- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Hereditary Angioedema
Total 2659 results
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Ankara Universitesi TeknokentCompleted
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Retina Implant AGWithdrawnRetinitis PigmentosaGermany
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University of Sao PauloCompletedRetinitis PigmentosaBrazil
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Red de Terapia CelularFundacion para la Formacion e Investigacion Sanitarias de la Region de Murcia and other collaboratorsCompleted
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University Health Network, TorontoFoundation Fighting BlindnessUnknown
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Hillel Yaffe Medical CenterTechnion, Israel Institute of TechnologyUnknownRetinitis Pigmentosa
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Johns Hopkins UniversityCompletedRetinitis PigmentosaUnited States
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AllerganCompletedRetinitis PigmentosaFrance, United States, Germany, Portugal
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National Eye Institute (NEI)Completed
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Azienda Policlinico Umberto ICompletedRetinitis PigmentosaItaly
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National Center for Complementary and Integrative...Completed
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Mayo ClinicExact Sciences CorporationRecruitingLynch Syndrome | Colorectal CarcinomaUnited States
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Ann-Sofie BackmanThe Swedish Research CouncilRecruitingLynch Syndrome | Colon Cancer | Colon NeoplasmSweden, Denmark, Italy, Poland
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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City of Hope Medical CenterNational Cancer Institute (NCI)Active, not recruitingBRCA1 Syndrome | BRCA2 Syndrome | No Evidence of Disease | Hereditary Ovarian Carcinoma | Hereditary Female Breast CarcinomaUnited States
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Batman Training and Research HospitalCompletedCorneal Dystrophy | Macular Dystrophy | Hyperemesis Gravidarum - SevereTurkey
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Oslo University HospitalUniversity of Oslo; Norwegian National Advisory Unit on Rare Disorders (NKSD); Foreningen for MuskelsykeEnrolling by invitationHereditary Motor and Sensory Neuropathy | Polyneuropathies | Charcot-Marie-ToothNorway
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Icare Finland OyUnknownCorneal Dystrophy | Corneal Degeneration | Corneal Sensation Reduced | Corneal Transplant Failure | Herpetic Keratitis
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University Hospital, Strasbourg, FranceTerminated
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OcugenRecruitingStargardt DiseaseUnited States
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Akcea TherapeuticsRecruitingPregnancy | Hereditary Transthyretin-mediated Amyloidosis With PolyneropathyUnited States
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University of California, San DiegoNew York University; Heinrich-Heine University, Duesseldorf; Universität TübingenRecruitingGenetic Disease | Mitochondrial Encephalomyopathies | Neonatal Encephalopathy | Mutation | Hereditary Spastic Paraplegia | White Matter Disease | Spastic ParaplegiaUnited States
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University of South FloridaUniversity of Miami; National Institutes of Health (NIH); University of KansasCompletedAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | Hereditary Spastic Paraplegia
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University Hospital, AngersNot yet recruitingNicotinamide Adverse Reaction
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Unity Health TorontoNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingHereditary Hemorrhagic TelangiectasiaCanada, United States, Netherlands
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Alnylam PharmaceuticalsApproved for marketingAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid Polyneuropathies
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Hoffmann-La RocheActive, not recruitingHemophilia A | Mild Hereditary Factor VIII Deficiency Disease Without Inhibitor | Moderate Hereditary Factor VIII Deficiency Disease Without InhibitorUnited States, Netherlands, Belgium, France, Germany, South Africa, Spain, Canada, United Kingdom, Poland
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University of Kansas Medical CenterActive, not recruitingColorectal Cancer | Lynch SyndromeUnited States
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Ohio State University Comprehensive Cancer CenterCompletedColorectal Cancer | Lynch SyndromeUnited States
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Vejle HospitalCompletedColorectal Cancer | Lynch Syndrome | HNPCCDenmark
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University Medical Center GroningenMaastricht University Medical Center; Erasmus Medical Center; Medtronic - MITG; Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA) and other collaboratorsCompletedLynch Syndrome | Small Bowel NeoplasiaNetherlands
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Mayo ClinicUnity Health Toronto; Augusta University; Schering-PloughTerminatedAnemia | Liver Disease | HypoxemiaUnited States
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OcugenRecruitingRetinitis PigmentosaUnited States
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Mahidol UniversityNot yet recruitingRetinitis PigmentosaThailand
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Power Life Sciences Inc.Not yet recruitingRetinitis Pigmentosa
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2C Tech CorpORA, Inc.Not yet recruitingRetinitis Pigmentosa
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Peking University Third HospitalRecruitingSafety and Tolerability Study of Gene Editing Drug ZVS203e in Participants With Retinitis PigmentosaRetinitis PigmentosaChina
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University College, LondonMedical Research Council; Moorfields Eye Hospital NHS Foundation TrustRecruiting
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University of MichiganCures Within ReachRecruitingRetinitis PigmentosaUnited States
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University Hospital, Strasbourg, FranceRecruitingRetinitis PigmentosaFrance
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Sheba Medical CenterNot yet recruiting
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University of California, DavisCures Within Reach; Retina SocietyCompletedRetinitis PigmentosaUnited States
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STZ eyetrialActive, not recruiting
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University Hospital TuebingenCompletedRetinitis PigmentosaGermany
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BiogenCompletedChoroideremiaUnited States, Germany, France
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Novartis PharmaceuticalsActive, not recruitingRetinitis PigmentosaSweden
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Centre d'Etude des Cellules SouchesActive, not recruitingRetinitis PigmentosaFrance
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jCyte, IncCalifornia Institute for Regenerative Medicine (CIRM)CompletedRetinitis PigmentosaUnited States
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Duke UniversityFoundation Fighting BlindnessWithdrawnChoroideremiaUnited States
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Nova Southeastern UniversityNational Eye Institute (NEI)Active, not recruitingRetinitis PigmentosaUnited States