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Clinical Trials on Genetics in United Kingdom
Total 7708 results
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University of NottinghamNottingham University Hospitals NHS TrustRecruitingChronic Obstructive Pulmonary Disease | Alpha 1-Antitrypsin DeficiencyUnited Kingdom
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King's College LondonCHDI Foundation, Inc.Recruiting
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PfizerCompletedHemophilia AUnited Kingdom, Hungary, Bulgaria
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St George's, University of LondonUniversity College London HospitalsUnknownPeripheral Neuropathy | CMT - Charcot-Marie-Tooth Disease | Hereditary Peripheral Neuropathy | CMT1AUnited Kingdom
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REGENXBIO Inc.CompletedMucopolysaccharidosis IIBrazil, United States, United Kingdom
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University of AberdeenEnrolling by invitationHuntington DiseaseUnited Kingdom
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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London North West Healthcare NHS TrustUnknownFamilial Adenomatous PolyposisUnited Kingdom
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Vanderbilt-Ingram Cancer CenterActive, not recruitingSickle Cell Disease | HemoglobinopathiesUnited States, United Kingdom, France
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HemoShear TherapeuticsPrometrika, LLC; AllStripes Research Inc.; Genome MedicalTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Canada, United Kingdom
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Medexus Pharma, Inc.TerminatedHemophilia BUnited States, United Kingdom, India
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Edimer PharmaceuticalsCompletedX-Linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustRecruiting
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Imperial College LondonRoyal Brompton & Harefield NHS Foundation Trust; British Heart FoundationRecruitingCardiovascular Diseases | Dilated CardiomyopathyUnited Kingdom
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Savara Inc.CelerionCompletedBronchiectasis | Cystic Fibrosis | Acute Respiratory Distress Syndrome | Pulmonary Alveolar ProteinosisUnited Kingdom
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Sheffield Teaching Hospitals NHS Foundation TrustSociety for Endocrinology; The Clinical Endocrinology TrustCompletedCongenital Adrenal HyperplasiaUnited Kingdom
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Institute of Child HealthGreat Ormond Street Hospital for Children NHS Foundation TrustCompletedAtaxia Telangiectasia (AT)United Kingdom
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Birmingham Women's and Children's NHS Foundation...BioMarin PharmaceuticalWithdrawnMucopolysaccharidosis IV | Morquio A DiseaseUnited Kingdom
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John Carroll UniversityUniversity Hospital Southampton NHS Foundation TrustActive, not recruitingPTEN Hamartoma Tumor SyndromeUnited States, United Kingdom
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St. Jude Children's Research HospitalChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingHemophilia BUnited States, United Kingdom
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University of CambridgeLund University; GE Healthcare; Cambridge University Hospitals NHS Foundation... and other collaboratorsRecruitingAtherosclerosis | Carotid Artery Plaque | Hypercholesterolemia | Hypercholesterolemia, FamilialUnited Kingdom
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TakedaRecruitingHereditary Angioedema (HAE)United Kingdom
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Ajinomoto Co., Inc.Great Ormond Street Hospital for Children NHS Foundation Trust; Birmingham...Active, not recruiting
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Inozyme PharmaIQVIA BiotechActive, not recruitingPseudoxanthoma Elasticum | Generalized Arterial Calcification of Infancy | ATP-Binding Cassette Subfamily C Member 6 DeficiencyUnited States, United Kingdom
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Joanne TurnerRecruiting
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The Royal Wolverhampton Hospitals NHS TrustCompletedApparent Mineralocorticoid ExcessUnited Kingdom
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London North West Healthcare NHS TrustCompletedColorectal Neoplasms, Hereditary NonpolyposisUnited Kingdom
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Edimer PharmaceuticalsActive, not recruitingX-linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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RwHealthNorthern Care Alliance NHS Foundation Trust; Alnylam PharmaceuticalsNot yet recruitingHereditary Amyloidosis | Guillain-Barre Syndrome | Chronic Inflammatory Demyelinating PolyneuropathyUnited Kingdom
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University of LeedsCompletedPrimary Ciliary DyskinesiaUnited Kingdom
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The Leeds Teaching Hospitals NHS TrustCompletedCystic Fibrosis | COPD | Chronic Respiratory Disease | Hypoxia, Altitude | ILDUnited Kingdom
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ShireTerminatedSanfilippo SyndromeNetherlands, United Kingdom
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Manchester University NHS Foundation TrustManchester Metropolitan UniversityCompletedMuscle Weakness | Neurofibromatosis Type 1United Kingdom
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GenethonActive, not recruitingLGMD2IDenmark, France, United Kingdom
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Nottingham University Hospitals NHS TrustUniversity of Nottingham; Neurotherapeutics LtdCompletedTourette Syndrome | Chronic Tic DisorderUnited Kingdom
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University of NottinghamNottingham University Hospitals NHS Trust; Birmingham Women's and Children's... and other collaboratorsUnknownCystic Fibrosis | Sensorineural Hearing LossUnited Kingdom
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University College, LondonTerminatedHemophilia BIreland, United Kingdom, Italy, United States
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Netherlands, Spain, United Kingdom
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Agios Pharmaceuticals, Inc.Active, not recruitingThalassemiaUnited States, Canada, United Kingdom
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Edimer PharmaceuticalsCompletedX-Linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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University of PlymouthRecruitingAtaxia Telangiectasia | Ataxia Telangiectasia in ChildrenUnited Kingdom
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Vitaflo International, LtdUniversity College London Hospitals; University Medical Center Groningen; University... and other collaboratorsCompletedGlycogen Storage DiseaseUnited States, United Kingdom, France, Netherlands
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ReNeuron LimitedActive, not recruitingRetinitis PigmentosaUnited States, United Kingdom, Spain
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King's College LondonUnknown
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University College London HospitalsUnknownBrugada SyndromeBrazil, Portugal, United Kingdom
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EspeRare FoundationIqvia Pty Ltd; Pierre Fabre MedicamentRecruitingX-Linked Hypohidrotic Ectodermal Dysplasia (XLHED)United States, Spain, France, Germany, Italy, United Kingdom
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Rocket Pharmaceuticals Inc.Enrolling by invitationLeukocyte Adhesion DeficiencySpain, United States, United Kingdom
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David WilliamsActive, not recruitingGene Therapy | Severe Combined Immunodeficiency, X LinkedUnited States, United Kingdom
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AlbireoCompletedPrimary Biliary Cirrhosis | Alagille Syndrome | Progressive Familial Intrahepatic Cholestasis | Orphan Cholestatic Liver DiseasesUnited Kingdom