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Clinical Trials on Lactic Acidemia in United Kingdom
Total 178 results
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Women and Infants Hospital of Rhode IslandFoundation for Society of Maternal-Fetal MedicineRecruiting
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Sheffield Teaching Hospitals NHS Foundation TrustCompleted
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HemoShear TherapeuticsPrometrika, LLC; AllStripes Research Inc.; Genome MedicalTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Canada, United Kingdom
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Recordati Rare DiseasesRecruitingPropionic Acidemia | Methylmalonic AcidemiaFrance, Spain, Italy, United Kingdom, Norway, Germany, Sweden
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ModernaTX, Inc.CompletedPropionic Acidemia | Methylmalonic AcidemiaUnited States, United Kingdom, Spain, France
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CoA Therapeutics, Inc., a BridgeBio companyTerminatedHealthy Volunteers | Propionic Acidemia | Methylmalonic Acidemia | Organic AcidemiaUnited States
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University of FloridaCompleted
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ModernaTX, Inc.RecruitingMethylmalonic AcidemiaUnited States, Spain, Canada, Netherlands, France, Australia, United Kingdom
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Target PharmaSolutions, Inc.Recordati Rare DiseasesEnrolling by invitationPropionic Acidemia | Methylmalonic Acidemia | HyperammonemiaUnited States
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National Institute of Environmental Health Sciences...Completed
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Recordati Rare DiseasesTarget PharmaSolutions, Inc.RecruitingPropionic Acidemia | Methylmalonic Acidemia | HyperammonemiaUnited States
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ModernaTX, Inc.RecruitingMethylmalonic AcidemiaUnited States, Canada, Netherlands, United Kingdom
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Oxford Brookes UniversityUniversity of OxfordCompletedPhysical Activity | Mental Health Wellness 1 | Cognitive Function 1, Social | Academic Attainment | Fitness TestingUnited Kingdom
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Canada, United Kingdom
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National Human Genome Research Institute (NHGRI)RecruitingPropionic Acidemia | Metabolic Disease | Organic AcidemiaUnited States
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University of FloridaNo longer availableMitochondrial Enzyme DeficienciesUnited States
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Mendel TuchmanUniversity of Colorado, Denver; Children's Hospital of Philadelphia; University... and other collaboratorsTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States
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National Human Genome Research Institute (NHGRI)RecruitingInborn Errors of Metabolism | Methylmalonic Acidemia | Organic AcidemiaUnited States
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Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)SuspendedMethylmalonic Acidemia (MMA)United States
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HemoShear TherapeuticsTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Saudi Arabia, Australia
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Glasgow Royal InfirmaryCompletedMagnesium Deficiency | Alcohol Withdrawal | Lactic Acidosis | Vitamin B1 Deficiency | Wernicke EncephalopathyUnited Kingdom
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.TerminatedMethylmalonic AcidemiaUnited States
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Duke UniversityWithdrawnHypoxia | Lactic AcidosisUnited States
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Canada, United Kingdom
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University Hospitals, LeicesterCompletedHip Fractures | Blood Lactic Acid IncreasedUnited Kingdom
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SangartWithdrawnTrauma | Hemorrhagic Shock | Lactic AcidosisNew Zealand, United Kingdom, Israel, France, Switzerland, Australia, Belgium, Brazil, Germany, Norway, South Africa
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University of California, San DiegoCompletedLactic AcidosisUnited States
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NHS Greater Glasgow and ClydeJean Brown Bequest Fund, GlasgowCompleted
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Uta Lichter-KoneckiMedical College of Wisconsin; Children's National Research InstituteCompletedUrea Cycle Disorders | Organic AcidemiasUnited States
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NHS Greater Glasgow and ClydeJean Brown Bequest Fund, Glasgow, UKNot yet recruitingTelemedicine | Surgery, PlasticUnited Kingdom
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn... and other collaboratorsCompletedMethylmalonic Acidemia | Carbamoyl-Phosphate Synthase I Deficiency Disease | Propionic Acidemia, Type I and/or Type II | Ornithine Carbamoyltransferase DeficiencyUnited States
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedAmino Acid Metabolism, Inborn ErrorsFrance, United Kingdom, Italy, Belgium, Germany, Switzerland
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Khondrion BVJulius Clinical; ProPharma Group; CertaraCompletedMitochondrial Diseases | Mitochondrial DNA tRNALeu(UUR) m.3243A<G Mutation | Maternally Inherited Diabetes and Deafness (MIDD) | Mitochondrial Encephalomyopathy, Lactic Acidosis and Stroke Like Episodes (MELAS) | Chronic Progressive External Ophthalmoplegia (CPEO)Netherlands, Denmark, United Kingdom, Germany
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Imperial College LondonCompletedPharmacokinetics | Penicillin Allergy | Beta Lactam Adverse ReactionUnited Kingdom
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Vapotherm, Inc.Auburn UniversityActive, not recruitingExercise | Recovery | Dyspnea | Breathlessness | Muscle | Lactic AcidosisUnited States
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Nicola LongoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National...Completed
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New York Institute of TechnologyCompleted
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SangartCompletedShock, Hemorrhagic | Acidosis, Lactic | Shock, TraumaticFrance, United Kingdom, South Africa, Germany
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Immune Oncology Research InstituteRecruitingBlastic Plasmacytoid Dendritic Cell Neoplasm (BPDCN)United States, Armenia, Canada, Egypt, Georgia, United Kingdom, Cyprus, Italy, Turkey, India, Iraq, Taiwan, Kuwait
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The Cleveland ClinicWithdrawnSeptic Shock | Shock, Septic | Lactic Acidosis | Thiamine DeficiencyUnited States
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University of WashingtonInstitute of Education SciencesUnknownEmotional/Behavioral Function | Academic PerformanceUnited States
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Tisento TherapeuticsNot yet recruitingMitochondrial Encephalopathy, Lactic Acidosis and Stroke-Like Episodes (MELAS Syndrome)United States, Australia, Italy, Germany, Canada, United Kingdom
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Spain, Netherlands, France, United Kingdom, Australia, Canada, Italy
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Beth Israel Deaconess Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)TerminatedShock | Cardiac Arrest | Lactic Acidosis | Thiamin DeficiencyUnited States
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Wellstat TherapeuticsCompletedHereditary Orotic AciduriaUnited States
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Vitaflo International, LtdRecruitingPhenylketonurias | PKU | Maple Syrup Urine Disease | Homocystinuria | Glutaric Acidemia I | Hereditary TyrosinemiaUnited Kingdom
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingBlastic Plasmacytoid Dendritic Cell NeoplasmUnited States
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Dana-Farber Cancer InstituteAbbVieActive, not recruitingBlastic Plasmacytoid Dendritic Cell NeoplasmUnited States
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SangartCompletedShock, Hemorrhagic | Acidosis, Lactic | Shock, TraumaticNorway, Singapore, Israel, France, United Kingdom, Germany, Switzerland, Australia, Brazil, South Africa, New Zealand, Colombia, Austria, Spain