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Clinical Trials on Maple Syrup Urine Disease
Total 10846 results
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University of AarhusAarhus University HospitalRecruitingCardiovascular Diseases | Turner Syndrome | Metabolic Disease | Klinefelter Syndrome | Immunologic Disease | Sex Chromosome AbnormalityDenmark
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IpsenActive, not recruitingRenal Cell Carcinoma | Hepatocellular Carcinoma | Differentiated Thyroid CarcinomaKorea, Republic of
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The Cleveland ClinicNovartisCompletedBreast Cancer | Lung Cancer | Prostate Cancer | Bone Metastases
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Alpine Immune Sciences, Inc.RecruitingLupus Nephritis | Immunoglobulin A Nephropathy | Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis | Membranous NephropathyUnited States, Australia, Korea, Republic of
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SpineX Inc.Rancho Los Amigos National Rehabilitation Center, Downey, California, United... and other collaboratorsRecruitingStroke | Multiple Sclerosis | Neurogenic Bladder | Spinal Cord Injuries (Complete and Incomplete)United States, India, Canada
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaUnited States
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Ultragenyx Pharmaceutical IncKyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia | Hypophosphatemic RicketsUnited States, Brazil, Argentina, Canada, Chile, Colombia
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Wuerzburg University HospitalKyowa Kirin, Inc.Active, not recruiting
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AstraZenecaImaginAb, Inc.TerminatedCarcinoma, Non-Small-Cell Lung | Urinary Bladder Neoplasms | Colorectal CancerUnited States, Canada
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McGill University Health Centre/Research Institute...Canadian Institutes of Health Research (CIHR)RecruitingZellweger Spectrum DisorderCanada
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BayerCompletedOveractive Bladder | Diabetic Neuropathic Pain | Endometriosis Related Pain | Refractory or Unexplained Chronic CoughUnited States
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Pharmacyclics LLC.CompletedGastrointestinal Neoplasms | Breast Neoplasms | Lung Neoplasms | Prostatic Neoplasms | Ovarian NeoplasmsUnited States
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NovartisCompletedBreast Cancer | Multiple Myeloma | Prostate CancerUnited States
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National Cancer Institute (NCI)CompletedVaccine Therapy With or Without Sargramostim in Treating Patients With Advanced or Metastatic CancerOvarian Endometrioid Adenocarcinoma | Adenocarcinoma of the Pancreas | Recurrent Pancreatic Cancer | Stage III Pancreatic Cancer | Stage IV Pancreatic Cancer | Male Breast Cancer | Stage IV Breast Cancer | Stage IIIA Breast Cancer | Stage IIIB Breast Cancer | Recurrent Breast Cancer | Stage IV Colon Cancer | Stage IV Rectal Cancer and other conditionsUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingAndrogen Insensitivity Syndrome | Metabolic Parameters in AIS, CAIS, PAIS and MAIS | Tumor Formation in AIS, CAIS, PAIS and MAIS | Sexual Function AIS, CAIS, PAIS and MAISUnited States
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Maastricht University Medical CenterDiabetes FondsRecruitingType 2 Diabetes | Neuropathy, Diabetic | Nephropathy, Diabetic | Microvascular Function | Retinopathy, DiabeticNetherlands
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National Cancer Institute (NCI)CompletedRecurrent Melanoma | Stage IV Melanoma | Stage IV Renal Cell Cancer | Recurrent Renal Cell CancerUnited States
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Children's Hospital Medical Center, CincinnatiRecruiting
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University of VirginiaRecruitingObesity | Polycystic Ovary Syndrome | HyperandrogenemiaUnited States
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group AUnited States
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Peking Union Medical College HospitalEnrolling by invitationLupus Nephritis | Immune Thrombocytopenia | Refractory Systemic Lupus ErythematosusChina
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National Cancer Institute (NCI)CompletedCervical Cancer | Anal Cancer | Vaginal Cancer | Oropharyngeal Cancer | Penile CancerUnited States
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Odense University HospitalAarhus University Hospital; University of Copenhagen; University Hospital OstravaRecruitingQuality of Life | Multiple Sclerosis | Sexual Dysfunction | Bowel Dysfunction | Neurogenic Dysfunction of the Urinary Bladder | Sacral NeuromodulationDenmark
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Kyowa Kirin, Inc.CompletedX-Linked HypophosphatemiaUnited States
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked Hypophosphatemia (XLH)Sweden, Spain, United Kingdom, Italy, Austria, France
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Yale UniversityCompleted
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Hellenic Cooperative Oncology GroupUniversity of IoanninaCompletedBreast Cancer | Prostate Cancer | Non Small Cell Lung CancerGreece
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Children's Oncology GroupNot yet recruitingStage I Kidney Wilms Tumor | Stage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor
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Jonsson Comprehensive Cancer CenterNational Cancer Institute (NCI)CompletedT-Cell Response in Patients Receiving Trastuzumab and/or Chemotherapy for HER2-Positive Solid TumorsSarcoma | Breast Cancer | Ovarian Cancer | Lung Cancer | Prostate Cancer | Unspecified Adult Solid Tumor, Protocol SpecificUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedProstate Cancer | Brain and Central Nervous System TumorsUnited States, Spain
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Vanderbilt-Ingram Cancer CenterNational Cancer Institute (NCI)RecruitingMetastatic Clear Cell Renal Cell Carcinoma | Advanced Clear Cell Renal Cell Carcinoma | Stage III Renal Cell Cancer AJCC v8 | Stage IV Renal Cell Cancer AJCC v8United States
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University of Southern CaliforniaNational Cancer Institute (NCI)Active, not recruitingMetastatic Renal Cell Cancer | Recurrent Renal Cell Carcinoma | Stage III Renal Cell Cancer | Healthy Subject | Stage I Renal Cell Cancer | Stage II Renal Cell CancerUnited States
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Virginia Commonwealth UniversityUnited States Department of DefenseRecruitingBrain Cancer | Brain Tumor | Metastatic Lung Cancer | Metastatic Breast Cancer | Metastatic Melanoma | Brain Metastases | Metastatic Colon Cancer | Metastatic Kidney CancerUnited States
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Spruce BiosciencesRecruitingCongenital Adrenal Hyperplasia | 21-OHDUnited States
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University of California, San FranciscoNational Cancer Institute (NCI); Dana-Farber Cancer Institute; University of... and other collaboratorsRecruitingKidney Cancer | Renal Cell Carcinoma | Breast Cancer | Ovarian Cancer | Rectal Cancer | Prostate Cancer | Bladder Cancer | Endometrial Cancer | Colon CancerUnited States
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Adrenas Therapeutics IncRecruitingCongenital Adrenal HyperplasiaUnited States
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Neurocrine BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, United Kingdom, France, Greece, Italy, Spain, Belgium, Canada, Germany, Poland
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Diurnal LimitedEnrolling by invitationCongenital Adrenal HyperplasiaUnited States, France, Japan
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University of Texas Southwestern Medical CenterEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsSuspendedCongenital Adrenal HyperplasiaUnited States
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Estonia, Germany, Korea, Republic of, Latvia, Lithuania, Poland, Romania, Spain, Sweden, Turkey, Canada, Italy, United Kingdom
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University Hospital, MontpellierRecruiting
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Peking University Third HospitalRecruitingRenal Cell Carcinoma | Pancreatic Cancer | Lung Cancer | Liver CancerChina
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University Hospital, AntwerpKom Op Tegen Kanker; Stichting tegen KankerRecruitingEsophageal Cancer | Ovarian Cancer | Pancreas Cancer | Liver CancerBelgium
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Clinique OvoRecruitingPCOS (Polycystic Ovary Syndrome) of Bilateral OvariesCanada
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University of VirginiaWaterloo FoundationRecruitingPolycystic Ovary Syndrome | Puberty Disorders | Ovulation DisorderUnited States
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University of VirginiaRecruitingObesity | Polycystic Ovary Syndrome | HyperandrogenemiaUnited States
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaNetherlands, United States, United Kingdom, France
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Ultragenyx Pharmaceutical IncKyowa Kirin Co., Ltd.AvailableX-linked Hypophosphatemia | Tumor-Induced Osteomalacia
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Orthopedic Hospital Vienna SpeisingCompleted
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic Anemia (SAA) | Hypo-Plastic Myelodysplastic Syndrome (MDS)United States