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Clinical Trials on Leber Congenital Amaurosis in United States
Total 3894 results
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University of PennsylvaniaNational Eye Institute (NEI)Active, not recruitingRetinal Diseases | Amaurosis of LeberUnited States
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ProQR TherapeuticsTerminatedEye Diseases | Neurologic Manifestations | Eye Diseases, Hereditary | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Belgium
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ProQR TherapeuticsActive, not recruitingEye Diseases | Neurologic Manifestations | Eye Diseases, Hereditary | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Belgium, Brazil, Canada, France, Germany, Italy, Netherlands, United Kingdom
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QLT Inc.CompletedLCA (Leber Congenital Amaurosis) | RP (Retinitis Pigmentosa)Canada, United States, Germany, Netherlands, United Kingdom
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QLT Inc.CompletedLCA (Leber Congenital Amaurosis) | RP (Retinitis Pigmentosa)United States, Canada, Germany, Netherlands, United Kingdom
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MeiraGTx UK II LtdSyne Qua Non LimitedCompletedEye Diseases | Retinal Diseases | Eye Diseases, Hereditary | Leber Congenital Amaurosis (LCA)United States, United Kingdom
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ProQR TherapeuticsCompletedLeber's Congenital AmaurosisUnited States, Belgium
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QLT Inc.CompletedLeber Congenital Amaurosis (LCA) | Retinitis Pigmentosa (RP)United States, Canada, Denmark, Germany, Netherlands, Switzerland, United Kingdom
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ProQR TherapeuticsRecruitingEye Diseases | Neurologic Manifestations | Retinal Degeneration | Retinal Dystrophies | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalBelgium, Brazil, Canada, Germany, Italy, Netherlands, United Kingdom
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Editas Medicine, Inc.Active, not recruitingRetinal Degeneration | Eye Diseases, Hereditary | Vision Disorders | Leber Congenital Amaurosis 10 | Inherited Retinal Dystrophies | Retinal Disease | Eye Disorders CongenitalUnited States
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Editas Medicine, Inc.CompletedEye Diseases | Retinal Degeneration | Eye Diseases, Hereditary | Vision Disorders | Blindness | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Netherlands, France, Germany
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Spark TherapeuticsActive, not recruitingLeber Congenital AmaurosisUnited States
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MeiraGTx UK II LtdCompletedNatural History Study of Patients With Leber Congenital Amaurosis Associated With Mutations in RPE65Leber Congenital AmaurosisUnited Kingdom, United States
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Spark TherapeuticsCompleted
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Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, WorcesterCompletedLeber Congenital AmaurosisUnited States
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MeiraGTx UK II LtdCompletedLeber Congenital AmaurosisUnited Kingdom, United States
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Atsena Therapeutics Inc.Active, not recruitingLeber Congenital Amaurosis | LCA | LCA1United States
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University College, LondonMoorfields Eye Hospital NHS Foundation Trust; Targeted Genetics CorporationCompletedRetinal DegenerationUnited Kingdom
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HuidaGene Therapeutics Co., Ltd.Cholgene Therapeutics, Inc.RecruitingLeber Congenital Amaurosis | Inherited Retinal Diseases Caused by RPE65 MutationsUnited States, China
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OcugenRecruitingRetinitis Pigmentosa | Leber Congenital AmaurosisUnited States
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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Qlaris Bio, Inc.CompletedOcular Hypertension | Glaucoma | Glaucoma Congenital | Sturge-Weber Syndrome (SWS)United States
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Abbott Medical DevicesCompletedCarotid Artery Stenting Outcomes in the Standard Risk Population for Carotid Endarterectomy (CANOPY)Stroke | Carotid Artery Disease | Amaurosis Fugax | Transient Ischemic Attack (TIA)United States
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Johns Hopkins UniversityVascular Birthmarks FoundationCompletedEpilepsy | Sturge Weber SyndromeUnited States
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Wills EyeUniversity of Medicine and Dentistry of New JerseyTerminatedSturge Weber Syndrome | Port-wine MarkUnited States
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Baylor College of MedicineNovartis PharmaceuticalsWithdrawnSturge Weber SyndromeUnited States
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University of California, IrvineMainz UniversityCompletedSturge - Weber Syndrome (SWS)United States
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Neurophth Therapeutics IncRecruitingLeber Hereditary Optic Neuropathy (LHON)China, United States
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, United Kingdom, Germany
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Anne Comi, MDJazz Pharmaceuticals; Faneca 66 FoundationCompletedSturge-Weber SyndromeUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...National Institute of Neurological Disorders and Stroke (NINDS); National Institutes... and other collaboratorsCompleted
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Neurophth Therapeutics IncActive, not recruitingLeber Hereditary Optic Neuropathy (LHON)United States
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National Human Genome Research Institute (NHGRI)CompletedTelangiectasia, Hereditary Hemorrhagic | Osler-Rendu-Weber Disease | Osler-Rendu DiseaseUnited States
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, Spain, United Kingdom
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Anne Comi, MDJazz Pharmaceuticals; Faneca 66 FoundationCompletedSturge-Weber SyndromeUnited States
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Wayne State UniversityNational Institutes of Health (NIH)Recruiting
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GenSight BiologicsActive, not recruitingLeber Hereditary Optic NeuropathyBelgium, Spain, United States, France, United Kingdom, Taiwan, Italy
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GenSight BiologicsCompletedOptic, Atrophy, Hereditary, LeberUnited Kingdom, United States, France, Germany, Italy
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AdvanceCor GmbHCompletedStroke | Atherosclerosis | Carotid Stenosis | TIA | Transient-ischaemic Attack | Amaurosis FugaxGermany, United Kingdom
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Qlaris Bio, Inc.CompletedOcular Hypertension | Glaucoma | Sturge-Weber SyndromeUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...Baylor College of Medicine; New York University; National Institute of Neurological... and other collaboratorsActive, not recruitingSturge-Weber SyndromeUnited States
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GenSight BiologicsCompletedOptic, Atrophy, Hereditary, LeberUnited Kingdom, United States, Germany, Italy, France
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University of Illinois at ChicagoWayne State University; Boston Children's Hospital; Duke University; University... and other collaboratorsRecruitingSturge-Weber SyndromeUnited States
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Anne Comi, MDPfizer; National Institute of Neurological Disorders and Stroke (NINDS); National... and other collaboratorsCompletedSturge-Weber SyndromeUnited States
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University of California, Los AngelesUniversité de MontréalWithdrawnStroke | Epilepsy | Tuberous Sclerosis | Sturge-Weber Syndrome | Focal Cortical Dysplasia | Hemimegalencephaly | Polymicrogyria | Rasmussen Encephalitis | Gliosis | Tumor, BrainUnited States, Canada
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Children's Hospital Medical Center, CincinnatiLymphangiomatosis and Gorham's Disease Alliance (LGDA); Klippel Trenaunay (KT)... and other collaboratorsRecruitingKaposiform Hemangioendothelioma | Kaposiform Lymphangiomatosis | Vascular Anomaly | Klippel Trenaunay Syndrome | Generalized Lymphatic Anomaly | Gorham-Stout Disease | Congenital Lipomatous Overgrowth, Vascular Malformations, and Epidermal NeviUnited States
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Randy KardonRecruitingLeber Hereditary Optic Neuropathy | Ischemic Optic Neuropathy | Hemianopia | Branch Retinal Artery Occlusion | Acute Zonal Occult Outer RetinopathyUnited States
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Vanderbilt University Medical CenterEnrolling by invitationCongenital Heart Disease | Congenital Heart Defect | Congenital Heart MalformationsUnited States
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UConn HealthRecruitingAplasia Cutis CongenitaUnited States
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Mayo ClinicCompletedHemangioma | Arteriovenous Malformations | Vascular Malformations | Lymphatic Malformation | Venous Malformation | Vascular Anomaly | Klippel Trenaunay SyndromeUnited States