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Clinical Trials on Genetics/Birth Defects in South Africa
Total 1544 results
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Emalex Biosciences Inc.CompletedTourette SyndromeUnited States, Poland, France, Canada, Germany
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HP Therapeutics FoundationHuntington Study GroupUnknownHuntington DiseaseUnited States, Canada, Australia
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Eunice Kennedy Shriver National Institute of Child...CompletedFetal Growth Restriction | Growth DiscordancyUnited States
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Gilead SciencesCompleted
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CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Germany, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom
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University of Washington, the Collaborative Health...Cystic Fibrosis FoundationRecruitingColorectal Cancer | Adenoma | Cystic FibrosisUnited States
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingStage III Kidney Wilms Tumor | Stage IV Kidney Wilms TumorUnited States, Canada, Australia, New Zealand, Puerto Rico, Israel, Switzerland
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Novartis PharmaceuticalsActive, not recruitingType 2 Spinal Muscular AtrophyUnited States, China, Saudi Arabia, Thailand, Singapore, Brazil, Malaysia, Taiwan, Colombia, Mexico, Denmark, Egypt, India, South Africa, Vietnam
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Alliance for Clinical Trials in OncologyNational Cancer Institute (NCI)TerminatedFatigue | Cancer Survivor | Sleep Disorders | Psychosocial Effects of Cancer and Its TreatmentUnited States
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TakedaCompletedGout | Moderate Renal ImpairmentUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Denmark, Austria, Spain, Japan, Brazil, Algeria, Lithuania, Portugal, Russian Federation, Serbia, Turkey, Greece, Hong Kong, Puerto Rico, Hungary, China, Poland
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Target PharmaSolutions, Inc.RecruitingPsoriasis | Atopic Dermatitis | Vitiligo | Hidradenitis Suppurativa | Alopecia Areata | Chronic Spontaneous UrticariaUnited States, Spain, Canada, Germany
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Horizon Health NetworkMcGill University; University of Michigan; Carilion Clinic; Lawson Health Research... and other collaboratorsCompleted
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Noema Pharma AGRecruitingTuberous Sclerosis ComplexUnited States, Turkey, Poland, Spain, United Kingdom, India, Italy, Israel
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Reata, a wholly owned subsidiary of BiogenTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, United Kingdom, Australia, France, Japan, Germany, Belgium, Czechia, Italy
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Novartis PharmaceuticalsCompletedTransfusion-dependent Iron OverloadEgypt, Greece, Hong Kong, Taiwan, Germany, United Kingdom, Belgium, Italy, Spain, France, Israel, Korea, Republic of, Turkey, China, Australia, Denmark, Austria, Switzerland, Netherlands, South Africa, Lebanon, Malaysia, Thailand
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)TerminatedPain | Lymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Brain and Central Nervous System Tumors | Unspecified Adult Solid Tumor, Protocol Specific | Multiple Myeloma and Plasma Cell Neoplasm | Precancerous Condition | Lymphoproliferative Disorder | Myelodysplastic/Myeloproliferative...United States
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Neurocrine BiosciencesHuntington Study GroupCompletedChorea, HuntingtonUnited States, Canada
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BayerCompletedBronchiectasisItaly, Spain, Germany, United Kingdom, France
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National Eye Institute (NEI)CompletedRetinopathy of PrematurityUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Spain, Australia, France, Thailand, Italy, Malaysia, Austria, Greece, Japan, Taiwan, Canada, Israel, Algeria, Argentina, Bulgaria, Germany, Romania
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PrileniaHuntington Study Group; European Huntington's Disease NetworkCompletedHuntington's DiseaseUnited States, Australia, Austria, Canada, Denmark, France, Germany, Italy, Netherlands, Poland, Russian Federation, United Kingdom
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Cynata Therapeutics LimitedCerebral Palsy AllianceCompletedCovid19 | Acute Respiratory Distress SyndromeAustralia
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Emalex Biosciences Inc.RecruitingTourette DisorderUnited States, Canada, Spain, Poland, Italy, Bulgaria, Denmark, France, Germany, Hungary, Serbia, Romania
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI)TerminatedHematologic Diseases | Anemia, Sickle Cell | Cerebrovascular Accident | HemochromatosisUnited States
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CSL BehringActive, not recruitingHereditary AngioedemaAustralia, Canada, United States, New Zealand, Germany, Hong Kong, Netherlands, Taiwan, Czechia, Israel, Hungary, Japan, Russian Federation, Spain
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CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom
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National Eye Institute (NEI)UnknownRetinopathy of PrematurityUnited States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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LimFlow, Inc.CompletedCritical Limb Ischemia | Chronic Limb-Threatening IschemiaUnited States
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PTC TherapeuticsNo longer available
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Ashvattha Therapeutics, Inc.Terminated
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PfizerCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Age-Related Maculopathies | Age-Related MaculopathyUnited States
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Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingStage I Kidney Wilms Tumor | Stage II Kidney Wilms Tumor | Stage III Kidney Wilms TumorUnited States, Canada, Australia, New Zealand, Puerto Rico, Israel, Switzerland
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Jazz PharmaceuticalsActive, not recruitingTuberous Sclerosis Complex | Dravet Syndrome | Lennox Gastaut SyndromeUnited States
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CelgeneRecruitingBeta-thalassemia | Myelodysplastic Syndromes (MDS) | Myeloproliferative Neoplasm(MPN)-Associated MyelofibrosisUnited States, Japan, United Kingdom, Turkey, Greece, France, Australia, Belgium, Bulgaria, Canada, Germany, Israel, Italy, Malaysia, Spain, Sweden, Taiwan, Thailand, Tunisia, Lebanon, China, Netherlands
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Australia, Bulgaria, Canada, France, Germany, Greece, Hungary, Israel, Italy, Japan, Netherlands, New Zealand, North Macedonia, Poland, Portugal, Puerto Rico, Romania, Slovakia, Spain, United Kingdom
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University of MichiganGenentech, Inc.CompletedHealthy | Protein-Losing Enteropathies | Plastic BronchitisUnited States
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CHDI Foundation, Inc.RecruitingHuntington's DiseaseUnited States, Canada, Belgium, Spain, Australia, Germany, France, Netherlands, United Kingdom, New Zealand, Argentina, Austria, Chile, Colombia, Denmark, Ireland, Italy, Poland, Portugal, Switzerland
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Gilead SciencesTerminatedCystic Fibrosis | Pseudomonas Aeruginosa Respiratory Tract Infection/ColonizationUnited States, Spain, United Kingdom, Denmark, Belgium, France, Italy, Germany, Israel, Netherlands, Austria, Greece
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Hoffmann-La RocheRecruitingHuntington DiseaseUnited States, Australia, Argentina, Canada, Germany, Italy, France, United Kingdom, Spain, Portugal, New Zealand, Austria, Poland, Switzerland, Denmark
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Leiden University Medical CenterAcademisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA); Sanquin...RecruitingIntraventricular Hemorrhage | Neonatal Thrombocytopenia | Platelet TransfusionNetherlands, Sweden
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Emalex Biosciences Inc.CompletedTourette Syndrome in Children | Tourette Syndrome in AdolescenceUnited States, Poland, France, Canada, Germany
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KalVista Pharmaceuticals, Ltd.TerminatedAngioedema, Hereditary, Types I and IIUnited States, Czechia, Germany, Hungary, Italy, North Macedonia, United Kingdom, Australia, Bulgaria, Canada, France, New Zealand, Puerto Rico
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National Cancer Institute (NCI)RecruitingDown Syndrome | B Acute Lymphoblastic Leukemia | B Lymphoblastic LymphomaUnited States, Canada, Puerto Rico, Australia, New Zealand
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National Cancer Institute (NCI)SuspendedDown Syndrome | Recurrent B Acute Lymphoblastic LeukemiaUnited States, Canada, Puerto Rico, Australia
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Stealth BioTherapeutics Inc.Active, not recruitingMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial Complex I Deficiency | Mitochondrial Pathology | Mitochondrial DNA Depletion | Mitochondrial DNA Mutation | Mitochondrial DNA Deletion | Mitochondrial Metabolism DefectSpain, United States, Italy, Netherlands, Australia, Germany, Hungary, New Zealand, Norway, United Kingdom