- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Ichthyosis, X-Linked
Total 2418 results
-
JCR Pharmaceuticals Co., Ltd.Completed
-
JCR Pharmaceuticals Co., Ltd.Completed
-
Sangamo TherapeuticsTerminatedMucopolysaccharidosis II | MPS IIUnited States
-
REGENXBIO Inc.Withdrawn
-
Karen Brorup Heje PedersenCompletedHealthy Subjects | Spinal and Bulbar Muscular AtrophyDenmark
-
Green Cross CorporationCompletedMucopolysaccharidosis IIKorea, Republic of
-
Janssen-Ortho Inc., CanadaCompletedAutistic Disorder | Developmental Disabilities | Rett Syndrome | Asperger Syndrome | DCild Development Disorders, Pervasive
-
Eunice Kennedy Shriver National Institute of Child...University of MinnesotaCompleted
-
AO GENERIUMRecruitingMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
-
Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; Association...RecruitingAmyotrophic Lateral Sclerosis | Kennedy DiseaseFrance
-
JCR Pharmaceuticals Co., Ltd.RecruitingMucopolysaccharidosis IIUnited States, Germany, Spain, France, Brazil, Argentina, Turkey, United Kingdom, Poland, Italy
-
Denali Therapeutics Inc.Active, not recruitingMucopolysaccharidosis IIUnited States, Netherlands, Canada, United Kingdom
-
Denali Therapeutics Inc.Enrolling by invitationMucopolysaccharidosis IIUnited States, Canada, Belgium, Czechia, Netherlands
-
JCR Pharmaceuticals Co., Ltd.Enrolling by invitationMucopolysaccharidosis IIUnited States
-
Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
-
JCR Pharmaceuticals Co., Ltd.Completed
-
REGENXBIO Inc.CompletedMucopolysaccharidosis IIBrazil, United States, United Kingdom
-
REGENXBIO Inc.Enrolling by invitation
-
National Human Genome Research Institute (NHGRI)CompletedAutism | Asperger's Syndrome | Rett's DisorderUnited States
-
ArmaGen, IncCompletedMucopolysaccharidosis IIUnited States, Germany, Philippines
-
Soma JyonouchiBaylor College of MedicineCompletedX-linked Thrombocytopenia | Wiskott-Aldrich Syndrome (WAS)United States
-
Ramathibodi HospitalAstraZenecaCompletedSpinobulbar Muscular Atrophy | Kennedy's DiseaseThailand
-
National Institute of Neurological Disorders and...CompletedSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
-
University of Mississippi Medical CenterCompletedAutistic Disorder | Rett Syndrome | Asperger Syndrome | Pervasive Developmental Disorder | Childhood Disintegrative DisorderUnited States
-
Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
-
Frontera TherapeuticsPeking Union Medical College Hospital; Eye & ENT Hospital of Fudan University; Henan Provincial People's HospitalRecruitingX-Linked Retinitis PigmentosaChina
-
Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
-
Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
-
BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
-
4D Molecular TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
-
NightstaRx Ltd, a Biogen CompanyCompletedChoroideremiaFinland, United States, Canada, Denmark, Netherlands, Germany, United Kingdom, Brazil, France
-
Applied Genetic Technologies CorpCompletedX-Linked Retinitis PigmentosaUnited States
-
University Hospital, ToulouseAssociation for the development of research in DermatologyUnknown
-
University Hospital, ToulouseNot yet recruiting
-
University Hospital, ToulouseCompleted
-
AnaptysBio, Inc.Terminated
-
Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
-
Beacon TherapeuticsEnrolling by invitationX-Linked Retinitis PigmentosaUnited States
-
Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
-
TakedaRecruiting
-
TakedaAvailableHunter SyndromeUnited States, Australia, Mexico, Spain, United Kingdom
-
TakedaCompletedMucopolysaccharidosis (MPS)Brazil
-
Green Cross CorporationCompleted
-
Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
-
University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital for... and other collaboratorsRecruiting
-
GC Biopharma CorpRecruitingMucopolysaccharidosis II | Hunter SyndromeKorea, Republic of
-
Denali Therapeutics Inc.RecruitingMucopolysaccharidosis IIUnited States, Spain, United Kingdom, Czechia, France, Canada, Italy, Belgium, Netherlands, Germany, Argentina, Sweden, Turkey, Colombia
-
Homology Medicines, IncWithdrawnMucopolysaccharidosis IIUnited States, Canada
-
JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IIBrazil
-
ShireCompletedMucopolysaccharidosis IIUnited States, United Kingdom, Brazil, Germany