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Clinical Trials on Hereditary Diseases in Poland
Total 20952 results
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Oregon Health and Science UniversityTerminatedImmune System Diseases | Lipid Metabolism, Inborn Errors | Mevalonic Aciduria | Mevalonate Kinase Deficiency | Periodic Fever Syndromes, HereditaryUnited States
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Editas Medicine, Inc.CompletedEye Diseases | Retinal Degeneration | Eye Diseases, Hereditary | Vision Disorders | Blindness | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Netherlands, France, Germany
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Editas Medicine, Inc.Active, not recruitingRetinal Degeneration | Eye Diseases, Hereditary | Vision Disorders | Leber Congenital Amaurosis 10 | Inherited Retinal Dystrophies | Retinal Disease | Eye Disorders CongenitalUnited States
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University of BirminghamActive, not recruitingWolfram SyndromeFrance, United Kingdom, Poland, Spain
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Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, France, Netherlands, Spain, United Kingdom, Belgium, Bulgaria, Canada, Denmark, Germany, Israel, Italy, Poland, Turkey
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Atsena Therapeutics Inc.Active, not recruitingLeber Congenital Amaurosis | LCA | LCA1United States
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Ionis Pharmaceuticals, Inc.RecruitingHereditary AngioedemaUnited States, Puerto Rico, Belgium, Bulgaria, Canada, France, Germany, Israel, Italy, Netherlands, Poland, Spain, Turkey, United Kingdom
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ReNeuron LimitedActive, not recruitingRetinitis PigmentosaUnited States, United Kingdom, Spain
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Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, WorcesterCompletedLeber Congenital AmaurosisUnited States
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Applied Genetic Technologies CorpCompletedX-Linked Retinitis PigmentosaUnited States
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CSL BehringCompletedHereditary AngioedemaBulgaria, United States, Poland, Spain, Hungary, United Kingdom, Russian Federation, Macedonia, The Former Yugoslav Republic of, Argentina, Australia, Canada, Czech Republic, Israel, Romania, Sweden
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BiogenCompletedChoroideremiaUnited States, Germany, France
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Kowa Research Institute, Inc.RecruitingFuchs Endothelial Corneal DystrophyUnited States, Germany, Spain, Canada, United Kingdom, Denmark
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | Prophylaxis | HAEAustria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Switzerland, United Kingdom, United States, Australia, Hong Kong, Korea, Republic of, New Zealand, Serbia, Slovakia, South Africa, Spain
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Amsterdam UMC, location VUmcODASRecruiting
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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PYC TherapeuticsNot yet recruitingEye Diseases | Retinal Degeneration | Retinal Dystrophies | Retinal Disease | Retinitis Pigmentosa 11United States
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Kowa Research Institute, Inc.RecruitingFuchs Endothelial Corneal DystrophyUnited States, United Kingdom, Spain, Germany, Canada, Denmark
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Foundation Fighting BlindnessUnited States Department of DefenseCompleted
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Australia, Bulgaria, Canada, France, Germany, Greece, Hungary, Israel, Italy, Japan, Netherlands, New Zealand, North Macedonia, Poland, Portugal, Puerto Rico, Romania, Slovakia, Spain, United Kingdom
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Amsterdam UMC, location VUmcRecruitingRetinoblastoma | Trilateral RetinoblastomaNetherlands
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Applied Genetic Technologies CorpNational Eye Institute (NEI)Completed
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Hungary, Israel, Italy, Netherlands, New Zealand, North Macedonia, Poland, Spain, United Kingdom, Australia, Germany, South Africa, Austria, Portugal, Slovakia, Romania, Canada, Saudi Arabia, Japa...
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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Amsterdam UMC, location VUmcCompleted
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Endogena Therapeutics, IncActive, not recruitingRetinitis Pigmentosa | Retinitis Pigmentosa SyndromeUnited States
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Beacon TherapeuticsEnrolling by invitationX-Linked Retinitis PigmentosaUnited States
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Hoffmann-La RocheActive, not recruitingHemophilia A | Mild Hereditary Factor VIII Deficiency Disease Without Inhibitor | Moderate Hereditary Factor VIII Deficiency Disease Without InhibitorUnited States, Netherlands, Belgium, France, Germany, South Africa, Spain, Canada, United Kingdom, Poland
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Data Collection Analysis Business ManagementPAS Research ServicesUnknownHereditary CancerUnited States
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BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
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Applied Genetic Technologies CorpActive, not recruitingAchromatopsiaUnited States, Israel
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Clementia Pharmaceuticals Inc.TerminatedExostoses, Multiple HereditaryUnited States, Spain, Canada, Japan, Italy, Portugal, United Kingdom, Turkey, Australia, Belgium, France, Netherlands
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Academisch Medisch Centrum - Universiteit van Amsterdam...UnknownPiebaldism | Segmental Vitiligo | Non-segmental VitiligoNetherlands
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4D Molecular TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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ProQR TherapeuticsCompletedEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, Canada, France
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Applied Genetic Technologies CorpNational Eye Institute (NEI)Active, not recruitingAchromatopsiaUnited States
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Amsterdam University Medical CenterEnrolling by invitationRetinoblastoma | Neurocognitive Dysfunction | Health-Related BehaviorNetherlands
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Neurotech PharmaceuticalsCompletedRetinitis PigmentosaUnited States
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Oregon Health and Science UniversityActive, not recruitingAnterior Cutaneous Nerve Entrapment SyndromeUnited States
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National Center for Research Resources (NCRR)Oregon Health and Science UniversityTerminatedRetinitis Pigmentosa | Usher SyndromeUnited States
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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ShireTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, France, Netherlands, Spain, Hungary, Italy, Canada, Poland, Japan, Germany
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Neurotech PharmaceuticalsCompletedRetinitis PigmentosaUnited States
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Immunovant Sciences GmbHRecruitingThyroid Eye DiseaseUnited States, Italy, Poland, United Kingdom, Canada, Israel, Germany, Japan, Georgia
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Bartlomiej GuzikAbbottRecruitingCoronary Artery Disease | Ischemic Heart Disease | Microvascular Angina | Vasospastic Angina | Ischemia and No Obstructive Coronary ArteriesPoland
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AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis Type 1United States, Spain, Poland, Russian Federation
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TakedaTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, Spain, Netherlands, Hungary, Italy, Canada, Germany, France, Japan, Poland
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Brothers Hospitallers Hospital in CracowJagiellonian UniversityRecruitingMetabolic Syndrome | CholelithiasisPoland
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Jakub AntczakCompleted