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Clinical Trials on Hemoglobinuria, Paroxysmal
Total 497 results
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King's College Hospital NHS TrustCompletedParoxysmal Nocturnal HaemoglobinuriaUnited Kingdom
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AKARI TherapeuticsRadboud University Medical CenterCompletedParoxysmal Nocturnal Haemoglobinuria (PNH)Netherlands
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Apellis Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Paroxysmal HemoglobinuriaMalaysia, United States, Czechia, France, Netherlands, Serbia, Spain, Thailand, United Kingdom
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria PNHLithuania, Japan, Czechia
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Ra PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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Alexion PharmaceuticalsAchillion, a wholly owned subsidiary of AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, New Zealand, Korea, Republic of, Italy
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AKARI TherapeuticsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Kazakhstan, Lithuania, Sri Lanka
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Alexion PharmaceuticalsTerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Czech Republic, Italy, Poland, United Kingdom
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AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Korea, Republic of, Canada, France, Germany, Spain, United Kingdom, Japan, Australia, Italy, Netherlands
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Ra PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Australia, Canada, Denmark, Finland, Germany, Hungary, New Zealand
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Alnylam PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Spain, United Kingdom
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Alexion PharmaceuticalsCompletedParoxysmal Hemoglobinuria, NocturnalUnited States, Australia, Belgium, Canada, Germany, Italy, Spain, Sweden, United Kingdom, France, Ireland, Netherlands
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National Heart, Lung, and Blood Institute (NHLBI)CompletedParoxysmal Hemoglobinuria, NocturnalUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedParoxysmal HemoglobinuriaUnited States
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AlexionActive, not recruitingParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Italy, Canada, Korea, Republic of, New Zealand, Spain, Turkey
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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AO GENERIUMCompletedParoxysmal Nocturnal Hemoglobinuria | Marchiafava-Micheli Syndrome | Paroxysmal HemoglobinuriaRussian Federation
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CARE Pharma Shanghai Ltd.CompletedParoxysmal Nocturnal Hemoglobinuria, Natural History StudyChina
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedAplastic Anemia | Paroxysmal Hemoglobinuria, NocturnalUnited States
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Longbio PharmaRecruitingParoxysmal Nocturnal Hemoglobinuria (PNH)China
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BioCryst PharmaceuticalsTerminatedBCX9930 for Treatment of PNH in Subjects With Inadequate Response to C5 Inhibitor Therapy (REDEEM-1)Paroxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Hungary, France, Italy, Spain
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Wuhan Createrna Science and Technology Co., LtdNot yet recruitingParoxysmal Nocturnal Hemoglobinuria (PNH)
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BioCryst PharmaceuticalsTerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)Malaysia, South Africa, Korea, Republic of
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AKARI TherapeuticsEnrolling by invitationParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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Ra Pharmaceuticals, Inc.TerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Australia, Canada, Finland, Germany, Hungary, New Zealand, United Kingdom
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Aplastic Anemia and MDS International FoundationNational Organization for Rare DisordersRecruiting
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Kira Pharmacenticals (US), LLC.Not yet recruitingParoxysmal Nocturnal HemoglobinuriaChina
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Wuhan Createrna Science and Technology Co., LtdCompletedParoxysmal Nocturnal HemoglobinuriaChina
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BioCryst PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom, Austria, South Africa
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Alexion PharmaceuticalsCMIC Co, Ltd. JapanCompletedParoxysmal Nocturnal Hemoglobinuria
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Peking Union Medical College HospitalUnknownParoxysmal Nocturnal HemoglobinuriaChina
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ADARx Pharmaceuticals, Inc.ADARx Australia Pty LtdRecruitingParoxysmal Nocturnal Hemoglobinuria (PNH)Australia
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NovelMed TherapeuticsNot yet recruitingPNH - Paroxysmal Nocturnal Hemoglobinuria
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Hoffmann-La RocheChugai PharmaceuticalActive, not recruitingParoxysmal Hemoglobinuria, NocturnalFrance, Korea, Republic of, Italy, Japan, Germany, Hungary, Netherlands
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Alexion Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Italy, United States, Taiwan, Thailand, Brazil, Russian Federation, United Kingdom, Belgium, Canada, Korea, Republic of, Poland, Malaysia, Japan, Czechia, Spain, Germany, Austria, France, Serbia, Mexico, Sweden, Estonia, Singapore, Ar... and more
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)China, Germany, Singapore, Korea, Republic of, Italy, United Kingdom, Malaysia, France
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Italy, Japan, Taiwan, Germany, France, United Kingdom, Spain, Korea, Republic of, Czechia, Brazil, Netherlands, United States
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Alexion Pharmaceuticals, Inc.Achillion, a wholly owned subsidiary of AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, United States, Italy
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Regeneron PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Hong Kong, Hungary, Korea, Republic of, Malaysia, United Kingdom
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Assistance Publique - Hôpitaux de ParisLeeds Cancer Centre at St. James's University HospitalCompleted
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaUnited States, France, Russian Federation, Korea, Republic of, Canada, Germany, Australia, Japan, Spain, Belgium, United Kingdom
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BiocadCompletedParoxysmal Nocturnal HemoglobinuriaRussian Federation
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaHong Kong, Thailand, New Zealand, Malaysia
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AO GENERIUMCompletedParoxysmal Nocturnal HemoglobinuriaRussian Federation
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Alexion PharmaceuticalsCompletedHemoglobinuria, ParoxysmalUnited States
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University of UtahNational Institutes of Health (NIH)CompletedHemoglobinuria, ParoxysmalUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Novartis PharmaceuticalsAvailableParoxysmal Nocturnal Hemoglobinuria (PNH) | C3 Glomerulopathy (C3G)
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AlexionCompletedParoxysmal Nocturnal HemoglobinuriaFrance, United Kingdom, Norway, Russian Federation, Netherlands, United States