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Clinical Trials on Inherited Neuromuscular Conditions
Total 437627 results
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Ohio State UniversityAdvanced BionicsRecruiting
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IntraBio IncRecruitingAtaxia Telangiectasia | Louis Bar SyndromeSpain, United States, Germany, United Kingdom
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Christoph ArnoldnerRecruiting
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St. Jude Children's Research HospitalRecruitingGlaucoma, Congenital | Retinoblastoma | Cataracts Infantile | LeucocoriaUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingAutism Spectrum Disorder | Fragile X Syndrome | Developmental Delay | Genetic Disorder | Asperger DisorderUnited States
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National Cancer Institute (NCI)RecruitingColorectal Neoplasms | Cholangiocarcinoma | Bile Duct Cancer | Pancreas Cancer | Gastric NeoplasmsUnited States
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University of WuerzburgGerman Federal Ministry of Education and Research; Deutsche Krebshilfe e.V....RecruitingCushing Syndrome | Pheochromocytoma | Adrenocortical Carcinoma | Conn Syndrome | Adrenal TumorsGermany
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Genzyme, a Sanofi CompanyRecruitingFabry DiseaseCroatia, United States, Argentina, Australia, Belgium, Bulgaria, Canada, Germany, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Malaysia, Philippines, Poland, Romania, Singapore, Slovakia, Taiwan, Thailand, United Kingdom, Vietn... and more
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National Cancer Institute (NCI)Active, not recruitingRecurrent Ewing Sarcoma | Recurrent Osteosarcoma | Stage III Osteosarcoma AJCC v7 | Stage IV Osteosarcoma AJCC v7 | Stage IVA Osteosarcoma AJCC v7 | Stage IVB Osteosarcoma AJCC v7 | Metastatic Osteosarcoma | Metastatic Ewing Sarcoma | Unresectable Ewing Sarcoma | Unresectable OsteosarcomaFrance
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National Human Genome Research Institute (NHGRI)CompletedParkinson Disease | Gaucher DiseaseUnited States
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National Cancer Institute (NCI)Canadian Cancer Trials GroupActive, not recruitingAnal Canal Cloacogenic Carcinoma | Stage III Anal Cancer AJCC v8 | Anal Margin Squamous Cell Carcinoma | Stage IIB Anal Cancer AJCC v8 | Anal Basaloid Squamous Cell CarcinomaUnited States, Canada
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Acera Surgical, Inc.Active, not recruitingDiabetic Foot Ulcer | Venous Leg UlcerUnited States
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Massachusetts General HospitalActive, not recruitingCovid19 | Diabetes Mellitus, Type I | Autoimmune Diabetes | Diabetes Mellitus, Type OneUnited States
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Passage Bio, Inc.Active, not recruitingGM1 Gangliosidosis | GM1 Gangliosidosis, Type I | GM1 Gangliosidosis, Type 2 | Beta-Galactosidase-1 (GLB1) DeficiencyUnited States, Canada, United Kingdom, Turkey, Brazil
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Amicus Therapeutics France SASCompleted
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Imperial College LondonTerminatedRNA Virus Infections | Respiratory Tract Infections | Covid19 | Influenza | Infection, Bacterial | SARS (Severe Acute Respiratory Syndrome) | Respiratory Viral Infection | Infection ViralUnited Kingdom
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University Hospital, AntwerpEnrolling by invitationRespiratory Viral Infection | Respiratory Morbidity | Cystic Fibrosis in Children | Respiratory Bacterial Infection | Inflammation LungsBelgium
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Sangamo TherapeuticsActive, not recruitingFabry DiseaseUnited States, United Kingdom, Taiwan, Australia, Germany, Italy, Canada
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ShireCompletedHunter SyndromeUnited States, Spain, Canada, United Kingdom, Mexico, Australia, France
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Hoffmann-La RocheActive, not recruitingNeoplasms | Neoplasms by Histologic Type | Lung Diseases | Neoplasms by Site | Adenocarcinoma | Carcinoma | Neoplasms, Germ Cell and Embryonal | Head and Neck Neoplasms | Carcinoma, Non-Small-Cell Lung | Bronchial Diseases | Respiratory Tract Neoplasms | Thoracic Neoplasms | Carcinoma, Bronchogenic | Neoplasms, Nerve... and other conditionsItaly, Korea, Republic of, Australia, Spain, Argentina, Belgium, Brazil, France, Portugal, United Kingdom, United States, Japan, Mexico, Poland, Norway, Costa Rica, Switzerland, Netherlands, Germany, Sweden, Turkey, Ireland, Panama
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Zimmer BiometActive, not recruitingOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Revision Total Shoulder Arthroplasty | Ununited Humeral Head Fracture | Irreducible 3-and 4-part Proximal Humeral Fractures | Gross Rotator Cuff DeficiencyUnited States, United Kingdom
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Vibrato Medical, Inc.National Institutes of Health (NIH); Vascular and Interventional Specialists...CompletedPeripheral Arterial Disease | Diabetic Foot Ulcer | Wound; FootUnited States
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Queen Mary University of LondonRoyal Free Hospital NHS Foundation TrustActive, not recruitingCarcinoid Syndrome | Carcinoid Heart Disease | Tricuspid Regurgitation | Tricuspid Valve DiseaseUnited Kingdom
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Vastra Gotaland RegionKarolinska University Hospital; Göteborg University; Uppsala University HospitalCompleted
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Peking Union Medical College HospitalActive, not recruitingHepatitis B | Hepatocellular CarcinomaChina
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingGenetically Modified T-Cells Followed by Aldesleukin in Treating Patients With Stage III-IV MelanomaMetastatic Melanoma | Stage III Cutaneous Melanoma AJCC v7 | Stage IV Cutaneous Melanoma AJCC v6 and v7 | Stage IIIC Cutaneous Melanoma AJCC v7 | Stage IIIA Cutaneous Melanoma AJCC v7 | Stage IIIB Cutaneous Melanoma AJCC v7United States
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Mayo ClinicNational Cancer Institute (NCI)CompletedGastroesophageal Junction Adenocarcinoma | Gastric Cardia Adenocarcinoma | Stage IB Gastric Cancer AJCC v7 | Stage II Gastric Cancer AJCC v7 | Stage IIA Gastric Cancer AJCC v7 | Stage IIB Gastric Cancer AJCC v7 | Stage IIIA Gastric Cancer AJCC v7 | Stage IIIB Gastric Cancer AJCC v7United States
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Green Cross CorporationCompleted
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VA Office of Research and DevelopmentActive, not recruitingIschemic Stroke | Obstructive Sleep Apnea | Transient Ischemic Attack (TIA)United States
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Alliance for Clinical Trials in OncologyNational Cancer Institute (NCI); Canadian Cancer Trials GroupActive, not recruitingStage II Breast Cancer | Stage IIIA Breast Cancer | Invasive Breast Carcinoma | Stage IIA Breast Cancer | Stage IIB Breast Cancer | Lobular Breast Carcinoma | Ductal Breast Carcinoma | Tubular Breast Carcinoma | Medullary Breast CarcinomaUnited States, Canada
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4D Molecular TherapeuticsActive, not recruitingFabry DiseaseUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedMetastatic Skin Squamous Cell Carcinoma | Metastatic Malignant Neoplasm | Unresectable Malignant Neoplasm | Refractory Malignant Neoplasm | Appendix Adenocarcinoma | Locally Advanced Malignant Neoplasm | Skin Squamous Cell Carcinoma | Locally Advanced Skin Squamous Cell Carcinoma | Metastatic Small... and other conditionsUnited States
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Henry Ford Health SystemAbiomed Inc.Enrolling by invitationAcute Myocardial Infarction | Cardiogenic Shock | STEMI | NSTEMI - Non-ST Segment Elevation MI | STEMI - ST Elevation Myocardial Infarction | NSTEMI | Acute Myocardial Infarction With ST Elevation | Acute Myocardial Infarction of Right Ventricle (Disorder) | Acute Myocardial Infarction of Left VentricleUnited States
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University of AlbertaTerminatedChronic Obstructive Pulmonary Disease | Obstructive Sleep Apnea | Hypoventilation | Sleep Related HypoventilationCanada
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Eli Lilly and CompanyActive, not recruitingJuvenile Psoriatic Arthritis | Enthesitis Related ArthritisSpain, Belgium, Germany, Italy, United Kingdom, Denmark, Mexico, Netherlands, Switzerland
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McGill University Health Centre/Research Institute...Weston Brain InstituteCompletedParkinson's Disease | Obstructive Sleep ApneaCanada
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McGill University Health Centre/Research Institute...Canadian Institutes of Health Research (CIHR); American Thoracic SocietyCompletedParkinson's Disease | Obstructive Sleep ApneaCanada
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R-PharmData Management 365; Exacte Labs LLC; Federal State Budgetary Institution "NMIC... and other collaboratorsActive, not recruitingHead and Neck Squamous Cell Carcinoma | Skin Melanoma | Squamous Non-small-cell Lung CancerRussian Federation
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Marinella TemprosaNational Institute on Aging (NIA)Enrolling by invitationDiabetes | Dementia | PreDiabetes | Alzheimer Disease | Dementia, VascularUnited States
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Stryker Trauma GmbHEnrolling by invitationRheumatoid Arthritis | Avascular Necrosis | Rotator Cuff Tears | Traumatic Arthritis | Osteoarthritis Shoulder | Correction of Functional Deformity | Fractures Humerus | Revision of Other Devices if Sufficient Bone Stock RemainsUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI)CompletedGastric Adenocarcinoma | Gastric Squamous Cell Carcinoma | Gastroesophageal Junction Adenocarcinoma | Metastatic Malignant Neoplasm in the Stomach | Stage IV Esophageal Adenocarcinoma AJCC v7 | Stage IV Esophageal Squamous Cell Carcinoma AJCC v7United States
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National Jewish HealthCystic Fibrosis FoundationEnrolling by invitationMycobacterium Infections | Cystic Fibrosis | Nontuberculous Mycobacterial Lung Disease | Nontuberculous Mycobacterium Infection | Mycobacterium; PulmonaryUnited States
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Fondation LenvalActive, not recruitingCOVID-19 | Psychiatric Disorder | Eating Disorders in AdolescenceFrance
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Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedNon Small Cell Lung Cancer | Stage Ib Lung Carcinoma | Stage IIA Lung Carcinoma | Stage IIIA Lung Carcinoma | Stage I Lung Cancer | Stage IA Lung Carcinoma AJCC V7United States
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Coloplast A/SCompletedDiabetic Foot Ulcer | Venous Leg UlcerUnited Kingdom
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University of NebraskaNational Cancer Institute (NCI)CompletedGastric Cancer | Unspecified Adult Solid Tumor, Protocol Specific | Liver Cancer | Gallbladder Cancer | Extrahepatic Bile Duct CancerUnited States
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Montreal Heart InstituteActive, not recruitingNeurodegenerative Diseases | Primary Progressive Aphasia | Semantic Dementia | Logopenic Progressive Aphasia | Non-fluent AphasiaCanada
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Freeline TherapeuticsCompletedLysosomal Storage Diseases | Fabry DiseaseGermany, United Kingdom
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Royal Liverpool University HospitalCompletedDepression | COVID-19 | Anxiety | Psychological Distress | Post-traumatic Stress Disorder | Post Intensive Care SyndromeUnited Kingdom
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Spark TherapeuticsActive, not recruitingLysosomal Storage Diseases | Glycogen Storage Disease Type II | Glycogen Storage Disease Type 2 | Pompe Disease (Late-onset) | Pompe Disease | LOPD | Acid Maltase DeficiencyUnited States, Canada, Netherlands, France, Denmark, Germany, Italy, United Kingdom