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Clinical Trials on Hereditary Angioedema in France
Total 392 results
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Jaeb Center for Health ResearchFoundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Inherited Retinal DegenerationUnited States, United Kingdom, France, Finland, Israel, Netherlands, Switzerland, Australia, Canada, Brazil, Mexico
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AstraZenecaRecruitingAdv Solid Malig - H&N SCC, ATM Pro / Def NSCLC, Gastric, Breast and Ovarian CancerSpain, United States, Belgium, United Kingdom, France, Hungary, Canada, Korea, Republic of, Australia
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AmgenActive, not recruitingThyroid Eye DiseaseUnited States, Spain, Germany, Italy, France, United Kingdom
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Enyo PharmaNot yet recruitingAlport SyndromeSpain, United States, France, Germany
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Promethera TherapeuticsCompletedUrea Cycle Disorders | Crigler Najjar SyndromeIsrael, United Kingdom, Belgium, France, Italy
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Genzyme, a Sanofi CompanyCompletedAlport Syndrome Patients With eGFR Between 45-90 ml/Min/1.73 m2France, Germany, Australia, United States, United Kingdom, Canada
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University Hospital, AngersUnknownAcute Lymphoblastic Leukemia | Nephroblastoma | Hepatic Veno-Occlusive DiseaseFrance
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom
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Gynecologic Oncology GroupNational Cancer Institute (NCI)CompletedOsteoporosis | Ovarian Carcinoma | Hereditary Breast and Ovarian Cancer SyndromeUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingHemophilia A | Hemophilia B | Cystic Fibrosis | Sickle Cell Disease | Muscular Dystrophy, Duchenne | Fragile X Syndrome | Huntington Disease | Myotonic Dystrophy | Autosomal Recessive Polycystic Kidney Disease | Neurofibromatosis-Noonan Syndrome | Muscular Dystrophy, Becker | Invasive PreNatal Diagnosis in a... and other conditionsFrance
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Alnylam PharmaceuticalsCompletedAcute Hepatic PorphyriaUnited States, Belgium, Bulgaria, France, Italy, Mexico, Spain, Taiwan, United Kingdom, Netherlands, Korea, Republic of, Switzerland, Czechia, Poland, Finland, Australia, Germany, Israel, Norway, South Africa
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory Syndrome | Muckle-Wells Syndrome | Neonatal Onset Multisystem Inflammatory Disease | Cryopyrin-associated Periodic SyndromesGermany, France, Belgium, Canada, Spain, Switzerland, United Kingdom
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AmgenRecruitingBehçet DiseaseSpain, United Kingdom, Turkey, France, Greece, Italy, Israel, Switzerland
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University of LeicesterUnknownKidney CancerFrance, Netherlands, Sweden, Norway, Denmark, Portugal, Belgium, Croatia, Czech Republic, Greece, Italy, Poland, Slovenia, Spain, United Arab Emirates
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UNICANCERCompletedLetrozole in Preventing Breast Cancer in Postmenopausal Women With a BRCA1 or BRCA2 Mutation (LIBER)Breast Cancer | Hereditary Breast/Ovarian Cancer (brca1, brca2) | brca1 Mutation Carrier | brca2 Mutation CarrierFrance
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory Syndrome | Muckle-Wells Syndrome | Neonatal Onset Multisystem Inflammatory Disease | Cryopyrin-associated Periodic SyndromesGermany, France, Belgium, Canada, Spain, Switzerland, United Kingdom
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Minoryx Therapeutics, S.L.Active, not recruitingAdrenoleukodystrophySpain, United States, Hungary, France, Germany, Italy, Netherlands, United Kingdom
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Austria, Czechia, Finland, Hungary, Ireland, Italy, Netherlands, Norway, Poland, Portugal, Spain, Sweden, United Kingdom
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NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
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Viridian Therapeutics, Inc.Active, not recruitingThyroid Eye DiseaseUnited States, Spain, United Kingdom, Canada, Germany, Italy, Netherlands, Australia, France, Turkey
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Viking Therapeutics, Inc.RecruitingAdrenomyeloneuropathy Form (AMN) of X-linked Adrenoleukodystrophy (X-ALD)United States, France, Germany, Italy, United Kingdom
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Marinus PharmaceuticalsEnrolling by invitationTuberous Sclerosis ComplexUnited States, Spain, United Kingdom, China, Italy, France, Israel, Germany, Canada, Australia
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Cyprus, France, Germany, Greece, Italy, Japan, Korea, Republic of, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Taiwan, United Kingdom
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Gyroscope Therapeutics LimitedNovartis PharmaceuticalsActive, not recruitingMacular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal Disease | Macular AtrophyUnited States, Spain, United Kingdom, France, Germany, Australia, Netherlands, Poland
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Genzyme, a Sanofi CompanyTerminatedAlport SyndromeAustralia, United States, China, France, Germany, Spain, United Kingdom
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Janssen Research & Development, LLCCompletedAdenomatous Polyposis ColiUnited States, Germany, Korea, Republic of, France, Netherlands, Spain, Puerto Rico
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River 3 Renal Corp.RecruitingFocal Segmental Glomerulosclerosis | Alport SyndromeUnited States, Belgium, United Kingdom, France, Germany, Netherlands
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Jaeb Center for Health ResearchFoundation Fighting BlindnessActive, not recruitingUsher Syndrome, Type 2A | Retinitis Pigmentosa 39United States, Canada, France, Germany, Netherlands, United Kingdom
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth DiseaseUnited States
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ShireTerminatedMetabolic Diseases | Brain Diseases | Central Nervous System Diseases | Nervous System Diseases | Demyelinating Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Lysosomal Storage Diseases | Lipid Metabolism Disorders | Sphingolipidoses | Hereditary Central Nervous System Demyelinating Diseases and other conditionsUnited States, Denmark, France, Argentina, Belgium, Brazil, Canada, Germany, Japan, Turkey
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AstraZenecaRecruitingNeurofibromatosis Type 1Portugal, Spain, United Kingdom, Israel, France, Italy, Switzerland, Germany, Austria
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Novartis PharmaceuticalsCompletedCancerFrance, Australia, United States, Canada, United Kingdom
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Cellaion SAEnrolling by invitationUrea Cycle Disorder | Crigler-Najjar Syndrome | Acute on Chronic Liver FailureBelgium, Spain, France, Bulgaria, Poland
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Pharnext S.C.A.Premier Research Group plc; Eurofins Optimed; Synteract HCR (Syneos Health); Gr... and other collaboratorsActive, not recruitingCharcot-Marie-Tooth Disease, Type IAUnited States, Belgium, Canada, France, Netherlands, Spain, United Kingdom
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Novartis PharmaceuticalsCompletedBehcet DiseaseIndia, Turkey, Spain, Germany, Italy, France, Israel, Greece, Korea, Republic of, Hong Kong, United States, Egypt, Jordan, Singapore, Switzerland, Taiwan, Tunisia
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National Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Colon Mucinous Adenocarcinoma | Colon Signet Ring Cell Adenocarcinoma | Stage IIA Colon Cancer AJCC v7 | Stage IIB Colon Cancer AJCC v7 | Stage IIC Colon Cancer AJCC v7United States, Canada, Puerto Rico, Peru, South Africa
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Massachusetts General HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... and other collaboratorsCompletedNervous System Diseases | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Lou Gehrig's Disease | Hereditary Spastic ParaparesisUnited States, Canada
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Hospices Civils de LyonNot yet recruitingArteriovenous Malformations | Marfan Syndrome | Osler Rendu Disease | Vascular Anomaly | Lymphedema Primary | Cerebrospinal; DisorderFrance
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Marinus PharmaceuticalsActive, not recruitingTuberous Sclerosis ComplexUnited States, Spain, United Kingdom, Israel, Italy, Germany, France, Canada
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Pharnext S.C.A.Worldwide Clinical TrialsActive, not recruitingCharcot-Marie-Tooth DiseaseUnited States, Spain, Belgium, Italy, Israel, Canada, Denmark, France, Germany
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AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis 1 | Plexiform Neurofibroma (PN)United States, Canada, France, Italy, Germany, China, United Kingdom, Spain, Japan, Russian Federation, Australia, Poland, Brazil
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Pharnext SACompletedPhase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients (PLEO-CMT) (PLEO-CMT)Charcot-Marie-Tooth Disease Type 1AUnited States, United Kingdom, Belgium, Canada, France, Netherlands, Spain, Germany
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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University Hospital MuensterCompletedSoft Tissue Sarcoma | Acute Lymphoblastic Leukemia | Neuroblastoma | Wilms TumorGermany, France, United Kingdom, Italy
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AmgenCompletedBehçet's SyndromeUnited States, Korea, Republic of, Israel, Italy, Turkey, France, Germany, Greece, Lebanon, Japan
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University Hospital, LilleCSL Behring; Laboratoire français de Fractionnement et de Biotechnologies; Oc... and other collaboratorsTerminatedPneumococcal Infections | Pneumonia, Bacterial | Meningitis, Bacterial | Otitis Media | Chronic Sinus Infection | Streptococcal Infection | Antibody Deficiency | Complement Deficiency | Neisseria Infections | Haemophilus InfluenzaFrance
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National Cancer Institute (NCI)RecruitingSarcoma | Neuroblastoma | Retinoblastoma | Renal Cancer | Endocrine TumorsUnited States
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)United States, Canada, Belgium, Israel, Netherlands, United Kingdom, Germany, Spain, Japan, Brazil, Argentina, France, Greece, Italy
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Reata, a wholly owned subsidiary of BiogenCompletedAlport SyndromeUnited States, United Kingdom, Japan, Australia, France, Germany, Puerto Rico, Spain