- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Glycogen Storage Disorders
Total 150853 results
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Hospices Civils de LyonUnknownEnd Stage Renal Disease | Fabry Disease | Renal DialysisFrance
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Fondazione SISA (Societa Italiana per lo Studio...Recruiting
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Orchard TherapeuticsOspedale San RaffaeleActive, not recruitingLysosomal Storage Disease | Metachromatic LeukodystrophyItaly
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Orchard TherapeuticsOspedale San RaffaeleActive, not recruitingLysosomal Storage Disease | Metachromatic LeukodystrophyItaly
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AlexionCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited States, Canada, United Kingdom, Italy, France
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Patricia I. Dickson, M.D.National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Cognitive Decline | Hurler-Scheie SyndromeUnited States
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Dr. Anupam SehgalTaysha Gene Therapies, Inc.; GlycoNetActive, not recruitingInfantile GM2 Gangliosidosis (Disorder)Canada
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National Institute of Neurological Disorders and...CompletedHealthy | Motor Neuron Disease | Lysosomal Storage Disease | Movement Disorder | Demyelinating DiseaseUnited States
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National Institute of Neurological Disorders and...CompletedLysosomal Storage DiseaseUnited States, France, Israel, Netherlands
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Alexion PharmaceuticalsTerminatedLysosomal Acid Lipase DeficiencyUnited Kingdom, Finland, United States, Italy
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Assy NimerUnknownNon-alcoholic Fatty Liver Disease | Cholesterol Ester Storage DiseaseIsrael
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University of LincolnNottingham University Hospitals NHS TrustCompletedDepression | End-stage Renal DiseaseUnited Kingdom
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CENTOGENE GmbH RostockWithdrawnCholesterol Ester Storage Disease | Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Wolman TypeGermany, India, Sri Lanka
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University Of PerugiaRecruitingObesity | Ketosis | Lysosomal Acid Lipase Deficiency | Ketogenic DietingItaly
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Lawson Health Research InstituteSequana Medical N.V.RecruitingHemodialysis | Peritoneal Dialysis | End Stage Renal Disease on Dialysis | Nonosmotic Sodium StorageCanada
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Hospices Civils de LyonUnknownLiver Post-transplant PatientsFrance
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University of ZurichCompletedFabry DiseaseSwitzerland
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TakedaActive, not recruiting
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CENTOGENE GmbH RostockActive, not recruiting
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Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher DiseaseUnited States
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PfizerCompletedGaucher DiseaseIsrael, South Africa, Paraguay
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PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
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Hospices Civils de LyonUnknownPatients Waiting for a Liver Transplant.France
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Hospital St. Joseph, Marseille, FranceCompleted
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Assistance Publique - Hôpitaux de ParisCompletedGaucher DiseaseFrance
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Amicus TherapeuticsCompleted
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Wake Forest University Health SciencesNational Cancer Institute (NCI)CompletedTobacco Use Disorder | Stage IIIA Non-small Cell Lung Cancer | Stage IIIB Non-small Cell Lung Cancer | Recurrent Small Cell Lung Cancer | Limited Stage Small Cell Lung Cancer | Stage IA Non-small Cell Lung Cancer | Stage IB Non-small Cell Lung Cancer | Stage IIA Non-small Cell Lung Cancer | Stage IIB...United States
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Eunice Kennedy Shriver National Institute of Child...RecruitingLysosomal Storage Disease | Cholesterol MetabolismUnited States
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ShireTerminated
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TakedaCompleted
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseCanada, Russian Federation, Tunisia
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ShireCompleted
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PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain
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PfizerCompletedGaucher DiseaseChile, United Kingdom, Canada, Spain, Israel, United States, Australia, South Africa
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PfizerCompletedGaucher DiseaseIsrael, Paraguay, South Africa
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Yasmeen Abd Elbaset HamzaaUnknownGaucher Disease
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States, Sweden, India, Netherlands, Austria, Japan, China, Serbia, France, Croatia, Australia, Portugal, Canada, Brazil, Greece, Romania, Russian Federation
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ISU Abxis Co., Ltd.Completed
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University of MinnesotaRecruitingGaucher DiseaseUnited States
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TakedaNot yet recruiting
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Duke UniversityRecruiting
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TakedaCompletedGaucher DiseaseUnited States
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ShireCompletedGaucher DiseaseIndia
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PfizerCompleted
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ShireQuintiles, Inc.Completed
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ISU Abxis Co., Ltd.CompletedGaucher DiseaseAustralia