- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Mitochondrial Genetic Disorders
Total 151779 results
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Baxalta now part of ShireTakedaCompleted
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PfizerCompletedHemophilia BGermany, Austria
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Suellen Marinho AndradeNot yet recruiting
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BUnited States
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University of Illinois College of Medicine at PeoriaRady Children's Institute of Genomic MedicineActive, not recruitingGenetic Disease | Genetic SyndromeUnited States
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States
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Nicklaus Children's Hospital f/k/a Miami Children...Rady Pediatric Genomics & Systems Medicine InstituteRecruiting
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University Hospital, Clermont-FerrandRecruitingPulmonary Disease, Chronic Obstructive | Oxygen Deficiency | Mitochondrial AlterationFrance
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Duke UniversitySuspendedLysosomal Storage Diseases | Genetic Disease | Inborn Errors of Metabolism | Glycogen Storage Disease | Storage DiseaseUnited States
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University of California, DavisEunice Kennedy Shriver National Institute of Child Health and Human Development...Enrolling by invitationIntellectual Disability | Down Syndrome | Attention Deficit Hyperactivity Disorder | Fragile X SyndromeUnited States
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AB2 Bio Ltd.CompletedNLRC4-MAS | XIAP DeficiencyUnited States, Canada, Germany
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AB2 Bio Ltd.Active, not recruitingNLRC4-MAS | XIAP DeficiencyUnited States, Canada, Germany
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Fundación Pública Andaluza para la Investigación...Delos ClinicalCompleted
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Hasan Kalyoncu UniversityNot yet recruitingHemophilia A | Hemophilia B | HemophiliaTurkey
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Assiut UniversityNot yet recruitingHemophilia A | Hemophilia B
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BUnited States, Italy, Spain, Taiwan, Australia, Belgium, United Kingdom, France, Germany, India, South Africa, Canada, Poland, Armenia, Turkey
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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Regeneron PharmaceuticalsRecruitingHemophilia BUnited States, Germany, United Kingdom, Canada
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Swedish Orphan BiovitrumIQVIA Pvt. LtdTerminatedHemophilia A | Hemophilia BBulgaria, Croatia, Czechia, France, Hungary, Ireland, Italy, Romania, Slovenia, Spain, United Kingdom
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St. Jude Children's Research HospitalChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingHemophilia BUnited States, United Kingdom
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Freeline TherapeuticsTerminatedHemophilia BUnited States, United Kingdom
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BBulgaria, United States, United Kingdom, Russian Federation, Switzerland
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University College, LondonTerminatedHemophilia BIreland, United Kingdom, Italy, United States
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CSL BehringCompletedHemophilia BGermany, Denmark, Netherlands
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, Canada, China, France, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, Italy, Japan, South Africa, Spain, Taiwan
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, China, Denmark, France, Israel, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, South Africa, Spain, Taiwan, Hungary, Italy
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Sangamo TherapeuticsTerminated
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Catalyst BiosciencesCompletedHemophilia BSouth Africa
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Baxalta now part of ShireCompletedHemophilia BKorea, Republic of
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Baxalta now part of ShireCompleted
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Medexus Pharma, Inc.CompletedHemophilia BUnited States, France, United Kingdom, India, Israel, Italy, Poland
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Baxalta now part of ShireCompletedHemophilia A | Hemophilia BUnited States
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ISU Abxis Co., Ltd.Catalyst BiosciencesCompletedHemophilia BKorea, Republic of
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BayerCompletedHemophilia A | Hemophilia BUkraine, United Kingdom, Bulgaria, Germany, Japan
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Royal Free Hospital NHS Foundation TrustUnknown
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Nationwide Children's HospitalCompleted
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CSL BehringCompletedHemophilia BGermany, Australia, Italy, Israel, Czech Republic, Spain, France, Canada, Austria, Russian Federation
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PfizerCompletedHemophilia BCanada, Singapore, Turkey, Croatia, Korea, Republic of, Mexico, Poland, Bulgaria, Malaysia
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CSL BehringCompletedHemophilia BSpain, Italy, France, Germany, Austria, Israel
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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CSL BehringNot yet recruiting
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Regeneron PharmaceuticalsIntellia TherapeuticsNot yet recruiting
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CSL BehringRecruiting
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.RecruitingHemophilia A | Hemophilia BChina
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Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruiting