- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Glycogen Storage Disease Type VI
Total 58418 results
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University of FloridaLacerta TherapeuticsCompletedPompe DiseaseUnited States
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University of FloridaBioMarin PharmaceuticalCompleted
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LMU KlinikumGenzyme, a Sanofi CompanyCompletedPompe DiseaseGermany, Taiwan, Italy
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Amicus TherapeuticsCompleted
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National Taiwan University HospitalCompleted
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National Taiwan University HospitalUnknown
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Germany, Israel, Italy, Netherlands, Taiwan
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUnknown
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National Taiwan University HospitalCompleted
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Amicus TherapeuticsCompletedGlycogen Storage Disease Type II | Pompe DiseaseUnited States
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Genzyme, a Sanofi CompanyActive, not recruiting
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Centre Hospitalier de CayenneCompleted
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Serhat Gumrukcu, MD PhDFrida Therapeutics LLCRecruiting
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Amicus TherapeuticsAvailable
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Duke UniversityCompleted
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Duke UniversityGenzyme, a Sanofi CompanyCompleted
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Duke UniversityCompletedPompe DiseaseUnited States
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Duke UniversityCompleted
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Dwight Koeberl, M.D., Ph.D.Completed
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University of California, IrvineGenzyme, a Sanofi CompanyCompletedPompe DiseaseUnited States
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Amicus TherapeuticsTerminated
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University of FloridaTerminated
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O & O Alpan LLCCompleted
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Genzyme, a Sanofi CompanyCompleted
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Netherlands
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National Taiwan University HospitalUnknown
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Children's Healthcare of AtlantaTerminatedCongenital Disorders
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GeneCradle IncRecruitingPompe Disease (Late-onset)China
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GeneCradle IncRecruitingPompe Disease Infantile-OnsetChina
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Seventh Medical Center of PLA General HospitalGeneCradle Therapeutics, IncRecruiting
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUnknownPompe Disease | Late Onset Pompe DiseaseSpain
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Cliniques universitaires Saint-Luc- Université...UnknownGlucose 6 Phosphatase Deficiency | Glycogen Storage Disease Type IBelgium
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy
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Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
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Duke UniversityCompleted
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom, Germany, France, Italy, Portugal, Belgium, Netherlands
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Genzyme, a Sanofi CompanyCompletedPompe DiseaseBelgium, United States, Czechia, Germany, Italy, Taiwan
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University of FloridaAmicus TherapeuticsTerminatedPompe Disease | Hypersensitivity Reaction
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Glycogenosis 2United States
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Huashan HospitalNot yet recruitingPompe Disease (Late-onset)China
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Rambam Health Care CampusRecruitingPompe Disease Infantile-OnsetIsrael
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, United Kingdom
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Japan, Australia, Taiwan, Canada
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Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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Duke UniversityGenzyme, a Sanofi CompanyActive, not recruitingPompe Disease (Late-onset) | Pompe Disease | GAA DeficiencyUnited States
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Amicus TherapeuticsAvailablePompe Disease Infantile-OnsetTaiwan, United States, Italy
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom
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Duke UniversityWithdrawnPompe Disease (Late-onset)United States