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Clinical Trials on Inherited BMF Syndrome
Total 35118 results
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Sohag UniversityAssiut University; Kyoto UniversityRecruitingInherited BMF SyndromeEgypt
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Peter MacCallum Cancer Centre, AustraliaNational Health and Medical Research Council, Australia; University of MelbourneRecruitingHematologic Diseases | Inherited Platelet Disorder | Inherited BMF SyndromeAustralia
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University of UlmActive, not recruitingPrimary Myelofibrosis | Secondary Myelofibrosis | Post-PV MF | PMF | SMF | Post-ET MFGermany
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Assistance Publique - Hôpitaux de ParisUnknownImmune Deficiency and Early BMF in ChildhoodFrance
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Stanford UniversityNational Institutes of Health (NIH)CompletedMyelodysplastic Syndromes | Myeloproliferative Disorders | Myelodysplastic Syndromes (MDS) | Blood and Marrow Transplant (BMT) | Myeloproliferative Disorders (MPD)United States
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Franziska WachterHarvard Clinical and Translational Science Center (Harvard Catalyst)RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | MDS | Aml | Myeloid Neoplasm | Myeloid Malignancies | Inherited Bone Marrow Failure SyndromeUnited States
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Juva Skin & Laser CenterAllerganCompletedBrassiere Strap Fat (BSF) | Bra Strap Fat (BSF)United States
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Mayo ClinicRecruitingHematologic Neoplasms | Myeloid Malignancy | Cytopenia | Bone Marrow Failure Syndrome | Clonal Cytopenia of Undetermined Significance | Clonal Hematopoiesis of Indeterminate Potential | Low Risk Myelodysplastic Syndrome | Inherited Bone Marrow Failure Syndrome | Clonal Expansion | Hereditary Neoplastic... and other conditionsUnited States
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National Institute of Allergy and Infectious Diseases...CompletedInherited Immune DeficienciesUnited States
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National Cancer Institute (NCI)RecruitingInherited Bone Marrow Failure Syndrome | Familial Platelet Disorder With Predisposition to Myeloid MalignanciesUnited States
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Kartos Therapeutics, Inc.RecruitingPrimary Myelofibrosis (PMF) | Post-Polycythemia Vera MF (Post-PV-MF) | Post-Essential Thrombocythemia MF (Post-ET-MF)United States, Korea, Republic of, Germany, Australia, Hungary, France, Spain, Italy, Taiwan, Thailand, Brazil, Poland, Turkey, Israel, Portugal, Romania, Argentina, Bulgaria, Canada, Croatia, Czechia, Lithuania, Mexico, Philippines, United... and more
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Massachusetts General HospitalNational Cancer Institute (NCI); Boston Medical CenterCompletedGenetic TestingUnited States
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Assistance Publique - Hôpitaux de ParisInstitut ImagineNot yet recruitingAutoinflammatory Disease | FMF | TRAPS | MKD | Cryopyrin Associated Periodic Syndrome | HaploinsufficiencyFrance
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Humanigen, Inc.SuspendedMyelodysplastic Syndrome (MDS) | Myelofibrosis (MF)United States, Australia
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Vanderbilt-Ingram Cancer CenterNational Cancer Institute (NCI); University of South FloridaRecruitingBreast Cancer | Colorectal Cancer | Prostate Cancer | Endometrial Cancer | Inherited Cancer SyndromeUnited States
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Stanford UniversityCompletedMyelodysplastic Syndromes | Leukemia | Myeloproliferative Disorders | Acute Disease | Myelodysplastic Syndromes (MDS) | Leukemia, Myeloid, Chronic | Blood and Marrow Transplant (BMT)United States
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Oklahoma State University Center for Health SciencesNational Institute on Minority Health and Health Disparities (NIMHD)Completed
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Novartis PharmaceuticalsCompletedPrimary Myelofibrosis (PMF) | Post Polycythaemia Myelofibrosis (PPV MF) | Post Essential Thrombocythaemia Myelofibrosis (PET-MF)United Kingdom
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National Cancer Institute (NCI)CompletedBMI | General Demographics CharacteristicsCosta Rica
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University of MinnesotaCompleted
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Stanford UniversityRecruitingBlood and Marrow Transplant (BMT)United States
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Rejuven Dermaceutical Co., Ltd.Completed
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Fondazione TelethonOspedale San RaffaeleCompleted
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Ajax Therapeutics, Inc.Not yet recruitingPrimary Myelofibrosis | Post-Polycythemia Vera Myelofibrosis | PMF | Post-Essential Thrombocythemia Myelofibrosis | PPV-MF | PET-MFUnited States
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University of Michigan Rogel Cancer CenterCompletedPatients Undergoing Bone Marrow Transplant (BMT)United States
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Fondazione TelethonOspedale San RaffaeleActive, not recruitingWiskott-Aldrich SyndromeItaly, United States
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David WilliamsActive, not recruitingWiskott-Aldrich SyndromeUnited States
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GenethonInstitute of Child Health; Great Ormond Street Hospital for Children NHS Foundation...Completed
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GlaxoSmithKlineCompletedWiskott-Aldrich SyndromeUnited States
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GenethonHôpital Necker-Enfants MaladesCompleted
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National Human Genome Research Institute (NHGRI)Active, not recruitingWiskott- Aldrich Syndrome | ADA Deficient SCIDUnited States
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GenethonActive, not recruitingWiskott-Aldrich SyndromeUnited Kingdom, France
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Capital Research Institute of PediatricsUnknownWiskott-Aldrich Syndrome
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St. Jude Children's Research HospitalCompletedWiskott-Aldrich SyndromeUnited States
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...CompletedWiskott-Aldrich SyndromeUnited States, Canada
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The Korean Society of Pediatric Hematology OncologyCompletedWiskott-Aldrich SyndromeKorea, Republic of
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National Eye Institute (NEI)TerminatedInherited Retinal Degeneration | Inherited Ophthalmic DiseasesUnited States
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Suzhou Zelgen Biopharmaceuticals Co.,LtdCompletedPrimary Myelofibrosis (PMF) | Post-polycythemia Vera Myelofibrosis(Post-PV MF) | Post-essential Thrombocythemia Myelofibrosis(Post-ET MF)China
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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Royal Brompton & Harefield NHS Foundation TrustBen Williams TrustUnknownInherited Cardiac Conditions
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Inherited Bone Marrow Failure SyndromeUnited States
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Icahn School of Medicine at Mount SinaiDompé Farmaceutici S.p.ARecruitingMyelofibrosis (PMF) | Post Essential Thrombocythemia Myelofibrosis (ET-MF) | Post Polycythemia Vera Related Myelofibrosis (PV-MF)United States
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Kartos Therapeutics, Inc.RecruitingPrimary Myelofibrosis (PMF) | Post-Polycythemia Vera Myelofibrosis (Post-PV-MF) | Post-Essential Thrombocythemia Myelofibrosis (Post-ET-MF)United States, Mexico, Bulgaria, Poland, Russian Federation, Belarus, Georgia, South Africa, Ukraine
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Samus Therapeutics, Inc.TerminatedPrimary Myelofibrosis (PMF) | Post-Polycythemia Vera Myelofibrosis (Post-PV MF) | Post-Essential Thrombocythemia Myelofibrosis (Post-ET MF)United States
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Tel-Aviv Sourasky Medical CenterUnknownDifference in BMD Between Both Hips
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Imago BioSciences, Inc., a subsidiary of Merck...CompletedMyelofibrosis | Primary Myelofibrosis (PMF) | Post-polycythemia Vera Myelofibrosis (PPV-MF) | Post-essential Thrombocythemia Myelofibrosis (PET-MF)Germany, United States, Australia, Italy, United Kingdom
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Manchester University NHS Foundation TrustRecruiting
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Soma JyonouchiBaylor College of MedicineCompletedX-linked Thrombocytopenia | Wiskott-Aldrich Syndrome (WAS)United States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic Anemia | Telomere Biology Disorders | Inherited Bone Marrow Failure SyndromesUnited States