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Clinical Trials on Hereditary Motor and Sensory Neuropathy
Total 7493 results
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Humanitas Hospital, ItalyRecruitingCoronary Artery Disease | Diabetes Mellitus | Contrast-induced Nephropathy | Lactic Acidosis With Diabetes Mellitus | Metformin Associated Lactic AcidosisItaly
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Seattle Children's HospitalActive, not recruitingMelanoma | Soft Tissue Sarcoma | Carcinoma | Osteosarcoma | Ewing Sarcoma | Rhabdoid Tumor | Neuroblastoma | Retinoblastoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Synovial Sarcoma | Desmoplastic Small Round Cell Tumor | Germ Cell Tumor | Pediatric Solid Tumor | Clear Cell Sarcoma | Malignant Peripheral Nerve Sheath...United States
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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Masonic Cancer Center, University of MinnesotaRecruiting
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Assistance Publique - Hôpitaux de ParisBraintaleNot yet recruitingX-linked Adrenoleukodystrophy
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Minoryx Therapeutics, S.L.RecruitingCerebral Adrenoleukodystrophy (cALD)United States, Brazil, Argentina
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingStage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor | Recurrent Kidney Wilms Tumor | Anaplastic Kidney Wilms TumorUnited States, Canada, Puerto Rico, Australia, New Zealand, Saudi Arabia
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National Cancer Institute (NCI)RecruitingNeurofibromatosis Type 1 | Low Grade Glioma | Visual Pathway GliomaUnited States, Canada, Puerto Rico
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom
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University Hospital, ToursCompletedTuberous Sclerosis Complex | LymphangioleiomyomatosisFrance
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser... and other collaboratorsCompletedX-linked AdrenoleukodystrophyUnited States
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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Shenzhen Geno-Immune Medical InstituteUnknown
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NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
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Masonic Cancer Center, University of MinnesotaWithdrawnCerebral Adrenoleukodystrophy
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FDA Office of Orphan Products DevelopmentHugo W. Moser Research Institute at Kennedy Krieger, Inc.Completed
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Far Eastern Memorial HospitalNational Taiwan University Hospital; Fu Jen Catholic UniversityUnknownAdrenoleukodystrophyTaiwan
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Fairview University Medical CenterUnknownHemophagocytic Lymphohistiocytosis | Graft Versus Host Disease | Chediak-Higashi Syndrome | Virus-Associated Hemophagocytic Syndrome | X-Linked Lymphoproliferative Syndrome | Familial Erythrophagocytic LymphohistiocytosisUnited States
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Maria Eugenia Galván PlataCentro de Investigación Biomédica de Michoacán.; Hospital General Regional... and other collaboratorsUnknownType 2 Diabetes Mellitus | Chronic Kidney Disease stage3 and 4Mexico
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Community Pharmacology Services LtdKeneric HealthcareNot yet recruitingDiabetic Foot Ulcer | Diabetic Foot Ulcer Neuropathic | Diabetic Foot Ulcer Ischemic
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George ZogopoulosRecruitingPancreatic Cancer | Bile Duct Cancer | Pancreas Cancer | Gallbladder Cancer | Pancreas Neoplasm | Familial Pancreatic Cancer | Duodenal Cancer | Hereditary Cancer | Pancreas Cyst | Ampullary Cancer | Pancreatic Precancerous ConditionCanada
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Vanderbilt UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingNeurofibromatosis Type 1 | Reading Disability | NF1 | Learning DisabilityUnited States
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingIntellectual Disability | Tuberous Sclerosis | Autism DisorderUnited States
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Vanderbilt UniversityNational Institute of Neurological Disorders and Stroke (NINDS)CompletedNeurofibromatosis Type 1 | Reading DisabilitiesUnited States
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University Hospital, ToulouseCompleted
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Boston Children's HospitalNational Eye Institute (NEI); Howard Hughes Medical InstituteRecruitingOcular Motility Disorders | Facial Palsy | Synkinesis | Sixth Nerve Palsy | Mobius Syndrome | Congenital Fibrosis of Extraocular Muscles | Duane Retraction Syndrome | Duane Radial Ray Syndrome | Brown Syndrome | Marcus Gunn Syndrome | Strabismus Congenital | Horizontal Gaze Palsy | Horizontal Gaze Palsy With Progressive... and other conditionsUnited States
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Mayo ClinicSuspendedDiabetes Mellitus | Chronic Kidney Diseases | Diabetic NephropathiesUnited States
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Centre Hospitalier de Charleville-MézièresInstitut PasteurCompletedHemorrhagic Fever With Renal Syndrome | Nephropathia EpidemicaFrance
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ChemoCentryxCompletedType 2 Diabetes Mellitus | Diabetic NephropathyNetherlands
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Ain Shams UniversityCompleted
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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Viking Therapeutics, Inc.RecruitingAdrenomyeloneuropathy Form (AMN) of X-linked Adrenoleukodystrophy (X-ALD)United States, France, Germany, Italy, United Kingdom
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Massachusetts General HospitalUniversity of Toronto; NeurOptics Inc.UnknownALS (Amyotrophic Lateral Sclerosis) | PSP - Progressive Supranuclear Palsy | PD - Parkinson's Disease | AD - Alzheimer's DiseaseUnited States
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St. Olavs HospitalNorwegian University of Science and Technology; The Research Council of Norway and other collaboratorsRecruitingSexual Dysfunctions, Psychological | Sleep Disturbance | Post Traumatic Stress Disorder | Depression, Anxiety | Activity, Motor | Pelvic Pain Syndrome | Rape Sexual Assault | Pelvic Floor Myalgia | Cortisol DeficiencyNorway
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingDiabetes Complications | Type 1 Diabetes | Diabetic Kidney Disease | Diabetic Nephropathies | Autoimmune DiabetesUnited States
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Talaris Therapeutics Inc.Duke UniversityNo longer availableMetachromatic LeukodystrophyUnited States
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NYU Langone HealthWithdrawnEpilepsy | Tuberous Sclerosis | Dravet Syndrome | Focal Seizures | Lennox-Gastaut SyndromeUnited States
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Washington University School of MedicineCompletedNeurofibromatosis Type 1 | Pediatric Brain TumorUnited States
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The University of Texas Health Science Center,...Society for Pediatric DermatologyCompletedTuberous Sclerosis | Neurofibromatoses | Neurofibroma | AngiofibromaUnited States
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National Institute of Neurological Disorders and...CompletedMuscle Rigidity | Spasm | Stiff Man SyndromeUnited States
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National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiCompletedMetabolism, Inborn Errors | Leukodystrophy, Globoid Cell | Tay-Sachs Disease | Porphyria, ErythropoieticUnited States
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Ontario Neurodegeneration Disease Research InitiativeCompletedStroke | Parkinson Disease | Amyotrophic Lateral Sclerosis | Alzheimer Disease | Frontotemporal DementiaCanada
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University of PittsburghNational Institute on Disability, Independent Living, and Rehabilitation...CompletedCerebral Palsy | Amyotrophic Lateral Sclerosis | Traumatic Brain Injury | Speech Disorders | Brain Stem StrokeUnited States
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University of SienaRecruitingBehcet Syndrome | Uveitis | Hereditary Autoinflammatory Diseases | Schnitzler Syndrome | Scleritis | PFAPA Syndrome | Still Disease | Autoinflammatory Syndrome, Unspecified | Vexas SyndromeEgypt, Spain, Turkey, Italy, Saudi Arabia, Greece, Belgium, United States, Algeria, Brazil, Germany, Ghana, Iran, Islamic Republic of, Lebanon, Morocco, Poland, Portugal, Romania, Taiwan
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Western Sydney Local Health DistrictRecruitingFamilial Adenomatous PolyposisAustralia
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Memorial Sloan Kettering Cancer CenterActive, not recruitingMesothelioma | Wilms Tumor | Pleural MesotheliomaUnited States
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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Karuna Labs Inc.CompletedRheumatoid Arthritis | Low Back Pain | Chronic Pain | Carpal Tunnel Syndrome | Fibromyalgia | Complex Regional Pain Syndromes | Upper Extremity Dysfunction | Phantom Limb Pain | Repetitive Strain InjuryUnited States
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Stine Maarbjerg, MD PhDCompletedMultiple Sclerosis | Trigeminal Neuralgia | Pain, Neuropathic
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Barbara Ann Karmanos Cancer InstituteNational Cancer Institute (NCI); Children's Hospital of MichiganTerminatedUnspecified Childhood Solid Tumor, Protocol Specific | Osteosarcoma | Neuroblastoma | Retinoblastoma | Recurrent/Refractory Childhood Hodgkin Lymphoma | Wilms Tumor and Other Childhood Kidney Tumors | Childhood Choroid Plexus Tumor | Childhood Soft Tissue Sarcoma | Childhood Medulloblastoma | Childhood... and other conditionsUnited States