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Clinical Trials on Mitochondrial Respiratory Chain Deficiencies
Total 230 results
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Institut National de Recherche pour l'Agriculture...CompletedMitochondrial Respiratory Chain DeficienciesFrance
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...RecruitingEnd Stage Liver Disease | Mitochondrial Diseases | Acute Liver Failure | Respiratory Chain Deficiencies, Mitochondrial | Disorder of Fatty Acid OxidationUnited States, Canada
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Abliva ABCompletedMitochondrial Diseases | Mitochondrial Myopathies | MELAS Syndrome | Mitochondrial Respiratory Chain DeficienciesUnited Kingdom
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Yungjin Pharm. Co., Ltd.CompletedMELAS Syndrome | Mitochondrial Respiratory Chain DeficienciesKorea, Republic of
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Millennium Pharmaceuticals, Inc.CompletedLight-Chain AmyloidosisUnited States, Canada, France, Germany, Italy
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Criterium, Inc.AmgenCompletedAmyloidosis | Systemic Light Chain AmyloidosisUnited States
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Peking Union Medical College HospitalRecruitingLight Chain (AL) Amyloidosis | Venetoclax | CCND1 TranslocationChina
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National Human Genome Research Institute (NHGRI)RecruitingMitochondrial Disorders | Leigh Disease | Oxidative Phosphorylation Deficiencies | Electron Transport Chain Disorders, MitochondrialUnited States
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Oregon Health and Science UniversityUniversity of PittsburghCompletedVery Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase 2 (CPT2) Deficiency | Mitochondrial Trifunctional Protein (TFP) Deficiency | Long-chain 3 hydroxyacylCoA Dehydrogenase (LCHAD) DeficiencyUnited States
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Tufts Medical CenterSanofiWithdrawnAmyloidosis | Light Chain (AL) Amyloidosis
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial Disorders | Mitochondrial Genetic Disorders | Disorder of Mitochondrial Respiratory Chain Complexes | Deletion and Duplication of Mitochondrial DNAUnited States, Canada
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Millennium Pharmaceuticals, Inc.TerminatedRelapsed or Refractory Systemic Light Chain AmyloidosisUnited States, Canada, Spain, Israel, France, Australia, Denmark, Germany, Korea, Republic of, Greece, Netherlands, Brazil, Czechia, Italy, United Kingdom
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Nanjing University School of MedicineRecruiting
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European Myeloma NetworkJanssen PharmaceuticaActive, not recruitingLight Chain (AL) Amyloidosis, Stage 3BNetherlands, Greece, France, Italy
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Peking Union Medical College HospitalXian-Janssen Pharmaceutical Ltd.Active, not recruitingAmyloidosis; SystemicChina
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Alfred Chung, MDAbbVie; Janssen PharmaceuticalsRecruitingAL Amyloidosis | Light Chain (AL) Amyloidosis | Systemic Light Chain DiseaseUnited States
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Nanjing University School of MedicineRecruitingLight Chain AmyloidosisChina
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Guangdong Provincial People's HospitalRecruitingImmunoglobulin Light-Chain AmyloidosisChina
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Mayo ClinicNational Cancer Institute (NCI)WithdrawnAmyloidosis | Immunoglobulin Light Chain Deposition
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Regeneron PharmaceuticalsNot yet recruitingRelapsed/Refractory Systemic Light Chain Amyloidosis
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Prothena Biosciences Ltd.RecruitingLight Chain (AL) AmyloidosisUnited States, Korea, Republic of, Australia, Denmark, France, Italy, Spain, Israel, Taiwan, Austria, Canada, Czechia, Germany, Greece, Hungary, Japan, Netherlands, Poland, Portugal, Turkey, United Kingdom, Belgium, Ireland
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University of FloridaNo longer availableMitochondrial Enzyme DeficienciesUnited States
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Florian MichelGerman Federal Ministry of Education and ResearchCompletedLight Chain (AL) Amyloidosis | Cardiac InvolvementGermany
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AbbVieRecruitingImmunoglobulin Light Chain (AL) AmyloidosisJapan
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Air Force Military Medical University, ChinaNot yet recruitingImmunoglobulin Light-chain Amyloidosis
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Steen Hvitfeldt PoulsenCompletedTransthyretin Amyloid Cardiopathy | Mitochondrial PathologyDenmark
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Jian LiPeking University First Hospital; Tongji Hospital; Nanfang Hospital of Southern... and other collaboratorsCompletedAmyloidosis; SystemicChina
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Cedars-Sinai Medical CenterEnrolling by invitationAmyloidosis, Immunoglobulin Light-chainUnited States, Canada
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Memorial Sloan Kettering Cancer CenterMillennium Pharmaceuticals, Inc.CompletedAmyloidosis | Light Chain Deposition Disease (LCDD or MIDD) | Light Chain and Heavy Chain Deposition Disease (LHCDD or MIDD) | Monoclonal Immunoglobulin Deposition Disease (MIDD)United States
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Nexcella Inc.Not yet recruitingLight Chain (AL) AmyloidosisUnited States
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Sorrento Therapeutics, Inc.WithdrawnLight Chain (AL) Amyloidosis
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National Cancer Institute (NCI)CompletedPrimary Systemic Amyloidosis | Light Chain Deposition DiseaseUnited States
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Sorrento Therapeutics, Inc.RecruitingLight Chain (AL) AmyloidosisUnited States
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IRCCS Policlinico S. MatteoTerminatedPrimary Amyloidosis of Light Chain TypeItaly
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IRCCS Policlinico S. MatteoCompletedPrimary Amyloidosis of Light Chain TypeItaly
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SanofiRecruitingRelapsed/Refractory Multiple Myeloma | Amyloid Light-chain AmyloidosisItaly, Australia, Hungary, United Kingdom, Czechia, Belgium, Spain
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
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The Cleveland ClinicCompletedAmyloidosis | Spinal Stenosis | Amyloid | Transthyretin Amyloidosis | Primary Amyloidosis of Light Chain TypeUnited States
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TakedaCompletedMultiple Myeloma | Immunoglobulin Light-chain AmyloidosisSpain
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National Human Genome Research Institute (NHGRI)RecruitingMitochondrial DiseaseUnited States
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Istanbul University - Cerrahpasa (IUC)Active, not recruitingChemotherapy Effect | Congestive Heart Failure | Amyloid CardiomyopathyTurkey
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The Cleveland ClinicCompletedAmyloidosis | Transthyretin Amyloidosis | Trigger Finger | Primary Amyloidosis of Light Chain TypeUnited States
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Mayo ClinicRecruitingAL AmyloidosisUnited States
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Intergroupe Francophone du MyelomeBristol-Myers Squibb; SanofiRecruiting
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European Myeloma NetworkGlaxoSmithKlineRecruitingAL AmyloidosisGermany, Netherlands, France, Greece, Italy, United Kingdom
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Tufts Medical CenterTerminatedAL AmyloidosisUnited States
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Columbia UniversityCephalonCompletedAL AmyloidosisUnited States
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Prothena Biosciences Ltd.TerminatedAL AmyloidosisUnited States, Spain, Australia, Italy, Germany, Austria, Greece, France, Israel, United Kingdom
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European Myeloma NetworkCompleted
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Jin Lu, MDRecruiting