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Clinical Trials on In Development for Cystic Fibrosis in Australia
Total 270 results
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Klinikum Wels-GrieskirchenGenzyme, a Sanofi CompanyCompletedFocus of Study: Prevalence of Fabry Disease in CKD PopulationAustria
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BioMarin PharmaceuticalCompletedAchondroplasiaUnited States, Australia, United Kingdom, Japan, Spain, Turkey
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QED Therapeutics, Inc.RecruitingAchondroplasiaUnited States, Spain, United Kingdom, France, Canada, Australia
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QED Therapeutics, Inc.Enrolling by invitationAchondroplasiaUnited States, Spain, United Kingdom, France, Australia, Canada
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Marinus PharmaceuticalsEnrolling by invitationTuberous Sclerosis ComplexUnited States, Spain, United Kingdom, China, Italy, France, Israel, Germany, Canada, Australia
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Genzyme, a Sanofi CompanyTerminatedPolycystic Kidney, Autosomal DominantBelgium, Germany, Czechia, United States, Italy, Poland, Argentina, Australia, Austria, Canada, China, Denmark, France, Israel, Japan, Korea, Republic of, Netherlands, Portugal, Romania, Spain, Taiwan, Turkey, United Kingdom
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BioMarin PharmaceuticalCompletedAchondroplasiaSpain, Denmark, Italy, Austria, Germany, Sweden
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Gilead SciencesCompletedHepatitis C | Cirrhosis | Portal Hypertension | With or Without Liver DecompensationUnited States, Spain, New Zealand, Australia, France
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Novartis PharmaceuticalsCompletedTuberous Sclerosis | Subependymal Giant Cell AstrocytomaUnited States, Belgium, Canada, Germany, Italy, Russian Federation, Netherlands, Poland, Australia, United Kingdom
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Children's Hospital Medical Center, CincinnatiUniversity of Pittsburgh; Vanderbilt University Medical Center; Children's Hospital... and other collaboratorsNot yet recruitingDepression, Postpartum | Neurodevelopmental Disorders | Heart Defects, Congenital | Trauma, Psychological | Anxiety in PregnancyUnited States, Australia
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Novartis PharmaceuticalsCompletedTuberous Sclerosis Complex-associated Refractory SeizuresUnited States, Colombia, Belgium, France, Japan, Taiwan, Turkey, Spain, Thailand, Korea, Republic of, Australia, Hungary, United Kingdom, Canada, Norway, Germany, Italy, Russian Federation, Denmark, Argentina, Netherlands, Greece, P... and more
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AmgenCompletedOsteogenesis ImperfectaUnited States, Italy, United Kingdom, Belgium, Czechia, Australia, Canada, France, Bulgaria, Poland, Spain, Hungary, Germany
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BioMarin PharmaceuticalActive, not recruitingAchondroplasiaUnited States, Australia, Germany, Spain, United Kingdom, Japan, Turkey
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Insmed IncorporatedCompletedLaron Syndrome | Growth Hormone Insensitivity Syndrome (GHIS)United States, Argentina, Australia, Brazil, China, Egypt, Germany, Israel, Italy, Norway, Peru, Slovakia, Turkey, United Kingdom
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SanofiRecruitingOsteochondrodysplasiaAustralia, Spain, Korea, Republic of, China, Italy
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BioMarin PharmaceuticalCompletedAchondroplasiaUnited States, Australia, Germany, Spain, United Kingdom, Japan, Turkey
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Warner ChilcottCompletedOsteogenesis ImperfectaChile, United States, Spain, Australia, Belgium, United Kingdom, Czech Republic, Finland, Germany, Hungary, Italy, Poland, South Africa
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Grifols Therapeutics LLCActive, not recruitingPulmonary Emphysema in Alpha-1 PI DeficiencyUnited States, Australia, Denmark, New Zealand, Estonia, Poland, Russian Federation, Sweden, Brazil, Canada, France, Finland
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Medacta International SARecruitingArthrosis | Congenital Hip Dysplasia | Traumatic Arthritis | Rheumatoid Polyarthritis | Avascular Necrosis of the Femoral HeadAustria, Italy, Switzerland, United Kingdom
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Zimmer BiometActive, not recruitingAvascular Necrosis | Inflammatory Arthritis | Osteoarthritis, Hip | Congenital Hip Dysplasia | Post-traumatic; Arthrosis | Rheumatoid Arthritis With Adequate Bone QualityNetherlands, Finland, Belgium, France, Spain, Australia, Canada, United Kingdom
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Lumos PharmaActive, not recruitingGrowth Hormone DeficiencyUnited States, Australia, Israel, New Zealand, Poland, Ukraine
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Otsuka Pharmaceutical Europe LtdUnknownAutosomal Dominant Polycystic Kidney DiseaseSpain, United Kingdom, Germany, France, Belgium, Switzerland, Austria
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AmgenCompletedOsteogenesis ImperfectaSpain, United States, Turkey, Austria, Germany, Greece, Hungary, Italy
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QED Therapeutics, Inc.Enrolling by invitationAchondroplasiaAustralia, United States, Argentina, Canada, France, Germany, Italy, Norway, Singapore, Spain, United Kingdom
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QED Therapeutics, Inc.RecruitingAchondroplasiaUnited States, Spain, Singapore, Canada, United Kingdom, France, Australia, Norway, Argentina, Germany, Italy
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Australia, Belgium, Germany, Italy, Poland, Romania, United Kingdom, Argentina, Canada, France, Netherlands, Russian Federation
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PfizerTerminatedAchondroplasiaUnited States, Canada, China, Japan, Australia, Germany, France, United Kingdom, Denmark, Belgium, Italy, Portugal, Spain, Switzerland
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DePuy InternationalTerminatedOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Nonunion of Femoral FracturesAustria, Czech Republic, Finland, Germany, Norway, Portugal, Switzerland, United Kingdom
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Ultragenyx Pharmaceutical IncMereo BioPharmaActive, not recruitingOsteogenesis ImperfectaUnited States, Turkey, Germany, United Kingdom, Italy, Portugal, Canada, Australia, Argentina, France, Netherlands, Poland
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Versartis Inc.Premier Research Group plcCompletedAdult Growth Hormone DeficiencyUnited States, Australia, Germany, United Kingdom
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Ascentage Pharma Group Inc.Merck Sharp & Dohme LLCRecruitingMelanoma | P53 Mutation | Uveal Melanoma | Cutaneous Melanoma | Mucosal Melanoma | Malignant Peripheral Nerve Sheath Tumors | MPNST | Unresectable or Metastatic Melanoma or Advanced Solid Tumors | MDM2 Gene MutationUnited States, Australia
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
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Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, Hungary, United Kingdom, Australia, Bulgaria, Poland, Turkey
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Otsuka Pharmaceutical Development & Commercialization...CompletedPolycystic Kidney, Autosomal DominantBelgium, Germany, Italy, Spain, Sweden, United States, Canada, Australia, Netherlands, Czechia, Poland, Denmark, Israel, Hungary, Russian Federation, South Africa, United Kingdom, Romania, Argentina, Norway
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ArQule, Inc. (a wholly owned subsidiary of Merck...Worldwide Clinical TrialsTerminatedPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus SyndromeUnited States, Australia, Italy, Spain
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PfizerCompletedPolycystic Kidney, Autosomal DominantUnited States, Canada, Australia, Sweden, Spain, Poland, Korea, Republic of, Switzerland, United Kingdom, Moldova, Republic of, Italy, Czech Republic, Hungary, Lithuania, Romania, Slovakia, Turkey
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Merck Sharp & Dohme LLCActive, not recruitingPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)United States, Australia, Brazil, Italy, United Kingdom
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Longboard PharmaceuticalsActive, not recruitingDravet Syndrome | Lennox-Gastaut Syndrome | Developmental and Epileptic EncephalopathyUnited States, Australia
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Reata, a wholly owned subsidiary of BiogenTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, United Kingdom, Australia, France, Japan, Germany, Belgium, Czechia, Italy
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Ascendis Pharma Endocrinology Division A/SCompletedA Safety, Tolerability and Efficacy Study of TransCon hGH in Children With Growth Hormone DeficiencyEndocrine System Diseases | Pituitary Diseases | Hormone Deficiency | Growth Hormone Deficiency, PediatricUnited States, Canada, Australia, New Zealand
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Longboard PharmaceuticalsCompletedDravet Syndrome | Lennox Gastaut Syndrome | Developmental and Epileptic EncephalopathyUnited States, Australia
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QED Therapeutics, Inc.RecruitingHypochondroplasiaUnited States, Australia, Norway, Portugal, Singapore, Spain, Canada, France, Germany, Sweden, United Kingdom
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
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Novartis PharmaceuticalsCompletedAutosomal Dominant Polycystic Kidney DiseaseGermany, Austria, France
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Ascendis Pharma Endocrinology Division A/SActive, not recruitingEndocrine System Diseases | Adult Growth Hormone Deficiency | Hormone DeficiencyUnited States, Armenia, Georgia, Greece, Ukraine, Australia, Canada, France, Israel, Italy, Japan, Malaysia, Poland, Romania, Serbia, Slovakia, Spain, Turkey, United Kingdom, Germany, Korea, Republic of
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OPKO Health, Inc.Active, not recruitingSafety and Efficacy Phase 3 Study of Long-acting hGH (MOD-4023) in Growth Hormone Deficient ChildrenPediatric Growth Hormone DeficiencyIsrael, United States, India, Korea, Republic of, Australia, Taiwan, Spain, Argentina, Belarus, Bulgaria, Canada, Colombia, Georgia, Greece, Mexico, New Zealand, Poland, Russian Federation, Ukraine, United Kingdom
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Grifols Therapeutics LLCEnrolling by invitationPulmonary Emphysema in Alpha-1 Antitrypsin DeficiencyUnited States, New Zealand, Denmark, Australia, Finland, Estonia, Canada, Poland, Russian Federation, Sweden, France
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University of PennsylvaniaNational Heart, Lung, and Blood Institute (NHLBI); University Medical Center... and other collaboratorsEnrolling by invitationAcute Respiratory Distress Syndrome in ChildrenUnited States, Netherlands, Israel, Thailand, New Zealand, United Kingdom, Australia, Brazil, Canada, China, India, Italy, Malaysia, United Arab Emirates, Spain
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AEterna ZentarisCompletedGrowth Hormone Deficiency With Pituitary AnomaliesUnited Kingdom, United States, France, Poland, Spain, Austria, Germany, Italy, Serbia
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Ascendis Pharma A/SCompletedEndocrine System Diseases | Pituitary Diseases | Hormone Deficiency | Growth Hormone Deficiency, PediatricUnited States, Armenia, Belarus, Bulgaria, Georgia, Greece, Russian Federation, Ukraine, Australia, New Zealand, Poland