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Clinical Trials on Ichthyosis, X-forbundet
Total 1863 results
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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University of DundeeCompleted
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States
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Centre Hospitalier Universitaire de NīmesCompletedInsulin Resistance | Metabolic Syndrome XFrance
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Maastricht University Medical CenterCompleted
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University of California, DavisCompleted
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University of GuelphCompletedMetabolic Syndrome XCanada
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GlaxoSmithKlineCompletedMetabolic Syndrome XSpain, Argentina, Australia, Latvia, India, Mexico, Pakistan, Slovakia, Costa Rica, New Zealand, Romania, Russian Federation, Chile
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Laval UniversityCompleted
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University of LausanneUniversity Hospital Inselspital, BerneCompleted
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Rocket Pharmaceuticals Inc.Recruiting
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University of California, San DiegoRocket Pharmaceuticals Inc.Recruiting
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TakedaRecruitingSpinal and Bulbar Muscular AtrophyJapan
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Novartis PharmaceuticalsCompletedSpinal and Bulbar Muscular AtrophyUnited States, Germany, Italy, Denmark
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Henri Mondor University HospitalCompletedPeripheral Nervous System Diseases | Metabolic Syndrome X | Diabetic PolyneuropathyFrance
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Mansoura University Children HospitalCompletedBody Composition | Preterm Infant | Dual X-ray Absorptiometry (DXA) ScanEgypt
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Vanderbilt University Medical CenterNational Center for Research Resources (NCRR)Completed
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Les Laboratoires des Médicaments StérilesUniversity Hospital Fattouma BourguibaCompletedAcute Coronary Syndrome | Factor XTunisia
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Radboud University Medical CenterZonMw: The Netherlands Organisation for Health Research and DevelopmentCompletedObesity | Metabolic Syndrome XNetherlands
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Chronic Granulomatous DiseaseUnited States
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Gianni SoraruMario Negri Institute for Pharmacological ResearchRecruitingSpinal and Bulbar Muscular AtrophyItaly
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Rocket Pharmaceuticals Inc.Completed
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Assistance Publique - Hôpitaux de ParisCompleted
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University Hospital, Basel, SwitzerlandCompletedObesity | Hypogonadism | Metabolic Syndrome XSwitzerland
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AlgoMedica, Inc.Cedars-Sinai Medical CenterUnknownCancer, Lung | X-rays; Effects | Cancer Liver
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The Chaim Sheba Medical CenterRecruitingFragile X Syndrome | Williams Syndrome | Velocardiofacial SyndromeIsrael
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USDA, Western Human Nutrition Research CenterUniversity of California, Davis; University of Arkansas; Dairy Research InstituteCompletedObesity | Insulin Resistance | Metabolic Syndrome XUnited States
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Nepal Mediciti HospitalUnknownCentral Venous Catheterization | Exposure to X-Rays
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Boehringer IngelheimCompletedHypertension | Metabolic Syndrome XPhilippines
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Denali Therapeutics Inc.CompletedMucopolysaccharidosis IIUnited Kingdom, United States, Netherlands
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AnnJi Pharmaceutical Co., Ltd.Active, not recruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IIJapan
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ShireCompleted
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TakedaTakeda Development Center Americas, Inc.Active, not recruitingHunter SyndromeUnited States, Germany, Malaysia, Philippines, Thailand, Dominican Republic, Serbia, Vietnam
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JCR Pharmaceuticals Co., Ltd.Completed
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JCR Pharmaceuticals Co., Ltd.Completed
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Sangamo TherapeuticsTerminatedMucopolysaccharidosis II | MPS IIUnited States
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REGENXBIO Inc.Withdrawn
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Karen Brorup Heje PedersenCompletedHealthy Subjects | Spinal and Bulbar Muscular AtrophyDenmark
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Green Cross CorporationCompletedMucopolysaccharidosis IIKorea, Republic of
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Janssen-Ortho Inc., CanadaCompletedAutistic Disorder | Developmental Disabilities | Rett Syndrome | Asperger Syndrome | DCild Development Disorders, Pervasive
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Eunice Kennedy Shriver National Institute of Child...University of MinnesotaCompleted
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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AO GENERIUMRecruitingMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; Association...RecruitingAmyotrophic Lateral Sclerosis | Kennedy DiseaseFrance
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JCR Pharmaceuticals Co., Ltd.RecruitingMucopolysaccharidosis IIUnited States, Germany, Spain, France, Brazil, Argentina, Turkey, United Kingdom, Poland, Italy
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Denali Therapeutics Inc.Enrolling by invitationMucopolysaccharidosis IIUnited States, Canada, Belgium, Czechia, Netherlands
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Denali Therapeutics Inc.Active, not recruitingMucopolysaccharidosis IIUnited States, Netherlands, Canada, United Kingdom
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JCR Pharmaceuticals Co., Ltd.Enrolling by invitationMucopolysaccharidosis IIUnited States