- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Hereditary Fructose Intolerance
Total 4097 results
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M.D. Anderson Cancer CenterRecruitingMultiple Endocrine NeoplasiaUnited States
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Jazz PharmaceuticalsActive, not recruitingTuberous Sclerosis Complex | Dravet Syndrome | Lennox Gastaut SyndromeUnited States
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University of CoimbraCompletedAutism Spectrum Disorder | Neurofibromatosis 1Portugal
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ShireTerminatedMetabolic Diseases | Brain Diseases | Central Nervous System Diseases | Nervous System Diseases | Demyelinating Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Lysosomal Storage Diseases | Lipid Metabolism Disorders | Sphingolipidoses | Hereditary Central Nervous System Demyelinating Diseases and other conditionsUnited States, Denmark, France, Argentina, Belgium, Brazil, Canada, Germany, Japan, Turkey
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Charite University, Berlin, GermanyUnknownColorectal Cancer | Crohn Disease | Ulcerative Colitis | Familial Adenomatous Polyposis | Crohn Colitis | Ileal PouchGermany
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Federal University of São PauloCompletedCarpal Tunnel Syndrome | Compression Neuropathy, Carpal Tunnel | Median Neuropathy, Carpal TunnelBrazil
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NovartisCompletedFamilial Cold Autoinflammatory Syndrome | Cryopyrin-Associated Periodic Syndromes | Neonatal Onset Multisystem Inflammatory Disease | Muckle Wells SyndromeUnited States, Germany, Italy, Spain, United Kingdom, Turkey, France, Belgium, India
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Therapeutic Advances in Childhood Leukemia ConsortiumRecruitingNeurofibromatosis 1 | JMML | Leukemia, Juvenile Myelomonocytic | JCML | CBL SyndromeUnited States
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Centre Hospitalier National d'Ophtalmologie des...RecruitingHypertension | Retinal Degeneration | Diabetic Retinopathy | Macular Edema | Retinitis Pigmentosa | Macular Dystrophy | Maculopathy, Age Related | Occlusion Retinal VeinFrance
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Newcastle UniversityLudwig-Maximilians - University of Munich; LGMD2i Research Fund; CureLGMD2iRecruitingLimb Girdle Muscular Dystrophy | Congenital Muscular Dystrophy | LGMDR9 | LGMD2I | Walker-Warburg Syndrome | Muscle-Eye-Brain Disease | FKRP Gene MutationUnited Kingdom
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingNeuroendocrine Neoplasm | Multiple Endocrine Neoplasia Type 1 | Advanced Carcinoid Tumor | Digestive System Neuroendocrine Neoplasm | Unresectable Carcinoid TumorUnited States
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University Hospital, Clermont-FerrandActive, not recruitingCharcot-Marie-Tooth Type 1A NeuropathyFrance
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Istanbul UniversityUnknownFMF | Behcet DiseaseTurkey
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Antalya Training and Research HospitalCompletedBehcet Syndrome | Erectile Dysfunction | Behçet DiseaseTurkey
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Novartis PharmaceuticalsCompletedNevoid Basal Cell Carcinoma Syndrome | Basal Cell Carcinoma | Gorlin SyndromeBelgium, Austria, Germany, Canada
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Children's Hospital Los AngelesGenentech, Inc.CompletedGrowth Hormone Deficiency | Hypopituitarism | Septo-Optic DysplasiaUnited States
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Roger PackerChildren's National Research InstituteCompletedTarceva/Rapamycin for Children With Low-grade Gliomas With or Without Neurofibromatosis Type 1 (NF1)Low-grade GliomasUnited States
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University of CalgaryNot yet recruitingPostural Orthostatic Tachycardia Syndrome | Post Acute Sequelae of SARS CoV 2 Infection
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Medical College of WisconsinUniversity College, London; Indiana UniversityRecruitingFunctional Gastrointestinal Disorders | Postural Orthostatic Tachycardia Syndrome | Hypermobile Ehlers-Danlos Syndrome | Autonomic Nervous System Disease | Autonomic Nervous System ImbalanceUnited States
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RWTH Aachen UniversityDLR German Aerospace CenterRecruitingPostural Tachycardia Syndrome | Autonomic Neuropathy | Small Fiber Neuropathy | Ehlers-Danlos Syndrome Hypermobility TypeGermany
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Children's Oncology GroupNot yet recruitingStage I Kidney Wilms Tumor | Stage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor
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Novartis PharmaceuticalsRecruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Russian Academy of Medical SciencesBlokhin's Russian Cancer Research CenterRecruitingMelanoma | Nevus | Nevus, Pigmented | Melanoma (Skin) | Mucosal Melanoma | Moles | Dysplastic Nevus Syndrome | Nevus, Blue | Nevus, Spitz | Nevi, Spindle Cell | Nevi, Dysplastic | Mucosal MelanosisRussian Federation
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M.D. Anderson Cancer CenterRecruitingHyperparathyroidism | Multiple Endocrine Neoplasia | Pancreatic Neuroendocrine TumorsUnited States
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National Cancer Institute (NCI)Enrolling by invitationHIV | Neurofibromatosis Type 1 | Brain TumorsUnited States
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Assistance Publique - Hôpitaux de ParisCompletedNephroblastoma With Vena Cava ThrombosisFrance
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HedgePath Pharmaceuticals, Inc.CompletedBasal Cell Carcinoma in Basal Cell Nevus SyndromeUnited States
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University Hospital, Clermont-FerrandCompletedCharcot-Marie-Tooth Type 1A NeuropathyFrance
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Bursa Yüksek İhtisas Education and Research HospitalCompletedCentral Sensitisation | Behcet's DiseaseTurkey
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M.D. Anderson Cancer CenterActive, not recruitingGenetic Mutation | MEN1United States
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National Cancer Institute (NCI)WithdrawnNeoplasms, Nerve Tissue | Peripheral Nervous System Diseases | Heredodegenerative Disorders, Nervous System | Neurofibromatosis 1
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University of California, DavisCompletedPsoriasis | Eczema | Rosacea | Actinic Keratosis | Skin Cancer | Atopic Dermatitis | Acne | Leg Ulcers | Foot Ulcers | Dysplastic NeviUnited States
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AstraZenecaCompletedHealthy Participants | Neurofibromatosis Type 1 (NF1)-Related Plexiform Neurofibromas (PNs)United States
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M.D. Anderson Cancer CenterInex PharmaceuticalsCompletedSoft Tissue Sarcoma | Lymphoma | Leukemia | Osteosarcoma | Wilms' TumorUnited States
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Connecticut Children's Medical CenterDuPont Nutrition and HealthWithdrawnPharyngitis | Aphthous Stomatitis | Periodic Fever | Cervical Adenitis
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Novartis PharmaceuticalsWithdrawnBasal Cell CarcinomaGreece, Switzerland, Germany, United Kingdom, Belgium, Canada, Czechia, Finland, Italy, Spain
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Pamela L. KunzGenentech, Inc.TerminatedNeuroendocrine Tumors | Neuroblastoma | Multiple Endocrine Neoplasia | Pancreatic Neuroendocrine Tumors | Carcinoid Tumors | Adrenal Gland TumorsUnited States
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Istituto Ortopedico RizzoliCompletedEntrapment Neuropathy, Carpal Tunnel | Compression Neuropathy, Carpal Tunnel | Median Neuropathy, Carpal TunnelItaly
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Universitaire Ziekenhuizen KU LeuvenUnknownNeurofibromatosis Type 1Belgium
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QLT Inc.NovartisTerminatedNevoid Basal Cell Carcinoma Syndrome | Basal Cell Carcinoma | Gorlin Syndrome
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Boston Children's HospitalNational Eye Institute (NEI); Howard Hughes Medical InstituteRecruitingOcular Motility Disorders | Facial Palsy | Synkinesis | Sixth Nerve Palsy | Mobius Syndrome | Congenital Fibrosis of Extraocular Muscles | Duane Retraction Syndrome | Duane Radial Ray Syndrome | Brown Syndrome | Marcus Gunn Syndrome | Strabismus Congenital | Horizontal Gaze Palsy | Horizontal Gaze Palsy With Progressive... and other conditionsUnited States
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Seattle Children's HospitalRecruitingSoft Tissue Sarcoma | Carcinoma | Osteosarcoma | Ewing Sarcoma | Rhabdoid Tumor | Neuroblastoma | Retinoblastoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Synovial Sarcoma | Desmoplastic Small Round Cell Tumor | Germ Cell Tumor | Pediatric Solid Tumor | Clear Cell Sarcoma | Malignant Peripheral Nerve Sheath TumorsUnited States
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National Cancer Institute (NCI)WithdrawnHematopoietic and Lymphoid Cell Neoplasm | Lynch Syndrome | Refractory Lymphoma | Refractory Malignant Solid Neoplasm | Recurrent Lymphoma | Recurrent Malignant Solid Neoplasm | Recurrent Neuroblastoma | Refractory Neuroblastoma | Recurrent Primary Central Nervous System Neoplasm | Refractory Primary Central... and other conditionsUnited States, Canada
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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University Hospital, AntwerpKom Op Tegen Kanker; Stichting tegen KankerRecruitingEsophageal Cancer | Ovarian Cancer | Pancreas Cancer | Liver CancerBelgium
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National Tuberous Sclerosis AssociationRecruitingTuberous Sclerosis | LymphangioleiomyomatosisUnited States, Canada
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Brigham and Women's HospitalMassachusetts General HospitalRecruitingTuberous Sclerosis Complex | LymphangioleiomyomatosisUnited States
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Medical University of BialystokUniversity of BialystokRecruitingOptic Neuritis | Ischemic Optic Neuropathy | Traumatic Optic Neuropathy | Toxic Optic Neuropathy | Compressive Optic Neuropathy | Hereditary Optic NeuropathiesPoland