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Clinical Trials on Hereditary Ataxia in United States
Total 1620 results
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National Eye Institute (NEI)Enrolling by invitation
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ShireCompletedHereditary AngioedemaUnited States
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Ionis Pharmaceuticals, Inc.Active, not recruitingHereditary AngioedemaNetherlands, United States
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Cornea Research Foundation of AmericaCompletedBullous Keratopathy | Fuchs' Endothelial Corneal Dystrophy | Iridocorneal Endothelial Syndrome | Posterior Polymorphous DystrophyUnited States
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National Human Genome Research Institute (NHGRI)CompletedBreast CancerUnited States
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ShireTakeda Development Center Americas, Inc.No longer availableAngioedema | Hereditary Angioedema (HAE)United States, Canada, Germany, Hungary, Spain
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The University of Texas Medical Branch, GalvestonTerminatedHereditary Coproporphyria | Acute Intermittent Porphyria | Variegate PorphyriaUnited States
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University of Southern CaliforniaStanford UniversityCompletedHereditary Breast and Ovarian CancerUnited States
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy (HIBM)United States
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The University of Texas Medical Branch, GalvestonActive, not recruitingHereditary Coproporphyria | Acute Intermittent Porphyria | Variegate PorphyriaUnited States
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University of PittsburghCompletedLynch Syndrome | Hereditary Diffuse Gastric Cancer | FAP | Peutz-Jeghers Syndrome | Juvenile Polyposis SyndromeUnited States
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Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, Netherlands
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ShireCompletedHereditary AngioedemaUnited States
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Memorial Sloan Kettering Cancer CenterHarvard University; Broad InstituteActive, not recruitingLynch Syndrome | Hereditary Colonic Polyposis SyndromesUnited States
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Emory UniversityCompletedHereditary Breast and Ovarian CancerUnited States
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University of SouthamptonUnknownKeratoconus | Fuchs Dystrophy | Corneal DiseaseUnited Kingdom
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ShireCompletedHereditary Angioedema (HAE)United States, Germany, Spain, Sweden
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Washington University School of MedicineCompletedVasculopathy, Retinal, With Cerebral Leukodystrophy | Cerebroretinal Vasculopathy, HereditaryUnited States
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Arizona State UniversityRecruitingStroke | Aphasia | Apraxia of SpeechUnited States
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The Cleveland ClinicCompletedHereditary Hemorrhagic Telangiectasia | Idiopathic Vascular EctasiaUnited States
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National Human Genome Research Institute (NHGRI)Completed
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CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Germany, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom
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Opus Genetics, IncRecruiting
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic NeuropathyCanada, Germany, United Kingdom
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Geisinger ClinicNational Cancer Institute (NCI)CompletedLynch SyndromeUnited States
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State University of New York at BuffaloHadley Jo FoundationCompletedMitochondrial Diseases | Optic Atrophy | Neurodegenerative Disease, HereditaryUnited States
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State University of New York at BuffaloThe Callum McKeefery and Nikki Albano McKeefery Pediatric Division of Genetics...CompletedMitochondrial Diseases | Optic Atrophy | Neurodegenerative Disease, HereditaryUnited States
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University of PittsburghCompleted
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Santen Inc.ActualEyes Inc.Active, not recruitingFuchs Endothelial Corneal DystrophyUnited States, France, India
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ShireDyax Corp.CompletedHereditary Angioedema (HAE)United States, Canada, Germany, Italy, Jordan, Puerto Rico, United Kingdom
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MD Stem CellsRecruitingGlaucoma | Age-Related Macular Degeneration | Macular Degeneration | Retinitis Pigmentosa | Leber Hereditary Optic Neuropathy | Optic Atrophy | Blindness | Optic Neuropathy | Vision, Low | Retinal Disease | Stargardt Disease | Maculopathy | Retinopathy | Optic Nerve Disease | Nonarteritic Ischemic Optic Neuropathy | Vision... and other conditionsUnited States, United Arab Emirates
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ShireCompletedHereditary Angioedema (HAE)United States, Canada, Australia, Austria, Colombia, Germany, Hungary, Israel, Italy, Spain
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Tufts UniversityAmerican Pistachio GrowersRecruitingEye Diseases | Macular Degeneration | Retinal Degeneration | Retinal DiseasesUnited States
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Memorial Sloan Kettering Cancer CenterSOUTH ASIAN COUNCIL FOR SOCIAL SERVICESActive, not recruitingHealthcare Access for Taxi DriversUnited States
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University of California, San FranciscoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedAcute Intermittent Porphyria (AIP) | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP)United States
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MeiraGTx UK II LtdSyne Qua Non LimitedCompletedEye Diseases | Retinal Diseases | Eye Diseases, Hereditary | Leber Congenital Amaurosis (LCA)United States, United Kingdom
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ShireCompletedHereditary AngioedemaUnited States
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ShireCompletedHereditary Angioedema (HAE)United States, United Kingdom, Germany, Canada, Italy, Jordan, Puerto Rico
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ShireCompletedHereditary Angioedema (HAE)Spain, Israel, United States, Hungary, Germany, Canada, Romania
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Nanoscope Therapeutics Inc.CompletedEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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ShireTakeda Development Center Americas, Inc.CompletedHereditary Angioedema (HAE)Canada, United States, Puerto Rico
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Massachusetts General HospitalNational Cancer Institute (NCI); Boston Medical CenterCompletedGenetic TestingUnited States
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National Eye Institute (NEI)CompletedHealthy Volunteer | Retinal Disease | Inherited Retinal DegenerationUnited States
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Nanoscope Therapeutics Inc.Enrolling by invitationEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Fox Chase Cancer CenterRecruiting
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PYC TherapeuticsRecruitingRetinitis Pigmentosa | Eye Diseases, Hereditary | Retinal Dystrophies | Retinal Dystrophy Rod | Retinal Dystrophy Rod ProgressiveUnited States, Australia
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Georgetown UniversityVirginia Commonwealth University; Cornell UniversityCompletedHereditary Breast and Ovarian CancerUnited States
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Ultragenyx Pharmaceutical IncCompletedGNE Myopathy | Hereditary Inclusion Body Myopathy (HIBM)United States, Israel
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Boston UniversityNational Institute on Minority Health and Health Disparities (NIMHD); University... and other collaboratorsRecruitingLynch Syndrome | Hereditary Breast and Ovarian CancerUnited States
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CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom