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Clinical Trials on Leber Congenital Amaurosis in South Africa
Total 327 results
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Medical University of South CarolinaCompleted
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Abbott Medical DevicesCompletedPatent Ductus Arteriosus (PDA)United States
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Glycomine, Inc.Recruiting24-Week Study to Assess the PD, Safety, Tolerability, and PK of GLM101 in Participants With PMM2-CDGPmm2-CDGSpain, Australia, United States
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Otto Bock Healthcare Products GmbHHanger Clinic: Prosthetics & OrthoticsActive, not recruitingLower Limb Amputation Above Knee (Injury) | Lower Limb Amputation Knee | Congenital Amputation of Lower LimbUnited States
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VentureMed Group Inc.RecruitingArterial Occlusive Diseases | Fistula | Arteriovenous Fistula | Arteriovenous GraftUnited States
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Children's Hospital Medical Center, CincinnatiRecruitingHypoplastic Left Heart Syndrome (HLHS)United States, United Kingdom, Canada
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Western Sydney Local Health DistrictRecruitingVentricular Tachycardia | Cardiomyopathy, Dilated | Heart Disease Structural Disorder | Sarcoidosis | Cardiomyopathy, Hypertrophic | Cardiomyopathy, Familial | Cardiomyopathy Ischemic | Arrhythmogenic Right Ventricular Cardiomyopathy 1 | Arrhythmogenic Left Ventricular CardiomyopathyAustralia
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La Jolla Pharmaceutical CompanyTerminatedBeta-ThalassemiaAustralia, Thailand, United States, Greece, Italy, Lebanon, Turkey, United Kingdom
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Intact Medical CorporationCompleted
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BayerCompletedContraception | Neural Tube Defects | Oral Contraceptives (OC)United States
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Mezzion Pharma Co. LtdRecruitingSingle Ventricle Heart DiseaseUnited States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); FDA Office of Orphan Products... and other collaboratorsCompletedMarfan SyndromeUnited States, Canada, Belgium
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Mezzion Pharma Co. LtdNational Heart, Lung, and Blood Institute (NHLBI)UnknownFunctional Single Ventricle Heart DiseaseUnited States, Korea, Republic of, Canada
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University of California, San DiegoBaylor College of Medicine; Boston Children's Hospital; Rare Diseases Clinical... and other collaboratorsCompletedNervous System Diseases | Angelman SyndromeUnited States
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Mirum Pharmaceuticals, Inc.CompletedAlagille SyndromeFrance, Belgium, Poland, Australia, Spain, United Kingdom
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Tenax Therapeutics, Inc.Active, not recruitingHeart Failure With Normal Ejection Fraction | Hypertension Pulmonary Secondary Heart Failure | Right Sided Heart Failure With Normal Ejection FractionUnited States
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Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
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Mayne Pharma International Pty LtdTerminatedLamellar IchthyosisUnited States, Spain, Canada, Germany, France, Australia, Israel, Ukraine, United Kingdom
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Hoffmann-La RocheRecruitingSickle Cell DiseaseUnited States, Spain, Brazil, United Kingdom, Italy, Turkey, Kenya, Netherlands, France, South Africa, Lebanon
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atHeart MedicalRecruitingHeart Diseases | Cardiovascular Diseases | Congenital Abnormalities | Heart Septal Defects, Atrial | Heart Defects, Congenital | Cardiovascular Abnormalities | Heart Septal DefectUnited States, France
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The University of QueenslandRecruitingAutosomal Dominant Polycystic Kidney DiseaseAustralia
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Timber Pharmaceuticals Inc.Active, not recruitingIchthyosisUnited States, Canada, Germany, France, Italy
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ActelionCanadian Heart Research CentreCompleted
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Mezzion Pharma Co. LtdNational Heart, Lung, and Blood Institute (NHLBI)CompletedSingle Ventricle Heart DiseaseUnited States, Korea, Republic of, Canada
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); University of Memphis; RTI...CompletedSickle Cell DiseaseUnited States
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Albert ParkGenentech, Inc.; National Institute on Deafness and Other Communication Disorders...Active, not recruitingCmv Congenital | CMV | Congenital Cmv | SNHL | Sensorineural Hearing LossUnited States
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Boston Children's HospitalBaylor College of Medicine; Vanderbilt University Medical Center; Children's... and other collaboratorsCompleted
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Novartis PharmaceuticalsCompletedThalassemia, Non-transfusional-dependent Thalassemia (NTDT), Myeloplastic Dysplasia (MDS), Other AnemiaAustralia
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W.L.Gore & AssociatesActive, not recruitingMigraine | Patent Foramen Ovale | PFO - Patent Foramen OvaleUnited States
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Abbott Medical DevicesCompletedAtrial Septal DefectUnited States
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Boston Children's HospitalChildren's Hospital Colorado; Cedars-Sinai Medical Center; Hospital for Special... and other collaboratorsRecruitingAdolescent Idiopathic Scoliosis | Idiopathic Scoliosis | Spondylolisthesis | Spine Deformity | Neuromuscular Scoliosis | Congenital ScoliosisUnited States
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Abbott Medical DevicesRecruitingStroke | Patent Foramen OvaleUnited States, Germany, Canada, Switzerland, Italy, Portugal, United Kingdom
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Wen-Hann TanBaylor College of Medicine; University of California, San Francisco; Vanderbilt... and other collaboratorsCompleted
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VentureMed Group Inc.CompletedArteriovenous Fistula StenosisUnited States
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National Institute of Allergy and Infectious Diseases...Completed
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SanofiTerminatedCongenital Cystic Kidney DiseaseGermany, Spain, United States, Australia, Belgium, Japan, Korea, Republic of, Netherlands
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Novo Nordisk A/SRecruitingSickle Cell DiseaseSpain, United States, United Kingdom, Canada, Italy, India, Turkey, Greece, South Africa, France, Lebanon, Oman
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Canada, Brazil, Taiwan, Singapore, South Africa, United Kingdom
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ArQule, Inc. (a wholly owned subsidiary of Merck...Worldwide Clinical TrialsTerminatedPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus SyndromeUnited States, Australia, Italy, Spain
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Imara, Inc.CompletedSickle Cell DiseaseUnited States, United Kingdom
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Duke UniversityNational Heart, Lung, and Blood Institute (NHLBI); RTI InternationalCompletedHematologic Diseases | Sickle Cell Disease | Anemia, Sickle Cell | Genetic DiseaseUnited States
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Abbott Medical DevicesActive, not recruitingVentricular Septal DefectsUnited States, Canada
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Novartis PharmaceuticalsActive, not recruitingSickle Cell Disease (SCD)United States, United Kingdom, Germany, Spain, Greece, Italy, Brazil, Lebanon, Turkey, Belgium, France, Jordan, India, Finland, Canada, Colombia, Netherlands, Oman, South Africa, Panama, Ghana
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Women and Infants Hospital of Rhode IslandPerkinElmer, Inc.CompletedDown Syndrome | Trisomy 18 | Trisomy 13United States, Canada, Italy
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SCAD AlliancePERFUSE Study GroupRecruitingSpontaneous Coronary Artery DissectionUnited States, Australia
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Castle Creek Pharmaceuticals, LLCTerminatedEpidermolysis Bullosa SimplexUnited States, Israel, Australia, Austria, France, Germany, Netherlands, United Kingdom
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Micelle BioPharma IncUnknownSickle Cell DiseaseUnited States
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Hoffmann-La RocheRecruitingAngelman SyndromeUnited States, Australia, Spain, Italy, France, Germany
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Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Switzerland, Netherlands, Portugal
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Merck Sharp & Dohme LLCActive, not recruitingPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)United States, Australia, Brazil, Italy, United Kingdom