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Clinical Trials on Hereditary Sensory and Autonomic Neuropathies
Total 6373 results
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Xinhua Hospital, Shanghai Jiao Tong University...UnknownLymphoma | Acute Myeloid Leukemia | Neuroblastoma | Retinoblastoma | Hepatoblastoma | Acute Lymphoid LeukemiaChina
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National Cancer Institute (NCI)CompletedFamilial Adenomatous PolyposisUnited States, Puerto Rico
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The Cleveland ClinicOhio State University Comprehensive Cancer CenterCompletedFamilial Adenomatous PolyposisUnited States
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Roswell Park Cancer InstituteCompletedLymphoma | Brain and Central Nervous System Tumors | Neuroblastoma | RetinoblastomaUnited States
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National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous Disease | Leukocyte Disorder | Job's Syndrome | Chediak Higashi SyndromeUnited States
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Radboud University Medical CenterDutch Cancer SocietyUnknownAdenomatous Polyposis ColiNetherlands
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University of RochesterUniversity of Colorado, Denver; Massachusetts General Hospital; Stanford UniversityRecruitingParkinson Disease | Multiple System Atrophy | Corticobasal Degeneration | Progressive Supranuclear Palsy | Parkinson's Disease and Parkinsonism | Dementia With Lewy Bodies | Vascular Parkinsonism | Parkinson Disease Dementia | Lewy Body ParkinsonismUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...CompletedTuberous Sclerosis Complex | Autism | Self-injuryUnited States
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Sarcoma Alliance for Research through CollaborationNational Cancer Institute (NCI)CompletedSarcoma | Neurofibromatosis Type 1United States
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Seattle Children's HospitalActive, not recruitingMelanoma | Soft Tissue Sarcoma | Carcinoma | Osteosarcoma | Ewing Sarcoma | Rhabdoid Tumor | Neuroblastoma | Retinoblastoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Synovial Sarcoma | Desmoplastic Small Round Cell Tumor | Germ Cell Tumor | Pediatric Solid Tumor | Clear Cell Sarcoma | Malignant Peripheral Nerve Sheath...United States
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SpringWorks Therapeutics, Inc.AvailableNeurofibromatosis Type 1-Associated Plexiform Neurofibromas | Histiocytic Neoplasm | Other MAP-K Pathway Driven Diseases
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CENTOGENE GmbH RostockWithdrawnMuscle Weakness | Peripheral NeuropathyEgypt, Germany, India, Sri Lanka
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Charite University, Berlin, GermanyUnknownColorectal Cancer | Crohn Disease | Ulcerative Colitis | Familial Adenomatous Polyposis | Crohn Colitis | Ulcerative Colitis Chronic | Ulcerative Colitis in Remission | Ileal PouchGermany
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Scripps Translational Science InstituteRecruitingChronic Fatigue Syndrome | Postural Orthostatic Tachycardia Syndrome | Dysautonomia | Long COVID | Long Covid19 | Myalgic EncephalomyelitisUnited States
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U.S. Wound RegistryRecruitingWounds and Injuries | Diabetic Foot | Leg Ulcer | Skin Ulcer | Diabetes Complications | Diabetic Neuropathies | Lymphedema | Peripheral Arterial Disease | Vasculitis | Venous Insufficiency | Varicose Ulcer | Pressure Ulcer | Pyoderma | Surgical Wound Dehiscence | Amputation StumpUnited States
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsActive, not recruitingDiabetes Mellitus, Type 1 | Diabetic Kidney Disease | Diabetic Nephropathies | Diabetes Mellitus Complication | Metabolic Disease | Type1 Diabetes Mellitus | Autoimmune Diabetes | Juvenile DiabetesUnited States
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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Masonic Cancer Center, University of MinnesotaRecruiting
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Assistance Publique - Hôpitaux de ParisBraintaleNot yet recruitingX-linked Adrenoleukodystrophy
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Minoryx Therapeutics, S.L.RecruitingCerebral Adrenoleukodystrophy (cALD)United States, Brazil, Argentina
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingStage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor | Recurrent Kidney Wilms Tumor | Anaplastic Kidney Wilms TumorUnited States, Canada, Puerto Rico, Australia, New Zealand, Saudi Arabia
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National Cancer Institute (NCI)RecruitingNeurofibromatosis Type 1 | Low Grade Glioma | Visual Pathway GliomaUnited States, Canada, Puerto Rico
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom
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University Hospital, ToursCompletedTuberous Sclerosis Complex | LymphangioleiomyomatosisFrance
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser... and other collaboratorsCompletedX-linked AdrenoleukodystrophyUnited States
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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Shenzhen Geno-Immune Medical InstituteUnknown
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NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
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Masonic Cancer Center, University of MinnesotaWithdrawnCerebral Adrenoleukodystrophy
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FDA Office of Orphan Products DevelopmentHugo W. Moser Research Institute at Kennedy Krieger, Inc.Completed
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Far Eastern Memorial HospitalNational Taiwan University Hospital; Fu Jen Catholic UniversityUnknownAdrenoleukodystrophyTaiwan
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Fairview University Medical CenterUnknownHemophagocytic Lymphohistiocytosis | Graft Versus Host Disease | Chediak-Higashi Syndrome | Virus-Associated Hemophagocytic Syndrome | X-Linked Lymphoproliferative Syndrome | Familial Erythrophagocytic LymphohistiocytosisUnited States
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University Hospital, Strasbourg, FranceRecruitingAlzheimer Disease | Multiple System Atrophy | Frontotemporal Dementia | Dementia With Lewy Bodies | Parkinson's Disease DementiaFrance
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Sheba Medical CenterEnrolling by invitationParkinson Disease | Cerebellar Ataxia | Dystonia | Multiple System Atrophy | Corticobasal Degeneration | Progressive Supranuclear Palsy | Essential Tremor | Dementia With Lewy Bodies | Normal Pressure HydrocephalusIsrael
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University of PennsylvaniaCompletedFrontotemporal Degeneration | Multiple System Atrophy | Progressive Supranuclear PalsyUnited States
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Medical College of WisconsinNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingDiabetes Mellitus, Type 2 | Chronic Kidney Diseases | Diabetic Nephropathies | Healthy LifestyleUnited States
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Vanderbilt UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingNeurofibromatosis Type 1 | Reading Disability | NF1 | Learning DisabilityUnited States
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingIntellectual Disability | Tuberous Sclerosis | Autism DisorderUnited States
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Vanderbilt UniversityNational Institute of Neurological Disorders and Stroke (NINDS)CompletedNeurofibromatosis Type 1 | Reading DisabilitiesUnited States
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University Hospital, ToulouseCompleted
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Karolinska InstitutetKarolinska University Hospital; PfizerRecruitingCOVID-19 | Post-COVID-19 Syndrome | Long COVID | Long Covid19 | Post COVID-19 Condition | Post-COVID Syndrome | Post COVID-19 Condition, Unspecified | POTS - Postural Orthostatic Tachycardia Syndrome | Postinfectious Inflammation | Postinfectious DisorderSweden
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Hospital Universitario La PazCompletedCPAP Effect on Albuminuria in Patients With Diabetic Nephropathy and Obstructive Sleep Apnea (DIANA)Diabetic Nephropathy | Sleep ApneaSpain
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George ZogopoulosRecruitingPancreatic Cancer | Bile Duct Cancer | Pancreas Cancer | Gallbladder Cancer | Pancreas Neoplasm | Familial Pancreatic Cancer | Duodenal Cancer | Hereditary Cancer | Pancreas Cyst | Ampullary Cancer | Pancreatic Precancerous ConditionCanada
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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Boston Children's HospitalNational Eye Institute (NEI); Howard Hughes Medical InstituteRecruitingOcular Motility Disorders | Facial Palsy | Synkinesis | Sixth Nerve Palsy | Mobius Syndrome | Congenital Fibrosis of Extraocular Muscles | Duane Retraction Syndrome | Duane Radial Ray Syndrome | Brown Syndrome | Marcus Gunn Syndrome | Strabismus Congenital | Horizontal Gaze Palsy | Horizontal Gaze Palsy With Progressive... and other conditionsUnited States
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Talaris Therapeutics Inc.Duke UniversityNo longer availableMetachromatic LeukodystrophyUnited States
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NYU Langone HealthWithdrawnEpilepsy | Tuberous Sclerosis | Dravet Syndrome | Focal Seizures | Lennox-Gastaut SyndromeUnited States
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Washington University School of MedicineCompletedNeurofibromatosis Type 1 | Pediatric Brain TumorUnited States
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The University of Texas Health Science Center,...Society for Pediatric DermatologyCompletedTuberous Sclerosis | Neurofibromatoses | Neurofibroma | AngiofibromaUnited States
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National Institute of Neurological Disorders and...CompletedMuscle Rigidity | Spasm | Stiff Man SyndromeUnited States