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Clinical Trials on MPS - Mucopolysaccharidosis
Total 806 results
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ArmaGen, IncCompletedMucopolysaccharidosis IUnited States
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Ultragenyx Pharmaceutical IncCompleted
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Joyce FoxUltragenyx Pharmaceutical IncNo longer availableMucopolysaccharidosis Type 7United States
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National MPS SocietyMediResource Inc.TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidoses | Mucopolysaccharidosis VI | Mucopolysaccharidosis IVUnited States
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ArmaGen, IncCompletedMucopolysaccharidosis IBrazil
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Nadia Ali, PhDBioMarin PharmaceuticalCompletedMorquio A Syndrome | Mucopolysaccharidosis IV AUnited States
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Lundquist Institute for Biomedical Innovation at...Active, not recruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis I | Hurler SyndromeUnited States
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Lundquist Institute for Biomedical Innovation at...TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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Institut National de la Santé Et de la Recherche...RecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multiple Sulfatase Deficiency Disease | Mucopolysaccharidosis IXFrance
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Lundquist Institute for Biomedical Innovation at...Not yet recruitingMucopolysaccharidosis III | Sanfilippo SyndromeUnited States
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis VI | Maroteaux-Lamy SyndromeUnited States, Portugal, France
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IIJapan
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JCR Pharmaceuticals Co., Ltd.Completed
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Birmingham Women's and Children's NHS Foundation...BioMarin PharmaceuticalWithdrawnMucopolysaccharidosis IV | Morquio A DiseaseUnited Kingdom
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudNot yet recruitingSanfilippo Syndrome Type CUnited States, France
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agnes chenUniversity of California, Los Angeles; National Institute of Neurological Disorders... and other collaboratorsTerminatedMucopolysaccharidosis I | Cognitive DeclineUnited States
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler Syndrome | Hurler-Scheie SyndromeNetherlands, France, Germany, United Kingdom
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis IIUnited States, Spain, United Kingdom, Czechia, France, Canada, Italy, Belgium, Netherlands, Germany, Argentina, Sweden, Turkey, Brazil, Colombia
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AO GENERIUMCompletedA Multi-cohort Study of the Tolerance, Safety, and Pharmacokinetics of GNR-055 in Healthy VolunteersMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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Nadia Ali, PhDBioMarin PharmaceuticalCompletedMucopolysaccharidosis IV | Morquio DiseaseUnited States
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AO GENERIUMRecruitingMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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Denali Therapeutics Inc.Enrolling by invitationMucopolysaccharidosis IIUnited States, Canada, Belgium, Czechia, Netherlands
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JCR Pharmaceuticals Co., Ltd.Enrolling by invitationMucopolysaccharidosis IIUnited States
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REGENXBIO Inc.CompletedMucopolysaccharidosis IIBrazil, United States, United Kingdom
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ShireCompletedSanfilippo Syndrome Type BUnited States, United Kingdom, Germany
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis IVA (Morquio A Syndrome)Australia
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler Syndrome | Hurler-Scheie SyndromeJapan
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University of LeipzigDeutsche Krebshilfe e.V., Bonn (Germany)RecruitingMDS | MDS/MPNGermany, Austria
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Hurler's Syndrome | Hurler-Scheie Syndrome | Scheie's SyndromeUnited States
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Hurler-Scheie Syndrome | Hurlers SyndromeUnited States, Canada, Germany
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCTerminatedMucopolysaccharidosis I | Hurler's Syndrome | Hurler-Scheie Syndrome | ScheieItaly
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler's Syndrome | Hurler-Scheie SyndromeUnited States, Canada, United Kingdom, Brazil, Germany, Italy, Netherlands
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler's Syndrome | Hurler-Scheie SyndromeBrazil, Canada
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Patricia I. Dickson, M.D.University of California, Los Angeles; FDA Office of Orphan Products Development and other collaboratorsTerminatedMucopolysaccharidosis I | Lysosomal Storage Diseases | Spinal Cord CompressionUnited States, Finland
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Assiut UniversityUnknown
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Tehran University of Medical SciencesUnknownMucopolysaccharidosisIran, Islamic Republic of
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
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Michael SavonaIncyte Corporation; Astex Pharmaceuticals, Inc.; TheradexRecruiting
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Manchester University NHS Foundation TrustOrchard TherapeuticsRecruitingMucopolysaccharidosesUnited Kingdom
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Hacettepe UniversityCompletedMucopolysaccharidosesTurkey
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Mackay Memorial HospitalBioMarin PharmaceuticalUnknown
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Shrouk Shaban BakrRecruiting
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis I | Mucopolysaccharidosis VI | Mannosidosis | Mucolipidosis Type II (I-cell Disease)United States
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Hasan Kalyoncu UniversityCompleted
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Manchester University NHS Foundation TrustCompletedMucopolysaccharidosis Type IIUnited Kingdom
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedHurler Syndrome | Sanfilippo Syndrome Type A | Sanfilippo Syndrome Type BUnited States
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Manchester Royal Eye HospitalBioMarin PharmaceuticalUnknownMucopolysaccharidosesUnited Kingdom
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The First Affiliated Hospital with Nanjing Medical...Jiangbin Hospital Affiliated to Jiangsu University; Nanjing Second Hospital; Jiangning...Recruiting
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DKMS gemeinnützige GmbHRecruitingAML | MDS | Peripheral Blood Stem Cell Transplantation | Graft Vs Host Disease | CMML | MDS/MPNGermany