- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Mitochondrial Disease in United States
Total 147158 results
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Stealth BioTherapeutics Inc.CompletedLeber's Hereditary Optic NeuropathyUnited States
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Design TherapeuticsCompleted
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Larimar Therapeutics, Inc.Clinilabs, Inc.CompletedHealthy Volunteers | Friedreich AtaxiaUnited States
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLCCompletedFriedreich AtaxiaUnited States
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National Eye Institute (NEI)CompletedMacular Degeneration | Diabetic Retinopathy | Mitochondria | Hippel-Landau DiseaseUnited States
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The University of Texas Medical Branch, GalvestonWithdrawnGlaucoma | Eye Diseases | Diabetic Retinopathy | Age Related Macular Degeneration | Mitochondrial DNA | Ophthalmic TraumaUnited States
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University of California, IrvineWithdrawnDilated Cardiomyopathy | Hypertrophic Cardiomyopathy | Restrictive Cardiomyopathy | Mitochondrial Cardiomyopathy | Noncompaction CardiomyopathyUnited States
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Edison Pharmaceuticals IncNo longer availableLeber's Hereditary Optic NeuropathyUnited States
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Medical College of WisconsinTerminatedLeber's Hereditary Optic Neuropathy (LHON)United States
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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Children's Hospital of PhiladelphiaUniversity of California, Los Angeles; University of FloridaCompleted
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PTC TherapeuticsCompletedFriedreich's AtaxiaUnited States
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PTC TherapeuticsAxio Research. LLCCompleted
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University of NottinghamWithdrawnCovid19 | Muscle Loss | Mitochondrial AlterationUnited Kingdom
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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PTC TherapeuticsCompletedLeigh SyndromeUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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University of South FloridaCompletedFriedreich's Ataxia | Spinocerebellar Ataxia - All Sub-typesUnited States
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Neurocrine BiosciencesTakedaCompletedFriedreich AtaxiaUnited States
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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ShireCompletedFriedreich's AtaxiaUnited States
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Reata, a wholly owned subsidiary of BiogenAbbVie; Friedreich's Ataxia Research AllianceActive, not recruitingFriedreich AtaxiaUnited States, Australia, Austria, Italy, United Kingdom
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Neurophth Therapeutics IncRecruitingLeber Hereditary Optic Neuropathy (LHON)China, United States
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University of California, DavisNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Vanderbilt...RecruitingDiabetes | Fatigue | Chronic Kidney Diseases | Insulin Resistance | Metabolic Acidosis | Physical Endurance | Mitochondrial EnergeticsUnited States
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University of California, Los AngelesGilead SciencesCompletedHIV/AIDS | Mitochondrial Alteration | Antiviral Toxicity | Antiviral Drug Adverse ReactionUnited States
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Monash UniversityChildren's Hospital of Philadelphia; McGill University; University of Florida; University... and other collaboratorsActive, not recruitingFriedreich AtaxiaUnited States, Canada, Australia, Brazil, Germany
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Neurophth Therapeutics IncActive, not recruitingLeber Hereditary Optic Neuropathy (LHON)United States
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Weill Medical College of Cornell UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingMyocardial Fibrosis | Cardiomyopathies | Friedreich Ataxia | Cardiac HypertrophyUnited States
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, United Kingdom, Germany
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases...RecruitingPyruvate Dehydrogenase Complex Deficiency DiseaseUnited States
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University of PittsburghCompletedPulmonary Hypertension | Friedreich Ataxia | Iron-sulfur Cluster DeficiencyUnited States
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Imperial College LondonUnknown
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, Spain, United Kingdom
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Friedreich's Ataxia Research AllianceChildren's Hospital of Philadelphia; University of RochesterRecruitingFriedreich Ataxia | Neuro-Degenerative DiseaseUnited States, Canada, New Zealand, Australia, India
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GenSight BiologicsActive, not recruitingLeber Hereditary Optic NeuropathyBelgium, Spain, United States, France, United Kingdom, Taiwan, Italy
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Lexeo TherapeuticsRecruitingFriedreich Ataxia | Cardiomyopathy, SecondaryUnited States, Canada
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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Friedreich's Ataxia Research AllianceRecruitingFriedreich AtaxiaUnited States, Canada, New Zealand, Australia, France, Austria, Belgium, Brazil, Czechia, Germany, Greece, Ireland, Italy, Spain, United Kingdom, India, Netherlands
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Baylor College of MedicineChildren's National Research InstituteRecruitingOrnithine Transcarbamylase Deficiency | Urea Cycle Disorder | Carbamyl Phosphate Synthetase Deficiency | Argininosuccinic Aciduria | Hyperargininemia | Citrullinemia 1 | ARGI Deficiency | ASL Deficiency | ASS Deficiency | NAGS DeficiencyUnited States
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, Germany, United Kingdom
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RWTH Aachen UniversityAssistance Publique - Hôpitaux de ParisWithdrawnFriedreich AtaxiaSpain, Italy, Austria, Germany, United Kingdom, France
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University of ChicagoPfizer; Biogen; APDM Wearable TechnologiesActive, not recruitingSpinocerebellar Ataxia Type 3 | Friedreich Ataxia | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6United States
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic NeuropathyCanada, Germany, United Kingdom
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, United Kingdom, Belgium, France, Germany
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States