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Clinical Trials on Juvenile-Onset Huntington Disease in New Zealand
Total 286 results
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MDD US Operations, LLC a subsidiary of Supernus...CompletedParkinson's Disease | Akinesia | Motor Symptoms | Hypomobility | Delayed Levodopa OnsetUnited States
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UCB Biopharma S.P.R.L.CompletedFocal-Onset Seizures | Drug-resistant EpilepsyUnited States, Australia, Belgium, Bulgaria, Canada, Czechia, France, Germany, Hungary, Italy, Japan, Lithuania, Mexico, Poland, Portugal, Slovakia, Spain, Turkey, United Kingdom
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UCB Biopharma SRLTerminatedDrug-Resistant Epilepsy | Focal-Onset SeizuresUnited States, Australia, Belgium, Bosnia and Herzegovina, Bulgaria, Canada, Croatia, Czechia, Denmark, Estonia, Finland, France, Germany, Greece, Hungary, Ireland, Italy, Japan, Lithuania, Mexico, Poland, Romania, Serbia, Slovakia, Spain, Turk... and more
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Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
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Rutgers, The State University of New JerseyNational Cancer Institute (NCI)CompletedAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Secondary Acute Myeloid Leukemia | Myelodysplastic Syndrome | Recurrent Acute Myeloid Leukemia | Refractory Acute Myeloid Leukemia | Myeloproliferative Neoplasm | Myeloblasts 10 Percent or More of Bone Marrow Nucleated CellsUnited States
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Race Oncology LtdAstex Pharmaceuticals, Inc.WithdrawnAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Recurrent Acute Myeloid Leukemia | Refractory Acute Myeloid Leukemia | Higher Risk Myelodysplastic SyndromeAustralia
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National Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Chronic Myelomonocytic Leukemia | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesCanada, United States
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Indiana UniversityNational Institute on Aging (NIA); Alzheimer's Therapeutic Research Institute; Alzheimer's AssociationRecruitingAlzheimer Disease | Mild Cognitive Impairment | Early Onset Alzheimer DiseaseUnited States
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UCB Biopharma SRLTerminatedDrug-Resistant Epilepsy | Focal-Onset SeizuresUnited States, Australia, Belgium, Bosnia and Herzegovina, Bulgaria, Croatia, Czechia, Denmark, Estonia, Finland, France, Germany, Greece, Hungary, Ireland, Italy, Japan, Norway, Poland, Portugal, Romania, Serbia, Slovakia, Spain, Sweden, Switzerlan... and more
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Memorial Sloan Kettering Cancer CenterActive, not recruitingChronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | Myeloproliferative Neoplasms | Atypical Chronic Myeloid Leukemia | Myelodysplastic/Myeloproliferative Overlapping SyndromeUnited States
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Astex Pharmaceuticals, Inc.CompletedAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic LeukemiaUnited States
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LLS PedAL Initiative, LLCNational Cancer Institute (NCI); Children's Oncology GroupRecruitingAcute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Myeloid Leukemia Associated With Down Syndrome | Mixed Phenotype Acute Leukemia | Acute Myeloid Leukemia Post Cytotoxic Therapy | Myelodysplastic Syndrome Post Cytotoxic TherapyUnited States, Canada, Australia, Puerto Rico, New Zealand
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Millennium Pharmaceuticals, Inc.CompletedMyelodysplastic Syndromes | Leukemia, Myeloid, Acute | Leukemia, Myelomonocytic, ChronicUnited States, Israel, Spain, France, Ireland, Canada, Germany, Czechia, Italy, Netherlands, Belgium, Bulgaria
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Seagen Inc.CompletedAcute Myeloid Leukemia | Myeloproliferative Disorders | Chronic Myelomonocytic Leukemia | Myelodysplastic SyndromeUnited States
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Genzyme, a Sanofi CompanyTerminatedGlycogenosis 2 | Glycogen Storage Disease Type II (GSD II) | Acid Maltase Deficiency | Pompe Disease (Infantile-Onset)United States, Taiwan, Germany
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Treadwell Therapeutics, IncRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic Leukemia | AML | MDS | CMMLHong Kong, United States, Canada
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Roswell Park Cancer InstituteCelldex TherapeuticsCompletedAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | High Risk Myelodysplastic Syndrome | Refractory Anemia | Blasts 30 Percent or Less of Bone Marrow Nucleated CellsUnited States
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Center for International Blood and Marrow Transplant...National Marrow Donor Program; Pediatric Blood and Marrow Transplant ConsortiumActive, not recruitingJuvenile Myelomonocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Myelodysplasia | Acute Lymphoblastic Leukemia/LymphomaUnited States
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H. Lee Moffitt Cancer Center and Research InstituteAprea TherapeuticsCompletedAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | Myeloproliferative NeoplasmUnited States
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Dompé Farmaceutici S.p.AActive, not recruitingNew-onset type1 DiabetesUnited States, Belgium, Georgia, Germany, Italy, Serbia, Israel, Slovenia
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
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Growing Spine Study GroupGrowing Spine FoundationCompletedEarly Onset Scoliosis | Thoracic Insufficiency Syndrome | Congenital Spinal Deformities | Infantile Idiopathic Scoliosis | Neuromuscular Spinal Deformity | Syndromic Spinal DeformityUnited States, Canada, United Kingdom, Egypt, Ghana, Spain, Turkey
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National Cancer Institute (NCI)Children's Oncology GroupActive, not recruitingJuvenile Myelomonocytic Leukemia | Neurofibromatosis Type 1United States
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GAP Innovations, PBCCompletedAlzheimer Disease | Mild Cognitive Impairment | Alzheimer Disease, Early Onset | Memory Disorders | Memory Impairment | Memory LossUnited States
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EMD SeronoCompletedPituitary Dwarfism | Childhood-onset Growth Hormone DeficiencyUnited States
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Merck Sharp & Dohme LLCTerminatedRelapsed or Refractory Acute Myeloid Leukemia | Relapsed or Refractory Chronic Myelomonocytic LeukemiaUnited States, Israel, Spain
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Stemline Therapeutics, Inc.CompletedMyelofibrosis | Chronic Myelomonocytic LeukemiaUnited States, Canada
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Heinrich-Heine University, DuesseldorfKoordinierungszentrum für Klinische Studien - DuesseldorfRecruitingMyelodysplastic Syndromes | Chronic Myelomonocytic Leukemia | Secondary Acute Myeloid LeukemiaGermany
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National Cancer Institute (NCI)CompletedAcute Myeloid Leukemia | High Risk Myelodysplastic Syndrome | Myeloproliferative Neoplasm | Chronic Myelomonocytic Leukemia-2United States
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Faron Pharmaceuticals LtdRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic Leukemia | Relapsed/Refractory AMLUnited States, Finland
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National Cancer Institute (NCI)CompletedAcute Myeloid Leukemia | Leukemia | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Secondary Acute Myeloid Leukemia | Myelodysplastic Syndrome | Secondary Myelodysplastic Syndrome | de Novo Myelodysplastic SyndromeUnited States
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Roswell Park Cancer InstituteCompletedAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | Alkylating Agent-Related Acute Myeloid Leukemia | Refractory Anemia With Excess Blasts in TransformationUnited States
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Onconova Therapeutics, Inc.The Leukemia and Lymphoma SocietyCompletedMyelodysplastic Syndromes | Chronic Myelomonocytic Leukemia | MDS | RAEBUnited States, Belgium, Germany, Spain, France, Italy
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Omar AljitawiRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Myelofibrosis | Chronic Myelomonocytic Leukemia | Myelodysplastic/Myeloproliferative Neoplasm | Atypical Chronic Myeloid Leukemia | Chronic Monocytic LeukemiaUnited States
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National Cancer Institute (NCI)CompletedAcute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome | Chronic Myelomonocytic Leukemia | Previously Treated Myelodysplastic Syndrome | Recurrent Adult Acute Myeloid Leukemia | Myelodysplastic Syndrome | Secondary Myelodysplastic SyndromeUnited States
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Astex Pharmaceuticals, Inc.Enrolling by invitationAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic LeukemiaUnited States, Spain, Canada, Austria, Slovakia, Bulgaria, Hungary
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PfizerCompletedAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Myelodysplastic SyndromeUnited States, United Kingdom, Belgium, Canada, Germany, France
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NextCure, Inc.RecruitingRelapsed or Refractory Acute Myeloid Leukemia | Relapsed or Refractory Chronic Myelomonocytic Leukemia | Relapsed or Refractory Myelodysplastic SyndromeUnited States
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Heinrich-Heine University, DuesseldorfCelgene Corporation; Koordinierungszentrum für Klinische Studien DüsseldorfActive, not recruitingMyelodysplastic Syndromes | Leukemia, Myeloid, Acute | Chronic Myelomonocytic Leukemia | IDH2 Gene Mutation | IDH2 R172 | IDH2 R140Germany
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Bristol-Myers SquibbCompletedDermatomyositis | Polymyositis | Autoimmune Necrotizing Myopathy | Overlap Myositis | Juvenile Myositis Above the Age of 18France, United States, Australia, Brazil, Czechia, Germany, Italy, Japan, Korea, Republic of, Mexico, Sweden
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TetraLogic PharmaceuticalsTerminatedChronic Myelomonocytic Leukemia (CMML) | Myelodysplastic Syndrome (MDS)United States, Spain, Australia, Germany
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedJuvenile Myelomonocytic Leukemia | Childhood Acute Myeloid Leukemia in Remission | Childhood Acute Lymphoblastic Leukemia in Remission | Childhood Chronic Myelogenous Leukemia | Childhood Myelodysplastic Syndromes | Chronic Phase Chronic Myelogenous Leukemia | Previously Treated Myelodysplastic... and other conditionsUnited States
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Onconova Therapeutics, Inc.CompletedAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Myelodysplastic SyndromeUnited States, France
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Genzyme, a Sanofi CompanyApproved for marketingGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe Disease (Late-Onset)United States
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National Cancer Institute (NCI)RecruitingChronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | Myelodysplastic Syndrome With Excess Blasts | Myeloproliferative NeoplasmUnited States, Canada
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National Cancer Institute (NCI)CompletedChronic Myelomonocytic Leukemia | Recurrent Disease | Atypical Chronic Myeloid Leukemia, BCR-ABL1 Negative | Chronic Myelogenous Leukemia, BCR-ABL1 Positive | Myelodysplastic/Myeloproliferative Neoplasm, Unclassifiable | Accelerated Phase of Disease | Chronic Phase of DiseaseUnited States
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Janssen Research & Development, LLCCompletedErythroblastosis, Fetal | Early Onset Severe Hemolytic Disease of the Fetus and Newborn (EOS-HDFN)United States, Canada, Netherlands, Belgium, Australia, Germany, Spain, Sweden, United Kingdom
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2United States, France, Netherlands
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease (Late-Onset) | Glycogenesis Type II | Acid Maltase Deficiency (AMD)United States, France, Canada, Netherlands, Australia
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Novartis PharmaceuticalsActive, not recruitingMyelodysplastic Syndromes | Leukemia, Myelomonocytic, ChronicChina, Czechia, Japan, Saudi Arabia, Taiwan, Turkey, Germany, Spain, Netherlands, Italy, Singapore, Australia, Austria, France, United Kingdom, Korea, Republic of, Thailand, Israel, Belgium, Canada, Switzerland, Lithuania, Russian Federation and more