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Clinical Trials on MPS IIIB (Sanfilippo Syndrome)
Total 496 results
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVATaiwan, United States, Italy, United Kingdom
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Your Super, INC.CitruslabsCompletedMenstrual Pain | PMS | Menstrual DiscomfortUnited States
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Targazyme, Inc.UnknownLymphoma | Leukemia | Hodgkin's Lymphoma | Transplantation Infection | Myelodysplastic Syndrome (MDS) | Non-Hodgkin's Lymphoma (NHL) | Blood And Marrow TransplantationUnited States
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Memorial Sloan Kettering Cancer CenterRecruitingNon-Hodgkin's Lymphoma | Myelodysplastic Syndromes (MDS) | Acute Lymphoblastic Leukemia (ALL) | Myeloproliferative Disorder | Acute Myelogenous Leukemia (AML) | Chronic Myelogenous Leukemia (CML)United States
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medac GmbHSyneos Health; CelerionCompletedMyelodysplastic Syndromes (MDS) | Acute Lymphoblastic Leukaemias (ALL) | Acute Myeloid Leukaemias (AML) | Juvenile Myelomonocytic Leukaemias (JMML)Germany, United Kingdom, Italy, Austria, Czechia, Poland
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Groupe Francophone des MyelodysplasiesAstex Pharmaceuticals, Inc.Completed
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Joanne Kurtzberg, MDAldagenCompletedAnemia, Aplastic | MDS | Inborn Errors of Metabolism | Congenital Marrow Failure | Congenital Immunodeficiency SyndromeUnited States
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited Kingdom, United States, Germany
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St. Jude Children's Research HospitalKaryopharm Therapeutics IncCompletedAcute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS) | Mixed Phenotype Acute Leukemia (MPAL)United States
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Masonic Cancer Center, University of MinnesotaCompletedLymphoma | Chronic Lymphocytic Leukemia (CLL) | Myelodysplastic Syndromes (MDS) | Myeloma | Acute Lymphoblastic Leukemia (ALL) | Acute Myelogenous Leukemia (AML) | Chronic Myelogenous Leukemia (CML)United States
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IV AUnited States, Canada, France, Taiwan, Argentina, Colombia, Spain, Turkey, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, United Kingdom, Germany, Norway, Portugal, Italy, Qatar
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GeNeuro Innovation SASCompletedMultiple Sclerosis (MS) | Clinically Isolated Syndrome (CIS) | Secondary Progressive MS | Primary Progressive MS | Relapsing-Remitting MSFrance, Spain, Switzerland
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Ultragenyx Pharmaceutical IncAvailableSly Syndrome | Mucopolysaccharidosis VII | MPS VII
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AllerganRecruitingInterstitial Cystitis/Bladder Pain Syndrome (IC/BPS)United States, Canada
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Calliditas Therapeutics ABCompletedPost Polio Syndrome, PPSSweden
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Roncarolo, Maria Grazia, MDNational Cancer Institute (NCI)RecruitingHodgkin's Lymphoma | MDS (Myelodysplastic Syndrome) | ALL | Mixed Phenotype Acute Leukemia | AML - Acute Myeloid Leukemia | NHL - Non-Hodgkin's LymphomaUnited States
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NovartisCompletedMyelodysplastic Syndromes | Hemoglobinopathies | Diamond-Blackfan Anemia | Transfusional Iron Overload | Other Inherited or Acquired Anaemia | MPD Syndrome | Other Rare AnaemiasAustralia
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BioMarin PharmaceuticalCompletedMPS IV AUnited States, Canada, France, United Kingdom, Taiwan, Argentina, Colombia, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, Germany, Portugal, Italy, Qatar
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS) | Chronic Myeloid Leukemia (CML)United States
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National Cancer Institute (NCI)CompletedUterine Carcinosarcoma | Recurrent Fallopian Tube Carcinoma | Recurrent Ovarian Carcinoma | Recurrent Primary Peritoneal Carcinoma | Recurrent Uterine Corpus Carcinoma | Ovarian Endometrioid Adenocarcinoma | Ovarian Seromucinous Carcinoma | Endometrial Serous Adenocarcinoma | Lung Carcinoid Tumor | Metastatic... and other conditionsUnited States, Canada
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Treadwell Therapeutics, IncRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic Leukemia | AML | MDS | CMMLHong Kong, United States, Canada
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Van Andel Research InstituteCompletedAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic Leukemia | AML | MDS | CMMLUnited States
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National Institute of Mental Health (NIMH)TerminatedDepression | Premenstrual Dysphoric Disorder | Premenstrual Syndrome | PMS | PMDDUnited States
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome)United States, France, Australia, Germany, Ireland, Austria, Belgium, Italy, Lithuania, Netherlands, Portugal, Sweden, United Kingdom
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Children's National Research InstituteNational Institute of Allergy and Infectious Diseases (NIAID)Active, not recruitingCovid19 | SARS-CoV2 Infection | MIS-C Associated With COVID-19 | MIS-C Multisystem Inflammatory Syndrome in ChildrenUnited States
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medac GmbHSynteract, Inc.RecruitingMyelodysplastic Syndrome (MDS) | Acute Myeloid Leukaemia (AML) | Allogeneic Hematopoietic Stem Cell Transplantation (HSCT)United States
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NexImmune Inc.Active, not recruitingAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)United States
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National Cancer Institute (NCI)RecruitingMDS | Immunodeficiency | GATA2United States
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National Cancer Institute (NCI)CompletedMDS | Immunodeficiency | GATA2United States
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Oregon Health and Science UniversityUniversity of Utah; BioMarin PharmaceuticalCompleted
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BioMarin PharmaceuticalApproved for marketingMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, Puerto Rico
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Sunnybrook Health Sciences CentreQueen's University; Ontario Molecular Pathology Research NetworkUnknownCardiovascular Diseases | Inflammation | MDSCanada
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National Heart, Lung, and Blood Institute (NHLBI)Children's National Research InstituteCompletedLymphoma, Non-Hodgkin | MDS (Myelodysplastic Syndrome) | Myeloproliferative Disorder | ALL (Acute B-Lymphoblastic Leukemia) | AML (Acute Myelogenous LeukemiaUnited States
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Jazz PharmaceuticalsCompletedAcute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS)United States
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Jazz PharmaceuticalsWithdrawnAcute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS)United States
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University of Kansas Medical CenterCompletedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Non-Hodgkins Lymphoma | Myelodysplastic Syndrome (MDS) | Hodgkins LymphomaUnited States
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Children's Hospital Medical Center, CincinnatiRecruitingLow Back Pain | Chronic Widespread Pain | Fibromyalgia | Complex Regional Pain Syndrome (CRPS) | Ehlers-Danlos Syndrome (EDS) | Amplified Musculoskeletal Pain Syndrome (AMPS)United States
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Emory UniversityBioMarin PharmaceuticalCompletedMPS - Mucopolysaccharidosis | Morquio DiseaseUnited States
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Memorial Sloan Kettering Cancer CenterPediatric Brain Tumor ConsortiumTerminatedFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML)United States
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National Institute of Allergy and Infectious Diseases...Autoimmunity Centers of Excellence; Clinical Trials in Organ Transplantation...CompletedSevere Acute Respiratory Syndrome Coronavirus 2 (SARS-CoV-2) | Coronavirus Disease 2019 (COVID-19) | Multisystem Inflammatory Syndrome in Children (MIS-C)United States
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Zachariah Michael DeFilippRegimmune CorporationActive, not recruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Hodgkin Lymphoma | Chronic Myelomonocytic Leukemia | Acute Lymphoblastic Leukemia | AML | Non Hodgkin Lymphoma | MDS | Myeloproliferative Disorder | GVHD | Graft Vs Host Disease | ALL | CMML | Blood Stem Cell Transplant Failure | MPN | Chemosensitive Hodgkin LymphomaUnited States
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis (MPS)United States, Argentina, Mexico, Spain, United Kingdom
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Medical College of WisconsinChildren's Hospital of PhiladelphiaCompletedMalignant Diseases (ie, Leukemia, MDS, Lymphoma) | Non-malignant Diseases (ie, Bone Marrow Failure Syndromes)United States
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TakedaTakeda Development Center Americas, Inc.RecruitingHunter Syndrome | Mucopolysaccharidosis (MPS)United States
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Gynecologic Oncology GroupNational Cancer Institute (NCI)UnknownFatigue | Anxiety | Recurrent Fallopian Tube Carcinoma | Recurrent Ovarian Carcinoma | Recurrent Primary Peritoneal Carcinoma | Stage I Ovarian Cancer AJCC v6 and v7 | Stage IA Fallopian Tube Cancer AJCC v6 and v7 | Stage IB Fallopian Tube Cancer AJCC v6 and v7 | Stage IC Fallopian Tube Cancer AJCC... and other conditionsUnited States
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Charite University, Berlin, GermanyUnknownMultiple Sclerosis, MS | Clinically Isolated SyndromeGermany
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Mesoblast International SàrlAvailableMultisystem Inflammatory Syndrome in Children (MIS-C) Associated With Coronavirus Disease (COVID-19)
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
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Ginna LaportTerminatedAcute Myelogenous Leukemia (AML) - Relapsed, Primary Refractory Disease or Poor Risk Factors | Chronic Myelogenous Leukemia (CML) - Accelerated or Second Chronic Phase | Myelodysplastic Syndrome (MDS) - High and Intermediate Risk | Non-Hodgkin's Lymphoma (NHL) | Chronic Lymphocytic Leukemia...United States
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Charite University, Berlin, GermanyNeuroCure Clinical Research Center, Charite, BerlinCompletedMultiple Sclerosis (MS) | Clinically Isolated Syndrome (CIS)Germany