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Clinical Trials on MPS-IH (Hurler Syndrome)
Total 489 results
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Mirati Therapeutics Inc.TerminatedAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)United States, Canada, United Kingdom
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Patrick StiffRecruitingMyelodysplastic Syndrome MDS | Acute Myelogenous Leukemia AMLUnited States
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Cornerstone PharmaceuticalsWithdrawnAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)United States
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M.D. Anderson Cancer CenterMerck Sharp & Dohme LLCCompletedAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)United States
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Viron Therapeutics IncVion PharmaceuticalsTerminatedAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)United States
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University of ChicagoTerminatedAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)United States
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GWT-TUD GmbHTerminatedAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)France, Germany
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis I | Hurler SyndromeUnited States
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Daegu Catholic University Medical CenterResearch Institute of Medical Science, Daegu Catholic UniversityCompletedBrachial Plexus Block | Horner Syndrome | Autonomic ImbalanceKorea, Republic of
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Regeneron PharmaceuticalsCompletedGenetic Diseases, Inborn | Familial Cold Autoinflammatory Syndrome (FCAS) | Familial Cold Urticaria | Muckle-Wells Syndrome (MWS)United States
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Nanexa ABUppsala UniversityCompletedMyelodysplastic Syndromes (MDS) | Acute Myeloid Leukemia (AML) | Chronic Myelomonocytic Leukemia (CMML)Sweden
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Stanford UniversityTerminatedCerebral Blood Flow | Horner Syndrome | Regional AnesthesiaUnited States
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Gunnar LachmannCompletedHemophagocytic Lymphohistiocytosis (HLH) | Macrophage Activation Syndrome (MAS) | Hemophagocytic Syndromes
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia (SAA) | Myelodysplastic Syndrome (MDS) With Refractory Anemia (RA)United States
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis II (MPS II)United States, France, United Kingdom, Germany, Sweden, Spain, Brazil, Canada, Italy, Romania
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Justin Watts, MDTakedaCompletedAML | Acute Myelogenous Leukemia | MDS | Advanced Myelodysplastic SyndromesUnited States
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University of UlmRecruitingAcute Myeloid Leukemia (AML) | Higher Risk Myelodysplastic Syndromes (MDS With Excess Blasts 2)Austria, Germany
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Jasper Therapeutics, Inc.RecruitingMYELODYSPLASTIC SYNDROME; MDS | ACUTE MYELOID LEUKEMIA; AMLUnited States
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Masonic Cancer Center, University of MinnesotaCompletedMyelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML)United States
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Duke UniversityRecruiting
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Washington University School of MedicineNational Cancer Institute (NCI); MacroGenicsRecruitingRelapsed Acute Myeloid LeukemiaUnited States
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Nova Scotia Health AuthorityTerry Fox Research InstituteCompletedAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)Canada
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Washington University School of MedicineCantex PharmaceuticalsCompletedAcute Myeloid Leukemia | Myelodysplastic Syndromes | AML | MDSUnited States
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Fred Hutchinson Cancer CenterPatient-Centered Outcomes Research Institute; American Cancer Society, Inc.CompletedAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)United States
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Institut de Recherches Internationales ServierADIR, a Servier Group companyCompletedMyelodysplastic Syndrome (MDS) | Acute Myeloid Leukaemia (AML)France, Australia
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Institut de Recherches Internationales ServierCelgene CorporationActive, not recruitingUntreated AML | Newly Diagnosed Acute Myeloid Leukemia (AML) | AML Arising From Myelodysplastic Syndrome (MDS) | AML Arising From Antecedent Hematologic Disorder (AHD) | AML Arising After Exposure to Genotoxic InjuryUnited States, Germany, Netherlands
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Institut de Recherches Internationales ServierADIR, a Servier Group companyCompletedMyelodysplastic Syndrome (MDS) | Acute Myeloid Leukaemia (AML)United States, Australia, France, Spain
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H. Lee Moffitt Cancer Center and Research InstitutePfizerCompletedChronic Myelomonocytic Leukemia (CMML) | Myelodysplastic Syndrome (MDS)United States
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University of PittsburghWithdrawnAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)United States
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Jason Robert GotlibCelgene CorporationTerminatedLeukemia | Anemia | Myelodysplastic Syndromes (MDS) | Acute Myeloid Leukemia (AML)United States
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University of ZurichRecruitingStroke | Horner's Syndrome | Dissection Carotid ArterySwitzerland
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Memorial Sloan Kettering Cancer CenterActive, not recruitingMyelodysplastic Syndromes (MDS) | Acute Myeloid Leukemia (AML) | Acute Lymphoid Leukemia (ALL)United States
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Masonic Cancer Center, University of MinnesotaCompleted
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University of Michigan Rogel Cancer CenterCompletedHemophagocytic Syndrome (HPS)United States
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Everett MeyerNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedLymphoma, Non-Hodgkin | Acute Myeloid Leukemia | Acute Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Myelodysplastic Syndromes (MDS) | Acute Lymphoblastic Leukemia (ALL) | Myeloid Leukemia, Chronic | Myeloproliferative SyndromeUnited States
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Cullinan Oncology Inc.RecruitingMyelodysplastic Syndrome (MDS) | Relapsed/Refractory Acute Myeloid Leukemia (AML)United States
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Opna-IO LLCCompletedHigh-risk Myelodysplastic Syndrome (MDS) | Relapsed Acute Myeloid Leukemia (AML) | Refractory Acute Myeloid Leukemia (AML)United States
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University Hospitals, LeicesterCompletedAbdominal Pain | Abdominal Myofascial Pain Syndrome (AMPS) | Abdominal Plane Blocks (APB)United Kingdom
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Wuhan Union Hospital, ChinaRecruitingAllogeneic Hematopoietic Stem Cell Transplantation | Acute Myeloid Leukemia, Adult | Myelodysplastic Syndrome(MDS)China
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BioLite, Inc.Not yet recruiting
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Vanderbilt UniversityCompletedCervical Dystonia | Refractory Cervicothoracic Myofascial Pain Syndrome (CMPS)United States
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Forma Therapeutics, Inc.RecruitingVery Low Risk, Low Risk, or Intermediate Risk MDS Per IPSS-RUnited States, France, Canada, Germany
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Brazil
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedLeukemia | Multiple Myeloma | Hodgkin's Lymphoma | Non Hodgkin's Lymphoma | Myelodysplastic Syndrome(MDS)United States
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Mayo ClinicCompleted
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Franziska WachterHarvard Clinical and Translational Science Center (Harvard Catalyst)RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | MDS | Aml | Myeloid Neoplasm | Myeloid Malignancies | Inherited Bone Marrow Failure SyndromeUnited States
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Shanghai Zhongshan HospitalUnknownIliac Vein Compression SyndromeChina
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Daiichi Sankyo, Inc.CompletedAcute Myeloid Leukemia | Leukemia | AML | Myelodysplastic Syndrome | MDSUnited States, Georgia
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University of UlmSunesis PharmaceuticalsCompletedAcute Myeloid Leukemia | Myelodysplastic Syndrome With Excess Blasts-2 (MDS-EB-2)Germany
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Onconova Therapeutics, Inc.The Leukemia and Lymphoma SocietyCompletedMyelodysplastic Syndromes | Chronic Myelomonocytic Leukemia | MDS | RAEBUnited States, Belgium, Germany, Spain, France, Italy