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- US Clinical Trials Registry
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Clinical Trials on Glycogen Storage Disease Type IA in United Kingdom
Total 29104 results
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Genzyme, a Sanofi CompanyApproved for marketingGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe Disease (Late-Onset)United States
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)CompletedPompe DiseaseUnited States
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University of FloridaCompletedPompe DiseaseUnited States
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Duke UniversitySanofiRecruiting
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingPompe DiseaseUnited States
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development...Completed
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University of FloridaLacerta TherapeuticsCompletedPompe DiseaseUnited States
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University of FloridaBioMarin PharmaceuticalCompleted
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2United States, France, Netherlands
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Asklepios Biopharmaceutical, Inc.Active, not recruiting
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Genzyme, a Sanofi CompanyCompleted
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe DiseaseUnited States
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University of California, IrvineGenzyme, a Sanofi CompanyCompletedPompe DiseaseUnited States
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Amicus TherapeuticsTerminated
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University of FloridaTerminated
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O & O Alpan LLCCompleted
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Serhat Gumrukcu, MD PhDFrida Therapeutics LLCRecruiting
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Duke UniversityCompleted
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Duke UniversityGenzyme, a Sanofi CompanyCompleted
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Duke UniversityCompletedPompe DiseaseUnited States
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Duke UniversityCompleted
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Dwight Koeberl, M.D., Ph.D.Completed
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Amicus TherapeuticsCompletedGlycogen Storage Disease Type II | Pompe DiseaseUnited States
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Amicus TherapeuticsRecruitingPompe DiseaseUnited States, Germany
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Netherlands
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Duke UniversityCompleted
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Genzyme, a Sanofi CompanyCompleted
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Duke UniversityGenzyme, a Sanofi CompanyActive, not recruitingPompe Disease (Late-onset) | Pompe Disease | GAA DeficiencyUnited States
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Duke UniversityWithdrawnPompe Disease (Late-onset)United States
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Germany, Israel, Italy, Netherlands, Taiwan
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Amicus TherapeuticsAvailablePompe Disease Infantile-OnsetTaiwan, United States, Italy
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Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
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Duke UniversityCompleted
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Vitaflo International, LtdUniversity College London Hospitals; University Medical Center Groningen; University... and other collaboratorsCompletedGlycogen Storage DiseaseUnited States, United Kingdom, France, Netherlands
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Genzyme, a Sanofi CompanyTerminatedPompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe Disease Infantile-OnsetUnited States, France, South Africa
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Glycogenosis 2United States
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy, Australia
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedPompe DiseaseBelgium, United States, Czechia, Germany, Italy, Taiwan
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Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Japan, Australia, Taiwan, Canada
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingLate-Onset Pompe Disease | Lysosomal DiseaseUnited States
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University of California, IrvineCompletedMuscle Weakness | Pompe DiseaseUnited States
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University of California, San FranciscoDuke UniversityRecruitingWolman Disease | MPS IVA | Pompe Disease Infantile-Onset | Gaucher Disease, Type 2 | MPS VI | MPS I | Gaucher Disease, Type 3 | MPS II | Mps VIIUnited States
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University of FloridaCompleted