- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Hereditary Diseases
Total 380298 results
-
National Health Research Institutes, TaiwanChang Gung Memorial HospitalUnknownHereditary Nonpolyposis Colorectal CancerTaiwan
-
National Eye Institute (NEI)Bausch & Lomb Incorporated; Eye Bank Association of America; Midwest Eye Banks; Tissue Banks International and other collaboratorsCompletedCorneal Disease | Fuch's Dystrophy | Pseudophakic Corneal EdemaUnited States
-
Nanoscope Therapeutics Inc.CompletedEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
-
University of PennsylvaniaAstraZeneca; Ionis Pharmaceuticals, Inc.Active, not recruitingHereditary Amyloidosis, Transthyretin-RelatedUnited States
-
Cornea Associates of TexasActive, not recruitingKeratoconus | Corneal Ectasia | Pellucid Marginal Corneal Degeneration | Corneal DegenerationUnited States
-
Imperial College LondonCompletedHereditary Haemorrhagic Telangiectasia (HHT)United Kingdom
-
University Hospital TuebingenCompleted
-
Universitaire Ziekenhuizen KU LeuvenCompletedLynch Syndrome | Hereditary Non-polyposis Colon Carcinoma | HNPCCBelgium
-
Case Western Reserve UniversityNational Eye Institute (NEI); Jaeb Center for Health ResearchRecruitingFuchs' Endothelial Dystrophy | Corneal Endothelial DecompensationUnited States
-
Wageningen UniversityDutch Cancer Society; Wereld Kanker Onderzoek Fonds; Funding: Biobanking and...RecruitingNeoplasms | Colorectal Neoplasms | Lynch Syndrome | Hereditary Nonpolyposis Colorectal CancerNetherlands
-
Alcon ResearchEnrolling by invitationCorneal Edema | Bullous Keratopathy | Corneal Dystrophy | Entropion | Corneal ErosionUnited States
-
Cornea Associates of TexasCompletedKeratoconus | Corneal Ectasia | Pellucid Marginal Corneal Degeneration | Corneal DegenerationUnited States
-
Michigan State UniversityRecruitingHereditary DiseasesUnited States
-
Randy KardonRecruitingLeber Hereditary Optic Neuropathy | Ischemic Optic Neuropathy | Hemianopia | Branch Retinal Artery Occlusion | Acute Zonal Occult Outer RetinopathyUnited States
-
National Human Genome Research Institute (NHGRI)CompletedHereditary Oral CleftsSyrian Arab Republic
-
Adam Fedyk, MD, FACSAlcon ResearchRecruitingCataract | Fuchs DystrophyUnited States
-
Aerie PharmaceuticalsCompleted
-
Centre Hospitalier Universitaire de Saint EtienneKyoto University, Graduate School of MedicineCompletedFuchs Endothelial Corneal DystrophyFrance
-
University Hospital, Strasbourg, FranceTerminated
-
Astria Therapeutics, Inc.RecruitingHereditary AngioedemaUnited States, United Kingdom, Canada, Germany, Bulgaria, Czechia
-
ADARx Pharmaceuticals, Inc.RecruitingHereditary AngioedemaAustralia
-
Pharming Technologies B.V.RecruitingHereditary AngioedemaGermany, Bulgaria, Croatia, Czechia, France, Hungary, Italy, North Macedonia, Poland, Slovakia, Norway, Slovenia, Sweden
-
Ionis Pharmaceuticals, Inc.AvailableHereditary Angioedema
-
Istituti Clinici Scientifici Maugeri SpACompleted
-
CSL BehringActive, not recruitingHereditary AngioedemaAustralia, Canada, United States, New Zealand, Germany, Hong Kong, Netherlands, Taiwan, Czechia, Israel, Hungary, Japan, Russian Federation, Spain
-
Astria Therapeutics, Inc.Enrolling by invitationHereditary AngioedemaUnited States, Canada
-
Intellia TherapeuticsActive, not recruitingHereditary AngioedemaFrance, New Zealand, Germany, United Kingdom, Netherlands, Australia
-
BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | HAEFrance, North Macedonia, Poland, Korea, Republic of, Slovakia, South Africa, Czechia
-
Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, Netherlands
-
KalVista Pharmaceuticals, Ltd.Completed
-
ShireHalozyme TherapeuticsCompletedHereditary AngioedemaUnited States
-
ShireCompletedHereditary AngioedemaUnited States
-
ShireCompletedAngioedemaUnited States
-
ShireCompletedHereditary AngioedemaUnited States
-
ShireCompletedHereditary AngioedemaUnited States
-
KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited Kingdom
-
BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
-
Pharming Technologies B.V.CompletedHereditary AngioedemaUnited States, Canada, Czechia, Italy, Macedonia, The Former Yugoslav Republic of, Romania, Serbia
-
BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
-
Massachusetts General HospitalShire Human Genetic Therapies, Inc.CompletedHereditary AngioedemaUnited States
-
BioCryst PharmaceuticalsCompleted
-
Pharming Technologies B.V.CompletedHereditary AngioedemaUnited States, Bulgaria, Canada, Hungary, Israel, Italy, Macedonia, The Former Yugoslav Republic of, Poland, Romania, Serbia, South Africa
-
CSL BehringCompletedHereditary AngioedemaUnited States, Canada
-
CSL BehringCompletedHereditary AngioedemaBulgaria, United States, Poland, Spain, Hungary, United Kingdom, Russian Federation, Macedonia, The Former Yugoslav Republic of, Argentina, Australia, Canada, Czech Republic, Israel, Romania, Sweden
-
BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
-
Nanoscope Therapeutics Inc.Enrolling by invitationEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
-
Radboud University Medical CenterZonMw: The Netherlands Organisation for Health Research and DevelopmentUnknownColorectal Neoplasms | Hereditary Nonpolyposis Colorectal CancerNetherlands
-
Radboud University Medical CenterJacques and Gloria Gossweiler FoundationCompletedHereditary Spastic Paraplegia | Strumpell DiseaseNetherlands
-
University of Texas Southwestern Medical CenterTerminatedHereditary Spherocytosis
-
Oslo University HospitalUnknownCorneal Dystrophies, Hereditary | Fuchs' Endothelial Dystrophy | Corneal Transplantation | Descemet Stripping Automated Endothelial KeratoplastyNorway