- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Metabolic Control
Total 83382 results
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Guy's and St Thomas' NHS Foundation TrustUnknownCardiovascular Diseases | PhenylketonuriasUnited Kingdom
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Taipei Veterans General Hospital, TaiwanBioMarin PharmaceuticalUnknownPAH Deficiency | Pku Phenylketonuria
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Nutricia UK LtdCompletedPhenylketonurias | Hyperphenylalaninaemia, Type IUnited Kingdom
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University of Southern CaliforniaBioMarin PharmaceuticalCompleted
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Stanford UniversityBioMarin PharmaceuticalWithdrawnClassical Phenylketonuria(PKU)
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Luca RonfaniUniversity of TriesteCompletedUrea Cycle Disorders, Inborn | Other Metabolic DiseasesItaly
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TakedaActive, not recruiting
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CENTOGENE GmbH RostockActive, not recruiting
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Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher DiseaseUnited States
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PfizerCompletedGaucher DiseaseIsrael, South Africa, Paraguay
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PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
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Hospital St. Joseph, Marseille, FranceCompleted
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Assistance Publique - Hôpitaux de ParisCompletedGaucher DiseaseFrance
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Amicus TherapeuticsCompleted
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University of PittsburghWithdrawnMetachromatic LeukodystrophyUnited States
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)Denmark, Germany, Japan, Australia, France, Brazil, Czechia
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National Organization for Rare DisordersFood and Drug Administration (FDA)Active, not recruitingMetachromatic LeukodystrophyUnited States
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Institut National de la Santé Et de la Recherche...Assistance Publique - Hôpitaux de Paris; European Leukodystrophy AssociationActive, not recruitingMetachromatic LeukodystrophyFrance
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Shenzhen Geno-Immune Medical InstituteUnknown
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Bellicum PharmaceuticalsNo longer availableHurler Syndrome | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Inherited Metabolic Disorder | Lysosomal Storage DisorderUnited States
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BioMarin PharmaceuticalActive, not recruitingPhenylketonuria (PKU)United States, Germany
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metaX Institut fuer Diatetik GmbHBirmingham Children's HospitalCompletedPhenylketonurias | Hyperphenylalaninaemia | Tetrahydrobiopterin DeficiencyUnited Kingdom
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Homology Medicines, IncEnrolling by invitationPhenylketonuria | PAH DeficiencyUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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University of British ColumbiaRare Disease Foundation, Vancouver, CanadaCompleted
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Brendan LeeCompleted
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University of GlasgowUnknownPhenylketonuria (PKU)United Kingdom
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University Hospital, ToursInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedPKU | HyperphenylalaninemiaFrance
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Dr. Linda RandolphBioMarin PharmaceuticalTerminated
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ShireTerminated
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TakedaCompleted
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseCanada, Russian Federation, Tunisia
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Nutricia ResearchCompletedInborn Errors of Metabolism | Urea Cycle DisorderUnited States
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ShireCompleted
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PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain
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PfizerCompletedGaucher DiseaseChile, United Kingdom, Canada, Spain, Israel, United States, Australia, South Africa
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PfizerCompletedGaucher DiseaseIsrael, Paraguay, South Africa
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Yasmeen Abd Elbaset HamzaaUnknownGaucher Disease
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States, Sweden, India, Netherlands, Austria, Japan, China, Serbia, France, Croatia, Australia, Portugal, Canada, Brazil, Greece, Romania, Russian Federation
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ISU Abxis Co., Ltd.Completed
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National Defense Medical Center, TaiwanCompletedPsychological Distress | Prediabetes | Autonomic Nervous System Imbalance | Poor Glycemic ControlTaiwan
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NYU Langone HealthGenzyme, a Sanofi CompanyCompleted
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Yassin Abdelghaffar Charity Center for Liver Disease...Society of Friends of Liver Patients in the Arab World (SLPAW)RecruitingHereditary Tyrosinemia, Type IEgypt
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Children's National Research InstituteBoston Children's HospitalRecruitingUrea Cycle DisordersUnited States
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University of Missouri-ColumbiaCompleted
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University Hospital, ToursCompletedPhenylketonuriaFrance