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Clinical Trials on Leber Congenital Amaurosis in Australia
Total 255 results
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Children's Hospital Medical Center, CincinnatiUniversity of Pittsburgh; Vanderbilt University Medical Center; Children's Hospital... and other collaboratorsNot yet recruitingDepression, Postpartum | Neurodevelopmental Disorders | Heart Defects, Congenital | Trauma, Psychological | Anxiety in PregnancyUnited States, Australia
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ActelionCompletedPulmonary Arterial Hypertension Related to Eisenmenger PhysiologyCanada, United Kingdom, Italy, United States, Netherlands, Australia, Austria, Belgium, France, Germany, Spain
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ShireCompletedDystrophic Epidermolysis BullosaUnited States, Czechia, Italy, Austria, Australia, France, Germany
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Kirby InstituteNational Heart, Lung, and Blood Institute (NHLBI); St Vincent's Hospital, Sydney and other collaboratorsCompletedGlucose Metabolism Disorders | Metabolic Diseases | HIV Infections | Cardiovascular Disease | Dyslipidemias | LipodystrophyAustralia
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Philip MoonsCompletedHeart Defects, CongenitalNorway, Taiwan, Belgium, Netherlands, United States, Sweden, Switzerland, Canada, Argentina, Australia, France, India, Italy, Japan, Malta
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PYC TherapeuticsRecruitingOptic Atrophies, Hereditary | Autosomal Dominant Optic Atrophy | Optic Atrophy, Autosomal Dominant | Kjer Optic AtrophyAustralia
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Cardiac Regeneration Technologies, LLCUnknownReduced Left Ventricular Function Defined as LVEF < 50% | Regional Left Ventricular Wall Motion AbnormalitiesAustria
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Garvan Institute of Medical ResearchCompletedPrader-Willi SyndromeAustralia
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Zimmer BiometActive, not recruitingAvascular Necrosis | Inflammatory Arthritis | Osteoarthritis, Hip | Congenital Hip Dysplasia | Post-traumatic; Arthrosis | Rheumatoid Arthritis With Adequate Bone QualityNetherlands, Finland, Belgium, France, Spain, Australia, Canada, United Kingdom
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University of ZurichActive, not recruitingTransposition of Great VesselsSpain, Switzerland, Austria, Netherlands, France
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Basal Cell CarcinomaAustralia
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Medacta International SARecruitingArthrosis | Congenital Hip Dysplasia | Traumatic Arthritis | Rheumatoid Polyarthritis | Avascular Necrosis of the Femoral HeadAustria, Italy, Switzerland, United Kingdom
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ActelionCompletedClinical Study Assessing the Efficacy and Safety of Macitentan in Fontan-palliated Subjects (RUBATO)Congenital Heart DiseaseUnited States, United Kingdom, Taiwan, Germany, France, Poland, China, Australia, Czechia, Canada, Denmark, New Zealand
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Zynerba Pharmaceuticals, Inc.Completed22Q Deletion SyndromeUnited States, Australia
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KU LeuvenCompletedCongenital Heart DiseaseBotswana, United States, Korea, Republic of, Belgium, Sweden, France, Switzerland, Denmark, Pakistan, Norway, Taiwan, Malta, Brazil, Bulgaria, India, Austria, Argentina, Australia, Cameroon, Canada, Chile, Colombia, Ethiopia, Greece, Italy and more
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The University of QueenslandRecruitingAutosomal Dominant Polycystic Kidney DiseaseAustralia
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Murdoch Childrens Research InstituteNational Health and Medical Research Council, Australia; Royal Children's Hospital and other collaboratorsRecruitingCommunicable Diseases | Quality of Life | Inflammation | Obesity | Congenital Abnormalities | Genetics | Healthy Aging | Child Development | Diet | Mental Health | Disability | Injuries | Cognition | Child Health | Environmental Exposure | Noncommunicable Diseases | Physical Fitness | Intergenerational Relations | Social Determinants... and other conditionsAustralia
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Sydney Local Health DistrictEnrolling by invitationClass III Malocclusion | UnderbiteAustralia
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RHEACELL GmbH & Co. KGRecruiting
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Eloxx Pharmaceuticals, Inc.Recruiting
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Medical University InnsbruckCompletedPectus Excavatum | Pectus CarinatumAustria
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Paragonix TechnologiesEnrolling by invitationHeart Diseases | Heart Failure | Heart Defects, CongenitalUnited States, Spain, Austria, United Kingdom
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Holostem Terapie Avanzate s.r.l.Paracelsus Medical UniversityTerminated
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Neuren Pharmaceuticals LimitedRecruiting
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormone Deficiency | Turner SyndromeArgentina, Australia, Austria, Canada, France, Germany, Italy, Norway, Russian Federation, Singapore, Spain, Sweden, United Kingdom
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Medical University of GrazRecruitingMissing ToothAustria
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University Hospital FreiburgCompletedMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond SyndromeSpain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
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Nacuity Pharmaceuticals, Inc.Foundation Fighting BlindnessActive, not recruitingUsher SyndromesAustralia
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Paracelsus Medical UniversityMedAlliance Swiss Medical TechnologyActive, not recruiting
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University of ZurichCompleted
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Murdoch Childrens Research InstituteRoyal Children's Hospital; Peter MacCallum Cancer Centre, AustraliaNot yet recruitingArteriovenous Malformations | Vascular Malformations | MAP2K1 Gene Mutation | PIK3CA-related Overgrowth Spectrum | Vascular Anomalies | Lymphangioma | Lymphatic Malformation | KRAS G12D | Venous Malformation | Vascular Anomaly | KRAS G12C | PI3K Gene Mutation | Slow-Flow Vascular Malformation | Fast-Flow Vascular... and other conditionsAustralia
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic Neuropathy (LHON)Italy, Germany, France, Austria, Greece, Netherlands
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DePuy InternationalTerminatedOsteoarthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Traumatic Femoral Fractures | Nonunion of Femoral Fractures | Perthes DiseaseAustria, Germany, Italy
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Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
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Queen Silvia Children's Hospital, Gothenburg, SwedenSahlgrenska University Hospital, Sweden; Swedish Heart Lung FoundationRecruitingAortic Valve Stenosis | Congenital Heart Disease | Hypoplastic Left Heart Syndrome | Fetal Cardiac DisorderUnited States, Austria, Canada, Finland, Germany, Poland, Spain, Sweden
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic Neuropathy (LHON)United States, United Kingdom, Spain, Poland, Austria, Belgium, Bulgaria, Germany, Italy, Portugal
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bluebird bioCompletedβ-thalassemia MajorUnited States, Australia, Thailand
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Cyathus Exquirere PharmaforschungsgmbhTerminated
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Holostem Terapie Avanzate s.r.l.Paracelsus Medical UniversityTerminatedRecessive Dystrophic Epidermolysis BullosaAustria
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Novartis PharmaceuticalsCompletedThalassemia, Non-transfusional-dependent Thalassemia (NTDT), Myeloplastic Dysplasia (MDS), Other AnemiaAustralia
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CelgeneCompletedMyelodysplastic Syndromes | Beta-thalassemiaAustria
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Mirum Pharmaceuticals, Inc.CompletedAlagille SyndromeFrance, Belgium, Poland, Australia, Spain, United Kingdom
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Medical University InnsbruckNot yet recruitingAnogenital Human Papillomavirus Infection | Condyloma AnalAustria
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AO Foundation, AO SpineCompletedSpinal DeformityUnited States, Turkey, Hong Kong, United Kingdom, China, Australia, Netherlands, Canada, Japan, Brazil, India, Israel, Pakistan, Spain
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FerroKin BioSciences, Inc.CompletedBeta-thalassemia | Transfusional Iron OverloadUnited States, Australia, Thailand
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Ionis Pharmaceuticals, Inc.TerminatedBeta Thalassemia IntermediaAustralia, Thailand, Greece, Lebanon, Turkey
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Prof. Johann BauerRecruiting
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TWi Biotechnology, Inc.RecruitingGeneralized Epidermolysis Bullosa SimplexUnited States, Taiwan, Australia, Philippines, Austria, Italy, Poland
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QED Therapeutics, Inc.RecruitingHypochondroplasiaUnited States, Australia, Norway, Portugal, Singapore, Spain