomasUnited States, Canada
-
Genzyme, a Sanofi CompanyRecruitingMucopolysaccharidosis I (MPS I)Croatia, United States, Argentina, Australia, Belgium, Brazil, Canada, Denmark, France, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Lebanon, Malaysia, Netherlands, Pakistan, Philippines, Poland, Saudi Arabia, Singapore, Slovaki... and more
-
Zimmer BiometActive, not recruitingOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Correction of Functional Deformity | RevisionKorea, Republic of, Canada, United Kingdom, Austria
-
Ankara City Hospital BilkentCompletedCarpal Tunnel Syndrome | Ultrasound Imaging | Electromyography | Low-Level Laser TherapyTurkey
-
Novartis PharmaceuticalsCompletedPhiladelphia Chromosome Positive Chronic Myelogenous LeukemiaGermany, Canada, France, Spain, Italy
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Netherlands, Spain, Switzerland, Taiwan, Turkey, United Kingdom, Croatia, Germany, Brazil, France, Japan, Australia, Hungary, Israel, Korea, Republic of, Lithuania, Portugal, Ukraine, Greece, Italy, Denmark, Norway, Canada and more
-
ShireCompletedHereditary Angioedema (HAE)United States, United Kingdom, Germany, Canada, Italy, Jordan, Puerto Rico
-
Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedCoronary Artery Disease | Heterozygous Familial HypercholesterolemiaUnited States, Canada
-
Sharp HealthCareChildren's Hospital of Philadelphia; University of South Florida; Yale University and other collaboratorsNot yet recruitingPremature Birth | Antibiotics | NeurodevelopmentUnited States, Canada
-
AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
-
CSL BehringActive, not recruitingHereditary AngioedemaAustralia, Canada, United States, New Zealand, Germany, Hong Kong, Netherlands, Taiwan, Czechia, Israel, Hungary, Japan, Russian Federation, Spain
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Spain, Australia, France, Thailand, Italy, Malaysia, Austria, Greece, Japan, Taiwan, Canada, Israel, Algeria, Argentina, Bulgaria, Germany, Romania
-
PrileniaHuntington Study Group; European Huntington's Disease NetworkCompletedHuntington's DiseaseUnited States, Australia, Austria, Canada, Denmark, France, Germany, Italy, Netherlands, Poland, Russian Federation, United Kingdom
-
Emalex Biosciences Inc.RecruitingTourette DisorderUnited States, Canada, Spain, Poland, Italy, Bulgaria, Denmark, France, Germany, Hungary, Serbia, Romania
-
Neurocrine BiosciencesHuntington Study GroupCompletedChorea, HuntingtonUnited States, Canada
-
DePuy OrthopaedicsRecruitingPrimary Knee ArthroplastyUnited States, Australia, Austria, Belgium, Canada, France, Germany, Ireland, Italy, Netherlands, New Zealand, Switzerland, United Kingdom
-
Alexion Pharmaceuticals, Inc.TerminatedWilson DiseaseSpain, Korea, Republic of, France, Germany, Japan, Australia, Poland, United Kingdom
-
Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States, Brazil, Belgium, Canada, Germany, Italy, Spain, Sweden, Turkey, United Kingdom
-
Pharnext S.C.A.Worldwide Clinical TrialsActive, not recruitingCharcot-Marie-Tooth DiseaseUnited States, Spain, Belgium, Italy, Israel, Canada, Denmark, France, Germany
-
Children's Oncology GroupNational Cancer Institute (NCI)CompletedMyeloid Proliferations Associated With Down SyndromeUnited States, Canada, Australia, Puerto Rico
-
Spark TherapeuticsActive, not recruitingLysosomal Storage Diseases | Glycogen Storage Disease Type II | Glycogen Storage Disease Type 2 | Pompe Disease (Late-onset) | Pompe Disease | LOPD | Acid Maltase DeficiencyUnited States, Canada, Netherlands, France, Denmark, Germany, Italy, United Kingdom
-
Genzyme, a Sanofi CompanyRecruitingFabry DiseaseCroatia, United States, Argentina, Australia, Belgium, Bulgaria, Canada, Germany, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Malaysia, Philippines, Poland, Romania, Singapore, Slovakia, Taiwan, Thailand, United Kingdom, Vietn... and more
-
Assistance Publique - Hôpitaux de ParisCompletedInfant, Newborn, Diseases | Anemia, Neonatal | Hematologic Disease | Blood and Blood DisordersUnited States, Canada, France
-
CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom
-
TVA Medical Inc.Completed
-
Children's Health System, Inc.Walter Lorenz Surgical CorporationUnknownRepair of Pectus ExcavatumUnited States, Canada
-
Nagoya UniversityTerminated
-
AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis 1 | Plexiform Neurofibroma (PN)United States, Canada, France, Italy, Germany, China, United Kingdom, Spain, Japan, Russian Federation, Australia, Poland, Brazil
-
Smith & Nephew, Inc.CompletedBunionectomy | Hallux Valgus Repairs | Medial or Lateral Instability Repairs/Reconstructions | Achilles Tendon Repairs/Reconstructions | Midfoot Reconstructions | Metatarsal Ligament/Tendon Repairs/Reconstructions | Scapholunate Ligament Reconstructions | Lateral Epicondylitis Repair | Ulnar | Bicep Tendon...United States, Canada
-
ShireDyax Corp.CompletedHereditary Angioedema (HAE)United States, Canada, Germany, Italy, Jordan, Puerto Rico, United Kingdom
-
Vertex Pharmaceuticals IncorporatedCompletedCystic Fibrosis, Homozygous or Heterozygous for the F508del-CFTR MutationUnited States, France, United Kingdom, Germany, Spain, Belgium, Canada, Australia, Netherlands, Denmark, Czech Republic, Italy, Austria, Ireland, Sweden
-
Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth Disease | Facioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
-
Children's Hospital Los AngelesRecruitingVentilator-Induced Lung Injury | Ards | Ventilation Therapy; ComplicationsUnited States, Italy, Canada
-
KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Israel, Netherlands, Spain, United Kingdom, Australia, Germany, South Africa, Slovakia, Austria, New Zealand, Romania, Canada, Japan
-
Leiden University Medical CenterKarolinska University Hospital; Universitaire Ziekenhuizen KU Leuven; Boston... and other collaboratorsRecruitingFetal Growth Retardation | Twin; Pregnancy, Affecting Fetus or Newborn | Twin Diseases | Twin Monochorionic Diamniotic PlacentaUnited States, Belgium, Netherlands, Sweden, Canada, Spain