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Clinical Trials on Genetics/Birth Defects in South Africa
Total 1541 results
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BiotestSyneos HealthCompletedPrimary Immunodeficiency DiseaseUnited States, Germany, Hungary, Russian Federation, Spain
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCDKL5 | Rett Syndrome | MECP2 Duplication | FOXG1 DisordersUnited States
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Mayne Pharma International Pty LtdTerminatedLamellar IchthyosisUnited States, Spain, Canada, Germany, France, Australia, Israel, Ukraine, United Kingdom
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Micelle BioPharma IncUnknownSickle Cell DiseaseUnited States
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Novoteris, LLCMallinckrodt; Cystic Fibrosis FoundationTerminatedCystic FibrosisUnited States, Canada
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisAustralia, United Kingdom
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SCAD AlliancePERFUSE Study GroupRecruitingSpontaneous Coronary Artery DissectionUnited States, Australia
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)CompletedAlpha 1-Antitrypsin DeficiencyAustralia, New Zealand
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Medical University of South CarolinaNational Center for Research Resources (NCRR); Alpha-1 FoundationCompletedAlpha-1 Antitrypsin DeficiencyUnited States
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Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
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Rafic Hariri University HospitalUnknown
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Kowa Research Institute, Inc.CompletedFuchs' Endothelial Corneal DystrophyUnited States, Australia, Germany, Spain, Denmark
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Tenax Therapeutics, Inc.Active, not recruitingHeart Failure With Normal Ejection Fraction | Hypertension Pulmonary Secondary Heart Failure | Right Sided Heart Failure With Normal Ejection FractionUnited States
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Q32 Bio Inc.RecruitingAtopic DermatitisUnited States
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AbbVieCompletedAtopic DermatitisUnited States, Australia, Canada, Finland, Germany, Japan, Netherlands, Spain
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Bristol-Myers SquibbCompletedDermatitis, AtopicGermany, Australia, Poland, Canada, Austria, United States, Spain
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Asana BioSciencesCompletedAtopic DermatitisUnited States, Germany, Canada
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Bioverativ Therapeutics Inc.CompletedHemophilia AUnited States, Canada, Italy, Australia, Austria, Belgium, Brazil, France, Germany, Hong Kong, India, Ireland, Israel, Japan, Netherlands, New Zealand, Poland, South Africa, Spain, Sweden, Switzerland, United Kingdom
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NewAmsterdam PharmaActive, not recruitingDyslipidemias | Hypercholesterolemia | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Familial Hypercholesterolemia | Metabolic Disease | High Cholesterol | Genetic Disease, Inborn | Lipid Metabolism DisorderUnited States, Canada, Czechia, Georgia, Netherlands, Norway, Poland, South Africa, Spain, United Kingdom
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Timber Pharmaceuticals Inc.Active, not recruitingIchthyosisUnited States, Canada, Germany, France, Italy
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Ralexar Therapeutics, Inc.CompletedAtopic Dermatitis | Eczema, AtopicUnited States
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PfizerCompletedPlaque Psoriasis | Atopic DermatitisUnited States, Australia, Canada, Poland
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Arrowhead PharmaceuticalsTerminatedCystic Fibrosis, PulmonaryAustralia, New Zealand
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Genzyme, a Sanofi CompanyActive, not recruitingHemophiliaChina, Hungary, Turkey, Canada, Korea, Republic of, United States, Australia, Denmark, France, Germany, India, Ireland, Israel, Italy, Japan, Malaysia, South Africa, Taiwan, Ukraine, United Kingdom
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Regeneron PharmaceuticalsSanofiCompletedEczema, Atopic | Atopic DisordersUnited States
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Genentech, Inc.Completed
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Regeneron PharmaceuticalsSanofiActive, not recruitingAtopic DermatitisUnited States, Canada, Czechia, Germany, Hungary, Poland, United Kingdom
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AbbVieCompletedAtopic DermatitisUnited States, Australia, Canada, Croatia, Czechia, Finland, France, Germany, Hungary, Ireland, Israel, Italy, Malaysia, Netherlands, New Zealand, Norway, Poland, Singapore, Spain, Taiwan, Ukraine, United Kingdom
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Acrotech Biopharma Inc.CompletedAtopic DermatitisUnited States
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Chris GossUniversity of Washington; University of Arkansas; Harvard University; Cystic Fibrosis...Completed
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Incyte CorporationCompletedAtopic DermatitisUnited States, Germany, Spain, Canada, Poland, Czechia, Bulgaria
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTerminatedMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Spain, Australia
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The University of QueenslandRecruitingAutosomal Dominant Polycystic Kidney DiseaseAustralia
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AmgenCompletedSevere Familial HypercholesterolemiaItaly, Czechia, United States, Israel, New Zealand, South Africa, France, Spain, Australia, Belgium, Canada, Netherlands, Hong Kong, Brazil, United Kingdom, Greece, Japan, Lebanon
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PfizerRecruitingAtopic DermatitisUnited States, Canada
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Eli Lilly and CompanyRecruiting
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Daiichi Sankyo, Inc.CompletedAtopic DermatitisUnited States
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Mast Therapeutics, Inc.CompletedSickle Cell DiseaseUnited States
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Tioga PharmaceuticalsCompletedPruritus | Atopic DermatitisUnited States
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Clemson UniversityUniversity of California, Los Angeles; Prisma Health-Upstate; Georgia State UniversityCompleted
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Suzhou Connect Biopharmaceuticals, Ltd.CompletedModerate-to-severe Atopic DermatitisUnited States, Australia, China, New Zealand
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Trefoil Therapeutics, Inc.CompletedEndothelial Dysfunction | Corneal Endothelial Dystrophy | Pseudophakic Bullous Keratopathy | Fuchs Endothelial Corneal DystrophyUnited States
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Arcutis Biotherapeutics, Inc.CompletedAtopic Dermatitis EczemaUnited States, Canada
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Brazil, Canada, France, Germany, Hungary, Israel, Italy, Netherlands, South Africa, Spain, United Kingdom
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Ardea Biosciences, Inc.CompletedGoutUnited States, Canada, Belgium, Australia, Germany, New Zealand, South Africa
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Ardea Biosciences, Inc.CompletedGoutUnited States, South Africa, Canada, Belgium, New Zealand, Australia, Germany
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BioCryst PharmaceuticalsCompleted
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Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisUnited States
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AbbVieActive, not recruitingAtopic DermatitisUnited States, Argentina, Australia, Bosnia and Herzegovina, Bulgaria, Canada, China, Colombia, Croatia, Denmark, Estonia, Finland, France, Germany, Italy, Japan, Malaysia, New Zealand, Puerto Rico, Romania, Russian Federation, Sw... and more
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AbbVieActive, not recruitingAtopic DermatitisAustralia, Belgium, Bulgaria, Canada, China, Germany, Hungary, Italy, Korea, Republic of, Netherlands, New Zealand, Poland, Portugal, Slovakia, Spain, Taiwan, United Kingdom, Japan