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Clinical Trials on Genetics/Birth Defects in South Africa
Total 1544 results
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Radiation Therapy Oncology GroupNational Cancer Institute (NCI); NRG OncologyCompletedSexual Dysfunction | Prostate Cancer | Radiation Toxicity | Psychosocial Effects of Cancer and Its TreatmentUnited States, Canada
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Ancora Heart, Inc.RecruitingDilated Cardiomyopathy | Heart Failure With Reduced Ejection Fraction (HFrEF)United States, France, Netherlands, Czechia, Belarus, Belgium, Serbia
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Spain, Ireland, Australia, Israel, United Kingdom, Germany, Switzerland, Canada, Denmark, Poland
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Baxalta now part of ShireCompletedVon Willebrand DiseaseNetherlands, Spain, United States, Belgium, Australia, United Kingdom, Austria, Italy, Bulgaria, Japan, Poland, Germany, India, Canada, Russian Federation, Sweden
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Southwest Oncology GroupNational Cancer Institute (NCI)CompletedDepression | Pain | Breast Cancer | Fatigue | Colorectal Cancer | Cognitive/Functional Effects | Anxiety Disorder | Psychosocial Effects of Cancer and Its Treatment | Weight ChangesUnited States
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Chris GossMedical University of South Carolina; University of Washington; Cystic Fibrosis... and other collaboratorsCompletedPulmonary Cystic FibrosisUnited States, Canada
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Vertex Pharmaceuticals IncorporatedCompletedCystic Fibrosis, Homozygous for the F508del CFTR MutationUnited States, Germany, Canada, Netherlands, Czech Republic, Italy, Ireland, Sweden, United Kingdom, Australia, France
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University of Alabama at BirminghamNational Institutes of Health (NIH); Mereo BioPharmaCompletedEmphysema or COPD | Alpha-1 Antitrypsin Deficiency (AATD) | Pi*ZZ, Pi*SZ, Pi*Null, Another Rare Phenotype/Genotype Known to be Associated With Either Low or Functionally Impaired AAT Including F or I MutationsUnited States
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Japan, Australia, Taiwan, Canada
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Gilead SciencesSalus Pharma, Inc.CompletedCystic Fibrosis | Pseudomonas Aeruginosa | Lung Infection | CFUnited States
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Ardea Biosciences, Inc.Completed
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Savient PharmaceuticalsCompletedGoutUnited States, Canada, Mexico
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Novartis PharmaceuticalsCompletedCystic FibrosisUnited States, Germany, United Kingdom, Colombia, Spain, France, Netherlands, Israel, Canada, Italy, Chile, Australia, Hungary, Mexico
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Alliance for Clinical Trials in OncologyNational Cancer Institute (NCI)CompletedBreast Cancer | Hot Flashes | Psychosocial Effects of Cancer and Its TreatmentUnited States
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New York State Institute for Basic ResearchEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsUnknownAlzheimer Disease | Down SyndromeUnited States, Canada, Australia, United Kingdom
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Mucpharm Pty LtdSt George Hospital, Australia; Mobius Medical Pty Ltd.CompletedCOVID-19 Pneumonia | COVID-19 Acute Respiratory Distress Syndrome | Bromelains Adverse Reaction | Acetylcysteine Adverse Reaction | Mucus; PlugAustralia
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AFrance, United States, Denmark, Netherlands, Sweden, Spain, Germany, Switzerland, Taiwan, Japan, United Kingdom, Croatia, Italy, Malaysia, Brazil, Australia, Hungary, Israel, Turkey, Puerto Rico, Norway, Korea, Republic of, Bulgaria, Russian...
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IpsenCompletedCarcinoid SyndromeUnited States, Turkey, Brazil, India, Ukraine, South Africa, Czechia, Latvia, Poland, Russian Federation, Serbia
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Wave Life Sciences Ltd.TerminatedHuntington's DiseaseUnited States, Denmark, Canada, Australia, United Kingdom, France, Germany, Poland
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Alexion Pharmaceuticals, Inc.TerminatedWilson DiseaseSpain, Korea, Republic of, France, Germany, Japan, Australia, Poland, United Kingdom
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Canadian Cancer Trials GroupQueen's University, Belfast; Survivorship Research GroupActive, not recruitingDepression | Fatigue | Colorectal Cancer | Sleep Disorders | Cognitive/Functional Effects | Anxiety Disorder | Psychosocial Effects of Cancer and Its Treatment | ExcerciseCanada, United States, Australia, France, Korea, Republic of, United Kingdom
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
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TakedaOvid Therapeutics Inc.CompletedEpilepsy | Dravet Syndrome | Lennox-Gastaut SyndromeUnited States, Canada, Israel, Poland, Spain, Australia, China, Portugal
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedKidney CancerUnited States, Canada, Puerto Rico, Australia, Netherlands, Switzerland, New Zealand
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Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedMethylphenidate to Improve Quality of Life in Patients Undergoing Radiation Therapy for Brain TumorsDepression | Quality of Life | Fatigue | Brain and Central Nervous System Tumors | Cognitive/Functional EffectsUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Netherlands, Spain, Switzerland, Taiwan, Turkey, United Kingdom, Croatia, Germany, Brazil, France, Japan, Australia, Hungary, Israel, Korea, Republic of, Lithuania, Portugal, Ukraine, Greece, Italy, Denmark, Norway, Canada and more
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Juniper Pharmaceuticals, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedPreterm Delivery | Short Cervix | Short Uterine Cervical LengthUnited States, Israel, Belarus, Chile, Czech Republic, India, Italy, Russian Federation, South Africa, Ukraine
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Alliance for Clinical Trials in OncologyNational Cancer Institute (NCI)CompletedBreast Cancer | Psychosocial Effects of Cancer and Its TreatmentUnited States
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Novartis PharmaceuticalsCompletedAcute GoutUnited States, Canada, Russian Federation, Netherlands, China
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedKidney CancerUnited States, Canada, Puerto Rico, Australia, Netherlands, New Zealand, Switzerland
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Novartis PharmaceuticalsRecruitingSickle Cell Disease (SCD)United States, Germany, Spain, Belgium, Italy, Lebanon, Brazil, Colombia, Oman, Switzerland, Turkey, United Kingdom, Canada, India, France
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Netherlands, Austria, Spain, Poland, United Kingdom, Croatia, Germany, Malaysia, Australia, France, Israel, Thailand, Ukraine, Turkey
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Pfizer's Upjohn has merged with Mylan to form Viatris...CompletedArthritis, GoutyCanada, United States, Spain, Russian Federation, Colombia, Costa Rica, Peru, Taiwan, Korea, Republic of, Mexico, Philippines, Thailand
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Azienda Ospedaliera Universitaria Integrata VeronaInternational Centre of Birth DefectsUnknown
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Michael ShyJohns Hopkins University; University of Colorado, Denver; King's College Hospital... and other collaboratorsRecruitingCharcot Marie Tooth DiseaseUnited States, Australia, Italy, United Kingdom, Canada
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Recursion Pharmaceuticals Inc.RecruitingSolid Tumor | APC Gene Mutation | AXIN1 Gene MutationUnited States
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TakedaCompleted
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Neurocrine BiosciencesCompletedTourette SyndromeUnited States, Puerto Rico
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Teva Branded Pharmaceutical Products R&D, Inc.Nuvelution TS Pharma, Inc.CompletedTourette SyndromeUnited States, Argentina, Australia, Colombia, Hungary, Italy, Korea, Republic of, Mexico, Poland, Ukraine
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Horizon Pharma Rheumatology LLCCompletedRefractory Chronic GoutUnited States
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Gilead SciencesCovance; ClinPhone, Inc.; Chiltern International Inc.CompletedCystic FibrosisBelgium, France, Germany, Italy, Netherlands, Spain, United States, Ireland, United Kingdom, Portugal, Austria, Denmark, Switzerland
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TakedaActive, not recruitingEpilepsy | Dravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)United States, Canada, Australia, China, Israel, Poland, Spain, Portugal
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Zogenix, Inc.Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.Active, not recruitingDravet Syndrome | Epileptic Encephalopathy | Lennox Gastaut SyndromeUnited States, Australia, Belgium, Canada, Denmark, France, Germany, Italy, Mexico, Netherlands, Poland, Spain, Sweden, United Kingdom
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Australia, Belgium, Germany, Italy, Poland, Romania, United Kingdom, Argentina, Canada, France, Netherlands, Russian Federation
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ShireCompletedHereditary AngioedemaUnited States
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Emalex Biosciences Inc.RecruitingTourette SyndromeUnited States, Spain, Canada, Italy, Bulgaria, Hungary, Poland
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Armata Pharmaceuticals, Inc.Cystic Fibrosis FoundationCompletedCystic Fibrosis | Pseudomonas Aeruginosa | Lung Infection | Pseudomonas | Lung Infection PseudomonalUnited States
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Olatec Therapeutics LLCRecruitingArthritis | Joint Pain | Gout | Gout Flare | Gouty Arthritis | Acute Gout Flare | Gout AttackUnited States, Spain, France
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BiomX, Inc.Active, not recruitingCystic Fibrosis | Chronic Pseudomonas Aeruginosa InfectionUnited States, Israel, Spain, Czechia, Netherlands
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Parion SciencesVertex Pharmaceuticals IncorporatedCompletedPrimary Ciliary DyskinesiaUnited States, United Kingdom, Netherlands, Denmark, Canada, Italy, Germany, Poland