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Clinical Trials on Hereditary Complement Deficiency Diseases
Total 11115 results
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Hoffmann-La RocheCompletedHaemophilia A | Moderate Hereditary Factor VIII Deficiency Disease Without Inhibitor | Severe Hereditary Factor VIII Deficiency Disease Without InhibitorItaly
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Scripps HealthJ. Craig Venter InstituteCompletedLi-Fraumeni Syndrome | Hereditary Cancer Syndromes | TP53 Gene Germline Mutation CarrierUnited States
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National Cancer Institute (NCI)CompletedColorectal Neoplasm | Hereditary NonpolyposisUnited States
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Apellis Pharmaceuticals, Inc.AvailableC3G | IC-MPGN | C3 Glomerulopathy | C3 Glomerulonephritis | Complement 3 Glomerulopathy | Complement 3 Glomerulopathy (C3G) | Complement 3 Glomerulonephritis | Dense Deposit Disease | DDD | Membranoproliferative Glomerulonephritis | Membranoproliferative Glomerulonephritis (MPGN) | Immune Complex Membranoproliferative...United States
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Apellis Pharmaceuticals, Inc.Active, not recruitingC3G | IC-MPGN | C3 Glomerulopathy | C3 Glomerulonephritis | Complement 3 Glomerulopathy | Complement 3 Glomerulopathy (C3G) | Complement 3 Glomerulonephritis | Dense Deposit Disease | DDD | Membranoproliferative Glomerulonephritis | Membranoproliferative Glomerulonephritis (MPGN) | Immune Complex Membranoproliferative...United States, Spain, France, Germany, United Kingdom, Netherlands, Brazil, Israel, Japan, Australia, Austria, Italy, Switzerland, Korea, Republic of, Czechia, Belgium, Argentina, Canada, Poland
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Apellis Pharmaceuticals, Inc.Active, not recruitingC3G | IC-MPGN | C3 Glomerulopathy | C3 Glomerulonephritis | Complement 3 Glomerulopathy | Complement 3 Glomerulopathy (C3G) | Complement 3 Glomerulonephritis | Dense Deposit Disease | DDD | Membranoproliferative Glomerulonephritis | Membranoproliferative Glomerulonephritis (MPGN) | Immune Complex Membranoproliferative...United States, Australia, Brazil, Czechia, France, Italy, Korea, Republic of, Netherlands, Spain, Switzerland, United Kingdom
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London North West Healthcare NHS TrustNot yet recruitingLynch Syndrome | Polyposis Syndrome, Hereditary Mixed, 1 | Polyposis Syndrome, Hereditary Mixed, 2United Kingdom
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University of MinnesotaRecruiting
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National Health Research Institutes, TaiwanChang Gung Memorial HospitalUnknownHereditary Nonpolyposis Colorectal CancerTaiwan
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Universitaire Ziekenhuizen KU LeuvenCompletedLynch Syndrome | Hereditary Non-polyposis Colon Carcinoma | HNPCCBelgium
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Dana-Farber Cancer InstituteNational Cancer Institute (NCI); Baylor College of Medicine; City of Hope Medical...RecruitingTP53 Gene Mutation | Li-Fraumeni Syndrome | Hereditary Cancer Syndrome | Mosaicism | Clonal HematopoiesisUnited States
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Radboud University Medical CenterZonMw: The Netherlands Organisation for Health Research and DevelopmentUnknownColorectal Neoplasms | Hereditary Nonpolyposis Colorectal CancerNetherlands
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Wageningen UniversityDutch Cancer Society; Wereld Kanker Onderzoek Fonds; Funding: Biobanking and...RecruitingNeoplasms | Colorectal Neoplasms | Lynch Syndrome | Hereditary Nonpolyposis Colorectal CancerNetherlands
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Apellis Pharmaceuticals, Inc.Active, not recruitingRenal Transplant | C3G | IC-MPGN | C3 Glomerulopathy | C3 Glomerulonephritis | Complement 3 Glomerulopathy | Complement 3 Glomerulopathy (C3G) | Complement 3 Glomerulonephritis | Membranoproliferative Glomerulonephritis | Membranoproliferative Glomerulonephritis (MPGN) | Immune Complex Membranoproliferative... and other conditionsUnited States, Australia, Austria, United Kingdom, Brazil, Argentina, France, Italy, Netherlands, Spain, Switzerland
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London North West Healthcare NHS TrustCompletedColorectal Neoplasms, Hereditary NonpolyposisUnited Kingdom
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University of OxfordWellcome TrustCompletedComplement Mediated Bacterial Killing in Healthy AdultsUnited Kingdom
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State Scientific Centre of Coloproctology, Russian...The Loginov MCSC MHD; Pirogov National Medical and Surgical Center; Moscow City... and other collaboratorsRecruitingColorectal Cancer | Lynch Syndrome | Hereditary Colorectal Cancer | MSIRussian Federation
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National Human Genome Research Institute (NHGRI)CompletedHNPCC | Hereditary Nonpolyposis Colon CancerUnited States
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Marmara UniversityNational Institute of Allergy and Infectious Diseases (NIAID)UnknownProtein-Losing Enteropathies | CD55 - Cluster of Differentiation Antigen 55 Deficiency | Primary Intestinal Lymphangiectasis | Complement Regulatory Factor DefectTurkey
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Heidelberg UniversityTerminatedHereditary Emphysema (Alpha 1-antitrypsin Deficiency)Germany
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Fox Chase Cancer CenterNational Cancer Institute (NCI)CompletedColorectal Cancer | Hereditary Non-polyposis Colon CancerUnited States
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National Eye Institute (NEI)CompletedHereditary Eye DiseaseUnited States
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National Eye Institute (NEI)Completed
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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Amyndas Pharmaceuticals S.A.CompletedComplement Mediated DiseasesUnited States
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Vanderbilt University Medical CenterNational Cancer Institute (NCI)CompletedColorectal Cancer | Precancerous Condition | Hereditary Non-polyposis Colon CancerUnited States
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St George's, University of LondonTerminatedEndometrial Cancer | Hereditary Non-polyposis Colon Cancer (hmsh2, hmlh1, hpms1, hpms2)United Kingdom
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Imperial College LondonTerminatedHereditary Haemorrhagic TelangiectasiaUnited Kingdom
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National Human Genome Research Institute (NHGRI)Completed
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Sheba Medical CenterUnknownInfantile Canavan Disease | Deficiency Disease, AspartoacylaseIsrael
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Johns Hopkins UniversityNational Human Genome Research Institute (NHGRI)CompletedHuntington Disease | Hereditary Cancer | Hereditary Breast and Ovarian Cancer | Hereditary Non-polyposis Colon Cancer | Hereditary Non-Polyposis Colorectal Cancer SyndromeUnited States
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Assistance Publique - Hôpitaux de ParisCompletedColorectal Neoplasms, Hereditary NonpolyposisFrance
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University of UtahUniversity of Witwatersrand, South AfricaCompletedHereditary Elliptocytosis (HE) | Hereditary Pyropoikilocytosis (HPP)United States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingLi-Fraumeni SyndromeUnited States
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Geisinger ClinicNational Cancer Institute (NCI)CompletedLynch SyndromeUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Hereditary Breast Carcinoma | Hereditary Ovarian CarcinomaUnited States
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PERROD GuillaumeNot yet recruiting
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UNC Lineberger Comprehensive Cancer CenterUniversity of North Carolina, Chapel Hill; National Center for Advancing Translational... and other collaboratorsRecruitingLynch SyndromeUnited States
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Fox Chase Cancer CenterRecruiting
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Albert Einstein College of MedicineRecruiting
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Second Affiliated Hospital, School of Medicine,...Guangzhou Burning Rock Medical Examination Institute Co., Ltd.CompletedLynch SyndromeChina
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University Medical Center GroningenAcademisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA); The Netherlands... and other collaboratorsCompletedLynch SyndromeNetherlands
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National Cancer Institute (NCI)RecruitingLynch SyndromeUnited States, Puerto Rico
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National Cancer Institute (NCI)CompletedLynch SyndromeUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...FUJIFILM Europe GmbHCompletedLynch Syndrome | ColonoscopyNetherlands
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Assistance Publique - Hôpitaux de ParisARC Foundation for Cancer ResearchCompleted
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University of North Carolina, Chapel HillNorth Carolina Translational and Clinical Sciences InstituteNot yet recruitingColorectal Cancer | Rectal Cancer | Rectal Neoplasms | Colon Cancer | Colon Adenocarcinoma | Colon Rectal Cancer | Hereditary Nonpolyposis Colon CancerUnited States
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Piazza della Vittoria 14 Studio Medico - Ginecologia...Not yet recruitingLynch Syndrome | ContraceptionItaly
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National Cancer Institute (NCI)RecruitingLynch SyndromeUnited States, Puerto Rico
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Assistance Publique - Hôpitaux de ParisRecruiting