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Clinical Trials on Hereditary Spastic Paraplegia
Total 3536 results
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Hugo W. Moser Research Institute at Kennedy Krieger...CompletedTuberous Sclerosis Complex | Autism | Self-injuryUnited States
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Pfizer's Upjohn has merged with Mylan to form Viatris...TerminatedAdenomatous Polyposis ColiItaly, United States, Belgium, Spain, Puerto Rico, Sweden, Israel, Czechia, Hong Kong, Hungary, Slovakia, South Africa, Ukraine, United Kingdom
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National Cancer Institute (NCI)CompletedPancreatic Neuroendocrine Carcinoma | Multiple Endocrine Neoplasia Type 1United States
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Queen's University, BelfastUniversity of SussexUnknownRetinitis Pigmentosa | Low Vision | Albinism | Stargardt Disease 1 | Stargardt Disease 3 | Stargardt Disease 4United Kingdom
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National Cancer Institute (NCI)CompletedSarcoma | Lymphoma | Neuroblastoma | Wilm's TumorUnited States
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Merck Sharp & Dohme LLCTerminatedAdenomatous Polyposis Coli
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University College, LondonUniversity of IowaUnknownCharcot-Marie-Tooth Disease, Type IA | Charcot-Marie-Tooth Disease Type 2A | Charcot-Marie-Tooth Disease, Type IB | Charcot-Marie-Tooth Disease, Type XUnited Kingdom
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Sarcoma Alliance for Research through CollaborationNational Cancer Institute (NCI)CompletedSarcoma | Neurofibromatosis Type 1United States
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National Taiwan University HospitalCompleted
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Masonic Cancer Center, University of MinnesotaWithdrawn
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Skin Neoplasm | Nodular Basal Cell Carcinoma of SkinAustralia
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University of MinnesotaNo longer availableX-linked AdrenoleukodystrophyUnited States
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New York Medical CollegeTerminatedSarcoma | Neuroblastoma | Wilms' Tumor | Refractory Solid Tumor | Recurrent Solid TumorUnited States
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MedDay Pharmaceuticals SACompletedAdrenoleukodystrophy | Adrenomyeloneuropathy | AMNFrance, Germany, Spain
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University of Sao PauloUnknownFamilial Adenomatous PolyposisBrazil
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Novartis PharmaceuticalsCompletedTreatment for Basal Cell Carcinomas (BCCs) in Gorlin Syndrome PatientsAustria, Switzerland
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Children's Hospital Medical Center, CincinnatiNovartisCompletedTuberous Sclerosis | Subependymal Giant Cell AstrocytomaUnited States
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Eunice Kennedy Shriver National Institute of Child...Food and Drug Administration (FDA)TerminatedAdrenoleukodystrophy | AdrenomyeloneuropathyUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD FoundationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophyNetherlands
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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University Hospital, AntwerpKom Op Tegen Kanker; Stichting tegen KankerRecruitingEsophageal Cancer | Ovarian Cancer | Pancreas Cancer | Liver CancerBelgium
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National Tuberous Sclerosis AssociationRecruitingTuberous Sclerosis | LymphangioleiomyomatosisUnited States, Canada
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Brigham and Women's HospitalMassachusetts General HospitalRecruitingTuberous Sclerosis Complex | LymphangioleiomyomatosisUnited States
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Medical University of BialystokUniversity of BialystokRecruitingOptic Neuritis | Ischemic Optic Neuropathy | Traumatic Optic Neuropathy | Toxic Optic Neuropathy | Compressive Optic Neuropathy | Hereditary Optic NeuropathiesPoland
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Poxel SANot yet recruiting
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Zarife SahenkRecruitingCharcot-Marie-Tooth Disease | Peripheral Neuropathy | Chronic Inflammatory Demyelinating PolyneuropathyUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...IRCCS Azienda Ospedaliero-Universitaria di Bologna; Hospital Clinic of Barcelona and other collaboratorsRecruitingFamilial Adenomatous PolyposisNetherlands
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George ZogopoulosRecruitingPancreatic Cancer | Bile Duct Cancer | Pancreas Cancer | Gallbladder Cancer | Pancreas Neoplasm | Familial Pancreatic Cancer | Duodenal Cancer | Hereditary Cancer | Pancreas Cyst | Ampullary Cancer | Pancreatic Precancerous ConditionCanada
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Masonic Cancer Center, University of MinnesotaRecruitingCerebral Adrenoleukodystrophy | Adrenoleukodystrophy | ALD (Adrenoleukodystrophy)United States
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National Cancer Institute (NCI)CompletedNeurofibromatosis | MPNSTUnited States
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National Cancer Institute (NCI)CompletedLeukemia | Solid Tumor | Sickle Cell Disease | NeurofibromatosisUnited States
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Cellaion SATerminatedUrea Cycle Disorder | Crigler-Najjar Syndrome | Acute on Chronic Liver FailureBelgium, Spain, France, Bulgaria, Poland
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SpringWorks Therapeutics, Inc.AvailableNeurofibromatosis Type 1-Associated Plexiform Neurofibromas | Histiocytic Neoplasm | Other MAP-K Pathway Driven Diseases
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Sarcoma Alliance for Research through CollaborationUnited States Department of Defense; AstraZenecaCompletedNeurofibromatosis 1 | Malignant Peripheral Nerve Sheath TumorsUnited States
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Florida International UniversityNicklaus Children's Hospital f/k/a Miami Children's Hospital; Cornelia T. Bailey...CompletedOsteosarcoma | Ewing Sarcoma | Rhabdomyosarcoma | Wilms Tumor | Sarcoma, Spindle Cell | Sarcoma Rhabdoid | Childhood Sarcoma of Soft TissueUnited States
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CENTOGENE GmbH RostockWithdrawnMuscle Weakness | Peripheral NeuropathyEgypt, Germany, India, Sri Lanka
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Ascend Biopharmaceuticals LtdSuspendedBasal Cell Carcinoma in Basal Cell Nevus SyndromeUnited States
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Onofre, Aurora Pujol, M.D.Completed
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Novartis PharmaceuticalsCompleted
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Cancer Prevention Pharmaceuticals, Inc.CompletedFamilial Adenomatous PolyposisUnited States, Belgium, Germany, Canada, Netherlands, Spain, United Kingdom
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedColorectal Cancer | Familial Adenomatous PolyposisUnited States
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Charite University, Berlin, GermanyUnknownColorectal Cancer | Crohn Disease | Ulcerative Colitis | Familial Adenomatous Polyposis | Crohn Colitis | Ulcerative Colitis Chronic | Ulcerative Colitis in Remission | Ileal PouchGermany
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Hugo W. Moser Research Institute at Kennedy Krieger...TerminatedAdrenoleukodystrophyUnited States
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Tel-Aviv Sourasky Medical CenterTel Aviv UniversityUnknownFamilial Adenomatous PolyposisIsrael
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Peking Union Medical College HospitalShijiazhuang Yiling Pharmaceutical Co. LtdUnknownEpilepsy | Tuberous Sclerosis Complex | Aspirin | Cognitive Decline | Skin LesionsChina
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Onofre, Aurora Pujol, M.D.Instituto de Salud Carlos III; Fundacion Hesperia; ELA España AssociationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophySpain
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Onofre, Aurora Pujol, M.D.Ministerio de Sanidad, Servicios Sociales e Igualdad; Fundacion HesperiaCompleted
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National Heart, Lung, and Blood Institute (NHLBI)CompletedTuberous Sclerosis | Lymphangioleiomyomatosis | LymphangioleiomyomasUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyUnited States
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National Cancer Institute (NCI)CompletedMultiple Endocrine Neoplasia Type 2 | Medullary Thyroid CarcinomaUnited States