- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Hereditary Angioedema in United Kingdom
Total 1441 results
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National Cancer Institute (NCI)RecruitingCancer | Hereditary Neoplasms | Genetic Predisposition to Cancer | EnvironmentUnited States
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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University of California, DavisCures Within Reach; Retina SocietyCompletedRetinitis PigmentosaUnited States
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Johns Hopkins UniversityCompleted
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University of Illinois at ChicagoCompletedRetinal DegenerationsUnited States
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The Cleveland ClinicCompletedRetinitis PigmentosaUnited States
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Wills EyeOkuvision GmbHWithdrawnRetinitis PigmentosaUnited States
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National Eye Institute (NEI)CompletedRetinitis PigmentosaUnited States
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National Eye Institute (NEI)CompletedRetinitis PigmentosaUnited States
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National Eye Institute (NEI)CompletedRetinitis PigmentosaUnited States
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Ray Therapeutics, Inc.The Vision Research and Assessment Institute (VRAI)RecruitingRetinitis PigmentosaUnited States
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Johns Hopkins UniversityActive, not recruiting
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Mayo ClinicSecond Sight Medical ProductsCompleted
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Johns Hopkins UniversityCompletedRetinitis PigmentosaUnited States
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National Eye Institute (NEI)Completed
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National Center for Complementary and Integrative...Completed
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Astellas Pharma Global Development, Inc.Active, not recruitingStargardt's Macular DystrophyItaly, United States, Israel, United Kingdom, Germany, Spain, Hungary, France
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Mayo ClinicUnity Health Toronto; Augusta University; Schering-PloughTerminatedAnemia | Liver Disease | HypoxemiaUnited States
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Nanoscope Therapeutics Inc.Completed
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Nanoscope Therapeutics Inc.Enrolling by invitationStargardt DiseaseUnited States
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan
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Akcea TherapeuticsRecruitingPregnancy | Hereditary Transthyretin-mediated Amyloidosis With PolyneropathyUnited States
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University of MichiganNational Eye Institute (NEI)Recruiting
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Aldeyra Therapeutics, Inc.Completed
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Second Sight Medical ProductsCompletedRetinitis PigmentosaUnited States
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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University of MichiganCures Within ReachRecruitingRetinitis PigmentosaUnited States
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Duke UniversityFoundation Fighting BlindnessWithdrawnChoroideremiaUnited States
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Nova Southeastern UniversityNational Eye Institute (NEI)Active, not recruitingRetinitis PigmentosaUnited States
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Georgetown UniversityNational Cancer Institute (NCI); Virginia Commonwealth UniversityEnrolling by invitation
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University of Kansas Medical CenterActive, not recruitingColorectal Cancer | Lynch SyndromeUnited States
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University of California, San DiegoNew York University; Heinrich-Heine University, Duesseldorf; Universität TübingenRecruitingGenetic Disease | Mitochondrial Encephalomyopathies | Neonatal Encephalopathy | Mutation | Hereditary Spastic Paraplegia | White Matter Disease | Spastic ParaplegiaUnited States
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Virginia Commonwealth UniversityNot yet recruitingAmyloidosis, HereditaryUnited States
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National Eye Institute (NEI)RecruitingRetinitis PigmentosaUnited States
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Minnesota HealthSolutionsJohns Hopkins University; Second Sight Medical ProductsCompleted
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Wills EyeRetina Implant AGWithdrawnRetinitis PigmentosaUnited States
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Johns Hopkins UniversityCompleted
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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City of Hope Medical CenterNational Cancer Institute (NCI)Active, not recruitingBRCA1 Syndrome | BRCA2 Syndrome | No Evidence of Disease | Hereditary Ovarian Carcinoma | Hereditary Female Breast CarcinomaUnited States
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National Cancer Institute (NCI)CompletedLynch SyndromeUnited States
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University of California, DavisActive, not recruitingDiabetic Retinopathy | Retinitis Pigmentosa | Non-exudative Age-related Macular Degeneration | Retina Vein Occlusion | Hereditary Macular DegenerationUnited States
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OcugenRecruitingRetinitis PigmentosaUnited States
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Complement TherapeuticsRecruitingEye Diseases | Macular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal Disease | Macular AtrophyUnited Kingdom, United States
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Washington University School of MedicineThe Foundation for Barnes-Jewish HospitalTerminatedLynch Syndrome | Hereditary Breast and Ovarian CancerUnited States
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Cedars-Sinai Medical CenterCalifornia Institute for Regenerative Medicine (CIRM)Recruiting
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University of California, San FranciscoUniversity of California, BerkeleyRecruiting