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Clinical Trials on Genetics in Netherlands
Total 795 results
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Swedish Orphan BiovitrumPediatric Rheumatology International Trials OrganizationCompletedCryopyrin-Associated Periodic SyndromesUnited Kingdom, Netherlands
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Amicus TherapeuticsCompleted
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Academisch Medisch Centrum - Universiteit van Amsterdam...UnknownPiebaldism | Segmental Vitiligo | Non-segmental VitiligoNetherlands
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PfizerCompleted
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Sanquin Research & Blood Bank DivisionsRadboud University Medical Center; Maastricht University Medical Center; Atrium...Completed
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Hoffmann-La RocheCompleted
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Academisch Medisch Centrum - Universiteit van Amsterdam...Erasmus Medical Center; Prothya BiosolutionsRecruitingAtopic Dermatitis | Atopic Dermatitis EczemaNetherlands
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Academisch Medisch Centrum - Universiteit van Amsterdam...RecruitingFabry Disease | Fabry Disease, Cardiac VariantNetherlands
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Vertex Pharmaceuticals IncorporatedCompleted
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UMC UtrechtCompletedPrimary Antibody DeficienciesNetherlands
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Academisch Medisch Centrum - Universiteit van Amsterdam...Leiden University Medical CenterRecruitingSickle Cell DiseaseNetherlands
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Academisch Medisch Centrum - Universiteit van Amsterdam...Dutch Heart FoundationCompletedFamilial HypercholesterolemiaNetherlands
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University Medical Center GroningenUniversity of Oxford; University of the Faroe Islands; Stichting Stofwisselkracht and other collaboratorsCompleted
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Sanquin Research & Blood Bank DivisionsRadboud University Medical Center; Maastricht University Medical Center; Atrium... and other collaboratorsUnknownHereditary HemochromatosisNetherlands
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Maastricht University Medical CenterCompletedNeutral Lipid Storage DiseaseNetherlands
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Academisch Medisch Centrum - Universiteit van Amsterdam...Recruiting
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University Medical Center GroningenErasmus Medical Center; De Najjar StichtingCompleted
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University Medical Center GroningenRecruiting
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Akros Pharma Inc.CompletedType II HyperlipidemiaNetherlands
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Academisch Medisch Centrum - Universiteit van Amsterdam...UnknownSickle Cell DiseaseNetherlands
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Japan Tobacco Inc.CompletedType II HyperlipidaemiaNetherlands
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Vertex Pharmaceuticals IncorporatedCompleted
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Maastricht University Medical CenterMyrovlytis TrustCompleted
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Academisch Medisch Centrum - Universiteit van Amsterdam...RecruitingSickle Cell DiseaseNetherlands
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Maastricht University Medical CenterPfizerCompleted
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Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Netherlands
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Leiden University Medical CenterCompletedVentricular Fibrillation | Tachycardia, Ventricular | Cardiomyopathy, DilatedNetherlands
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD FoundationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophyNetherlands
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BioMarin PharmaceuticalCompletedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
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Radboud University Medical CenterSolve FSHDRecruitingMuscular Dystrophy, FacioscapulohumeralNetherlands
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy 1Netherlands
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University Medical Center GroningenUnknownHeart Failure | Cognitive Impairment | Dilated Cardiomyopathy | Cerebral Hypoperfusion | PerfusionNetherlands
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CSL BehringActive, not recruiting
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Pharming Technologies B.V.CompletedHereditary Angioedema | Genetic DisordersNetherlands, Romania
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Pharming Technologies B.V.CompletedHereditary Angioedema | Genetic Disorders | Angioneurotic EdemaNetherlands, Romania
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Radboud University Medical CenterEnzyre B.V.Recruiting
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Novartis PharmaceuticalsCompletedHealthy Volunteers | Atopic Dermatitis | Netherton SyndromeNetherlands, United States
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Radboud University Medical CenterRecruitingSELENON-related Myopathy | LAMA2-related Muscular DystrophyNetherlands
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UMC UtrechtSanquin Research & Blood Bank Divisions; National Institute for Public Health... and other collaboratorsRecruitingDown Syndrome | SARS-CoV-2 VaccinationNetherlands
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University Medical Center GroningenUltragenyx Pharmaceutical IncCompletedGlycogen Storage Disease Type IANetherlands
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Hans SmitRijnstate Hospital; Prof. Dr. Jaap Swieringa stichting; Mr. Willem Bakhuys RoozeboomstichtingUnknown
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University College, LondonRadboud University Medical Center; Groupe Hospitalier Pitie-Salpetriere; Leiden... and other collaboratorsCompletedDuchenne Muscular DystrophyNetherlands, France, United Kingdom
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyNetherlands, Belgium, Italy, Sweden
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
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Radboud University Medical CenterActive, not recruiting
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Prothya BiosolutionsCompletedPrimary ImmunodeficiencyNetherlands
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Prothya BiosolutionsCompletedHemophilia BNetherlands
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Maastricht University Medical CenterRadboud University Medical CenterUnknown
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Lipid Metabolism, Inborn Errors | Hypobetalipoproteinemias | Hypolipoproteinemias | Hypolipopro... and other conditionsNetherlands
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University Medical Center NijmegenLeiden University Medical Center; Princess Beatrix Muscle FoundationCompletedPediatric Disorder | Facioscapulohumeral Muscular Dystrophy | Neurological ObservationsNetherlands