Clinical Trials on Idiopaattinen tulehduksellinen myopatia

Total 1174 results

Newcastle-upon-Tyne Hospitals NHS Trust

Recruiting

Myotubular and Centronuclear Myopathy Patient Registry

X-linked Myotubular Myopathy | Centronuclear Myopathy | Myotubular Myopathy | Myotubular Myopathy 1 | Myotubular (Centronuclear) Myopathy | Centronuclear Myopathy, X-Linked

United Kingdom
Clinic for Special Children

Recruiting

WiTNNess - TNNT1 Myopathy Natural History Study (WiTNNess)

Myopathy | Myopathy; Hereditary | Myopathies, Nemaline | TNNT1-associated Myopathy | Infantile-onset Nemaline Rod Myopathy | Myopathy, Rod | Amish Nemaline Myopathy | Nemaline Myopathy 5 | NEM5 | Genetic Muscle Disease | Recessive Hereditary Disorder (Autosomal) | ANM

United States
Vastra Gotaland Region

Enrolling by invitation

Changes of Motor Function Tests in Congenital Myopathy Subjects Treated With Oral Salbutamol as Compared to no Treatment (COMPIS)

Musculoskeletal Diseases | Neuromuscular Diseases | Centronuclear Myopathy | Nemaline Myopathy | Congenital Myopathy | Myosin Storage Myopathy

Sweden
Ultragenyx Pharmaceutical Inc

Terminated

A Study to Evaluate the Safety of Aceneuramic Acid Extended Release (Ace-ER; UX001) Tablets in Glucosamine (UDP-N-acetyl)-2-Epimerase (GNE) Myopathy (GNEM) (Also Known as Hereditary Inclusion Body Myopathy [HIBM]) Patients With Severe Ambulatory Impairment

Hereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing Myopathy

Canada, United States, Bulgaria
Radboud University Medical Center
UMC Utrecht

Not yet recruiting

The Natural History and Muscle Fatigability of Patients With Congenital Myopathies. (READYCOM)

Centronuclear Myopathy | Nemaline Myopathy | Central Core Disease | Multi-Minicore Disease

Netherlands
Ultragenyx Pharmaceutical Inc

Terminated

Study to Evaluate the Safety and Efficacy of Aceneuramic Acid Extended-Release (Ace-ER) Tablets in Patients With Glucosamine (UDP-N-acetyl)-2-epimerase Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM)

Hereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing Myopathy

United States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
Astellas Gene Therapies

Completed

A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects (INCEPTUS)

X-linked Myotubular Myopathy

United States, France, United Kingdom, Canada, Germany
University of Florida
Audentes Therapeutics

Completed

Respiratory Muscle Function in Untreated X-Linked Myotubular Myopathy (XLMTM)

X-linked Myotubular Myopathy

United States
James Dowling
Canadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... and other collaborators

Recruiting

Tamoxifen Therapy for Myotubular Myopathy (TAM4MTM)

X Linked Myotubular Myopathy

United Kingdom, Canada, United States
Assiut University

Not yet recruiting

Magnetic Resonance Imaging and Ultrasonography in Evaluation of Muscle Diseases

Myositis | Congenital Myopathy | Acquired Myopathy
Astellas Gene Therapies

Completed

A Medical Chart Review of Patients With X-Linked Myotubular Myopathy (XLMTM)

Males With X-linked Myotubular Myopathy (XLMTM)

United States, United Kingdom
Cure CMD
University of Michigan; Congenital Muscle Disease International Registr

Completed

Myotubular Myopathy Event Study (MTMES)

X-linked Myotubular Myopathy

United States
Ra Pharmaceuticals

Terminated

Safety and Efficacy Study of Zilucoplan in Subjects With Immune-Mediated Necrotizing Myopathy

Immune Mediated Necrotizing Myopathy

United States, Netherlands, France, United Kingdom
Rigshospitalet, Denmark

Active, not recruiting

Contractile Cross Sectional Areas and Muscle Strength in Patients With Congenital Myopathies

Congenital Myopathy | Inherited Muscle Diseases | RYR1-myopathy

Denmark
Ultragenyx Pharmaceutical Inc

Completed

Phase 3 Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Sialic Acid in Patients With Glucosamine (UDP-N-acetyl)-2-epimerase Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM) (GNEM)

Hereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type

United States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
Ultragenyx Pharmaceutical Inc
Newcastle University

Completed

GNE-Myopathy Disease Monitoring Program (GNEM-DMP): A Registry and Prospective Observational Natural History Study to Assess GNE Myopathy or Hereditary Inclusion Body Myopathy (HIBM)

Hereditary Inclusion Body Myopathy | GNE Myopathy | Nonaka Disease | Quadriceps Sparing Myopathy (QSM) | Distal Myopathy With Rimmed Vacuoles (DMRV)

United States, Bulgaria, Canada, France, United Kingdom
Boston Children's Hospital
Muscular Dystrophy Association

Recruiting

Molecular and Genetic Studies of Congenital Myopathies

Centronuclear Myopathy | Myotubular Myopathy | Nemaline Myopathy | Central Core Disease | Congenital Fiber Type Disproportion | Multiminicore Disease | Rigid Spine Muscular Dystrophy | Undefined Congenital Myopathy

United States
Astellas Gene Therapies

Active, not recruiting

Gene Transfer Clinical Study in X-Linked Myotubular Myopathy (ASPIRO)

X-Linked Myotubular Myopathy

United States, Canada, France, Germany
Nobelpharma

Completed

Efficacy Confirmation Study of NPC-09

GNE Myopathy | Nonaka Disease | Distal Myopathy With Rimmed Vacuoles (DMRV) | Hereditary Inclusion Body Myopathy (hIBM)

Japan
Shanghai Eye Disease Prevention and Treatment Center

Not yet recruiting

Differences and Wearing Safety and Comfort of New Defocus Incorporated Multiple Segments Spectacle Lenses

Myopia, Progressive
Beijing Airdoc Technology Co., Ltd.

Recruiting

Myopia Preventing With Distance-image Screen (DIS)

Myopia, Progressive

China
Shanghai Eye Disease Prevention and Treatment Center

Recruiting

Double Helix Design Defocus Lens Spectacle (RACE) for Myopia Control

Myopia, Progressive

China
Beijing Airdoc Technology Co., Ltd.
The First People's Hospital of Xuzhou

Recruiting

Myopia Control Combined PBM With Myopic Defocus Lens in Children

Myopia, Progressive

China
Universidad Complutense de Madrid
Cooperativa de Ensino Superior, Politécnico e Universitário; Novovision; Instituto... and other collaborators

Active, not recruiting

Clinical Evaluation of MyoCare in Europe (CEME) (CEME)

Myopia, Progressive

Spain
Nova Southeastern University

Withdrawn

A Unified Index to Predict the Success Probability of Myopia Control

Myopia, Progressive
Shanghai Eye Disease Prevention and Treatment Center
Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine

Enrolling by invitation

Shanghai Child and Adolescent Large-scale Eye Study -High Myopia Registration (SCALE-HM)

High Myopia | Pathologic Myopia

China
National Taiwan University Hospital

Unknown

Genomewide Screening of Pathological Myopia

Pathological Myopia

Taiwan
Lawson Health Research Institute

Completed

Evaluation of Patients With Statin Myopathy Using an N of 1 Trial Design

Statin Myopathy

Canada
He Eye Hospital

Not yet recruiting

Effect of Atropine on Pupil Size and Quality of Vision

Myopia, Progressive

China
University of Bradford
Coopervision, Inc.; University of Huddersfield

Not yet recruiting

Management of Myopia in University Students Using Dual Focus Soft Contact Lenses (MoMUS)

Myopia, Progressive
Visioneering Technologies, Inc

Recruiting

Progressive Myopia Treatment Evaluation for NaturalVue Multifocal Contact Lens Trial (PROTECT)

Myopia

United States, Canada, Hong Kong, Singapore
University Eye Hospital, Freiburg

Recruiting

Low-dose Atropine for Myopia Control in Children (AIM)

Myopia, Progressive

Germany
Shanghai 10th People's Hospital

Completed

Effect of Virtual Reality-Based Visual Training for Myopia Control in Children

Myopia | Myopia, Progressive

China
Tianjin Eye Hospital

Active, not recruiting

Myopia-control Efficacy by Peripheral Defocus Lens (PDL)

Myopia, Progressive

China
Tianjin Eye Hospital

Completed

Near Horizontal Heterophoria in Chinese Children

Myopia, Progressive

China
Sultan Qaboos University
Christian Medical College, Vellore, India

Unknown

Atropine 0.01% Eye Drops in Myopia Study (AIMS)

Myopia, Progressive

Oman
Peking University People's Hospital

Unknown

Efficacy Study of Different Lens Treatments on Chinese Adolescent Myopia (DLTCAM)

Progressive Myopia

China
Shanghai Eye Disease Prevention and Treatment Center

Recruiting

Low Concentration Atropine in the Prevention of Myopia in Children.

Myopia, Progressive

China
Shanghai Eye Disease Prevention and Treatment Center
Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine

Not yet recruiting

Myopia Prevention Through Monitoring and Motivating Outdoor Activities With Smartwatches

Myopia, Progressive
iVeena Delivery Systems, Inc.

Not yet recruiting

Efficacy of IVMED-85 on Pediatric Myopia

Myopia, Progressive
Shanghai Eye Disease Prevention and Treatment Center
Peking University People's Hospital; Shanghai General Hospital, Shanghai Jiao... and other collaborators

Not yet recruiting

Efficacy and Safety of Low-concentration Atropine for Myopia Control in Chinese Children and Adolescents (LAMC)

Myopia, Progressive
Scripps Health

Completed

Adverse Events Related to Low Dose Atropine (AELDA)

Myopia, Progressive

United States
Cloudbreak Therapeutics, LLC
Novotech (Australia) Pty Limited

Completed

Safety, Tolerability and Pharmacodynamics Evaluation of CBT-009 Eye Drop

Myopia, Progressive

Australia
Texas Tech University Health Sciences Center

Recruiting

Annatto-derived GG for Statin-associated Myopathy (GG-statin)

Myopathy; Primary

United States
Reneo Pharma Ltd

Completed

An Efficacy and Safety Study of 24 Week Treatment With Mavodelpar (REN001) in Primary Mitochondrial Myopathy Patients (STRIDE)

Primary Mitochondrial Myopathy

United States, Spain, Australia, France, United Kingdom, New Zealand, Denmark, Norway, Czechia, Belgium, Canada, Germany, Hungary, Italy, Netherlands
Stealth BioTherapeutics Inc.

Terminated

A Trial to Evaluate Safety and Efficacy of Elamipretide Primary Mitochondrial Myopathy Followed by Open-Label Extension (MMPOWER-3)

Primary Mitochondrial Myopathy

United States, Germany, Canada, Italy, United Kingdom, Denmark, Hungary
Reneo Pharma Ltd

Terminated

A Study of the Safety of REN001 in Patients With Primary Mitochondrial Myopathy

Primary Mitochondrial Myopathy

United Kingdom
Armgo Pharma, Inc.
National Institute of Nursing Research (NINR); National Institute of Neurological... and other collaborators

Completed

S 48168 (ARM 210) for the Treatment of RYR1-related Myopathies (RYR1-RM)

RYR-1 Myopathy

United States
Menicon Co., Ltd.
Universidad Europea de Madrid; Aston University; Clinica novovision

Completed

Myopia Control With Orthokeratology Contact Lenses in Spain (MCOS)

Children, Only | Myopia, Progressive | Contact Lens Complication | Perception, Self | Axial Myopia
Rockefeller University

Terminated

Metabolic Features of Post-Myopathy Patients Associated With Statin Treatment

Myopathy (Statin Associated)

United States

Clinical Trials on Idiopaattinen tulehduksellinen myopatia

Sponsors and Collaborators

Medical Conditions

Drug Interventions

CROs by country

CROs in France

Conditions

Rare Diseases

Drug Interventions

Dietary Supplements

Sponsor/Collaborators

Locations