- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Hunter Syndrome (MPS II)
Total 534 results
-
National Institute of Mental Health (NIMH)TerminatedDepression | Premenstrual Dysphoric Disorder | Premenstrual Syndrome | PMS | PMDDUnited States
-
medac GmbHSynteract, Inc.RecruitingMyelodysplastic Syndrome (MDS) | Acute Myeloid Leukaemia (AML) | Allogeneic Hematopoietic Stem Cell Transplantation (HSCT)United States
-
NexImmune Inc.Active, not recruitingAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)United States
-
University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedHurler Syndrome | Sanfilippo Syndrome Type A | Sanfilippo Syndrome Type BUnited States
-
Children's National Research InstituteNational Institute of Allergy and Infectious Diseases (NIAID)Active, not recruitingCovid19 | SARS-CoV2 Infection | MIS-C Associated With COVID-19 | MIS-C Multisystem Inflammatory Syndrome in ChildrenUnited States
-
Northwestern UniversitySeagen Inc.TerminatedExtranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent Adult Diffuse Small Cleaved Cell Lymphoma | Recurrent Adult Immunoblastic Large Cell... and other conditionsUnited States
-
Case Comprehensive Cancer CenterNational Cancer Institute (NCI)CompletedExtranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent Adult Diffuse Small Cleaved Cell Lymphoma and other conditionsUnited States
-
Oregon Health and Science UniversityUniversity of Utah; BioMarin PharmaceuticalCompleted
-
Wake Forest University Health SciencesNational Cancer Institute (NCI)CompletedPrimary Myelofibrosis | Stage I Multiple Myeloma | Stage II Multiple Myeloma | Stage III Multiple Myeloma | Recurrent Adult Acute Myeloid Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma and other conditionsUnited States
-
National Cancer Institute (NCI)RecruitingMDS | Immunodeficiency | GATA2United States
-
National Cancer Institute (NCI)CompletedMDS | Immunodeficiency | GATA2United States
-
Sunnybrook Health Sciences CentreQueen's University; Ontario Molecular Pathology Research NetworkUnknownCardiovascular Diseases | Inflammation | MDSCanada
-
BioMarin PharmaceuticalApproved for marketingMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, Puerto Rico
-
National Heart, Lung, and Blood Institute (NHLBI)Children's National Research InstituteCompletedLymphoma, Non-Hodgkin | MDS (Myelodysplastic Syndrome) | Myeloproliferative Disorder | ALL (Acute B-Lymphoblastic Leukemia) | AML (Acute Myelogenous LeukemiaUnited States
-
National Cancer Institute (NCI)Active, not recruitingMycosis Fungoides | Sezary Syndrome | Stage IB Mycosis Fungoides and Sezary Syndrome AJCC v8 | Stage II Mycosis Fungoides and Sezary Syndrome AJCC v8 | Stage III Mycosis Fungoides and Sezary Syndrome AJCC v8 | Stage IV Mycosis Fungoides and Sezary Syndrome AJCC v8 | Recurrent Mycosis Fungoides... and other conditionsUnited States
-
Jazz PharmaceuticalsCompletedAcute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS)United States
-
Jazz PharmaceuticalsWithdrawnAcute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS)United States
-
University of Kansas Medical CenterCompletedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Non-Hodgkins Lymphoma | Myelodysplastic Syndrome (MDS) | Hodgkins LymphomaUnited States
-
University Hospital, Strasbourg, FranceRecruitingCockayne Syndrome, Type I and IIFrance
-
University of TorontoAgriculture and Agri-Food CanadaCompletedObesity | Metabolic Syndrome | Type II Diabetes MellitusCanada
-
University of TorontoAgriculture and Agri-Food Canada; Pulse CanadaCompletedObesity | Metabolic Syndrome | Type II Diabetes MellitusCanada
-
SanofiCompletedPompe Disease | Mucopolysaccharidosis Type I (MPS I)Italy
-
Fundación Pública Andaluza para la gestión de la...Andaluz Health ServiceCompletedVERifynow in DIabetes Non-responsiveness: a Study on Switching From Clopidogrel to Prasugrel (VERDI)Acute Coronary Syndrome | Diabetes Mellitus Type IISpain
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedPrimary Myelofibrosis | Polycythemia Vera | Essential Thrombocythemia | Stage I Multiple Myeloma | Stage II Multiple Myeloma | Stage III Multiple Myeloma | Recurrent Adult Acute Myeloid Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell... and other conditionsUnited States, Italy
-
Children's Hospital Medical Center, CincinnatiRecruitingLow Back Pain | Chronic Widespread Pain | Fibromyalgia | Complex Regional Pain Syndrome (CRPS) | Ehlers-Danlos Syndrome (EDS) | Amplified Musculoskeletal Pain Syndrome (AMPS)United States
-
Institute for Clinical and Experimental MedicineSahlgrenska University Hospital, Sweden; University Hospital, MotolRecruitingInfertility, Female | Mayer Rokitansky Kuster Hauser Syndrome | Absolute Uterine Factor Infertility | Mullerian Aplasia | Uterus; Absence, Congenital | Uterus Absence, AcquiredCzechia
-
Memorial Sloan Kettering Cancer CenterPediatric Brain Tumor ConsortiumTerminatedFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML)United States
-
Emory UniversityBioMarin PharmaceuticalCompletedMPS - Mucopolysaccharidosis | Morquio DiseaseUnited States
-
Hopital FochRecruitingMayer Rokitansky Kuster Hauser SyndromeFrance
-
Alexion PharmaceuticalsTerminatedMPS IIIB (Sanfilippo B Syndrome)Spain, United States, Brazil, United Kingdom, Portugal, Italy
-
Fred Hutchinson Cancer CenterCompletedMyelodysplastic Syndrome (MDS) | Chronic Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive | Chronic Myelogenous Leukemia, BCR-ABL1 Positive | Acute Biphenotypic Leukemia | Acute Myeloid Leukemia in Remission | Acute Lymphoblastic Leukemia in Remission | Blasts Under 5 Percent of Bone Marrow...United States
-
University of California, San FranciscoNational Institute of Neurological Disorders and Stroke (NINDS)CompletedEpilepsy | Infantile Spasms | Lennox-Gastaut Syndrome | Polymicrogyria | Localization-related Epilepsy | Periventricular HeterotopiasUnited States, Argentina, Australia
-
City of Hope Medical CenterNational Cancer Institute (NCI)CompletedPrimary Myelofibrosis | Polycythemia Vera | Essential Thrombocythemia | Stage I Multiple Myeloma | Stage II Multiple Myeloma | Stage III Multiple Myeloma | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid... and other conditionsUnited States
-
National Institute of Allergy and Infectious Diseases...Autoimmunity Centers of Excellence; Clinical Trials in Organ Transplantation...CompletedSevere Acute Respiratory Syndrome Coronavirus 2 (SARS-CoV-2) | Coronavirus Disease 2019 (COVID-19) | Multisystem Inflammatory Syndrome in Children (MIS-C)United States
-
Radboud University Medical CenterCompletedAllogeneic Stem Cell Transplant | Acute Myeloid Leucaemia | Myelo Dysplastic Syndrome | Acute Graft Versus Host Disease Grade II-IVNetherlands, Belgium
-
Zachariah Michael DeFilippRegimmune CorporationActive, not recruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Hodgkin Lymphoma | Chronic Myelomonocytic Leukemia | Acute Lymphoblastic Leukemia | AML | Non Hodgkin Lymphoma | MDS | Myeloproliferative Disorder | GVHD | Graft Vs Host Disease | ALL | CMML | Blood Stem Cell Transplant Failure | MPN | Chemosensitive Hodgkin LymphomaUnited States
-
Imagine InstituteReference center for rare diseases (Rare Gynecologic Diseases)RecruitingMayer Rokitansky Kuster Hauser SyndromeFrance
-
Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis I | Hurler SyndromeUnited States
-
Masonic Cancer Center, University of MinnesotaCompleted
-
Medical College of WisconsinChildren's Hospital of PhiladelphiaCompletedMalignant Diseases (ie, Leukemia, MDS, Lymphoma) | Non-malignant Diseases (ie, Bone Marrow Failure Syndromes)United States
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedHIV Infection | Unspecified Childhood Solid Tumor, Protocol Specific | Primary Myelofibrosis | Polycythemia Vera | Essential Thrombocythemia | Stage I Multiple Myeloma | Stage II Multiple Myeloma | Stage III Multiple Myeloma | Chronic Myelomonocytic Leukemia | Juvenile Myelomonocytic Leukemia | Extranodal... and other conditionsUnited States
-
AmgenCompletedType II Refractory Celiac Disease (RCD-II) | In-situ Small Bowel T-cell LymphomaSpain, United States, Finland, France, Netherlands
-
City of Hope Medical CenterNational Cancer Institute (NCI)RecruitingSezary Syndrome | Stage IB Mycosis Fungoides and Sezary Syndrome AJCC v8 | Stage II Mycosis Fungoides and Sezary Syndrome AJCC v8 | Stage IIA Mycosis Fungoides and Sezary Syndrome AJCC v8 | Stage IIB Mycosis Fungoides and Sezary Syndrome AJCC v8 | Transformed Mycosis Fungoides | Folliculotropic... and other conditionsUnited States
-
Charite University, Berlin, GermanyUnknownMultiple Sclerosis, MS | Clinically Isolated SyndromeGermany
-
University of ArizonaAmgenCompletedSkin Cancer | Squamous Cell Carcinoma | Keratoacanthoma | Cutaneous Tumor | Skin Cancer, Squamous Cell | Lesion SkinUnited States
-
BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
-
University Hospital, Strasbourg, FranceUnknownAcute Respiratory Distress Syndrome After Cardiac Surgery Under Cardiopulmonary BypassFrance
-
Ginna LaportTerminatedAcute Myelogenous Leukemia (AML) - Relapsed, Primary Refractory Disease or Poor Risk Factors | Chronic Myelogenous Leukemia (CML) - Accelerated or Second Chronic Phase | Myelodysplastic Syndrome (MDS) - High and Intermediate Risk | Non-Hodgkin's Lymphoma (NHL) | Chronic Lymphocytic Leukemia...United States
-
Mesoblast International SàrlAvailableMultisystem Inflammatory Syndrome in Children (MIS-C) Associated With Coronavirus Disease (COVID-19)
-
University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States